-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

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Ticketed Session denotes that this is a ticketed session.

Understanding Immediate Toxicities of Current Gene and Cell Therapy Tools

Symposia: Scientific Workshop on Genomic Toxicities of Gene and Cell Therapies Program: Scientific Workshops
Friday, December 6, 2024: 2:03 PM-3:00 PM
Room 31 (San Diego Convention Center)
Moderators:
Marina Cavazzana, MD, PhD, ARRAY(0xf127ab0) and Saar Gill, MD, PhD, University of Pennsylvania
Disclosures:
Gill: Mission Bio: Membership on an entity's Board of Directors or advisory committees; Asher Biotherapeutics: Research Funding; Novartis: Patents & Royalties, Research Funding; Carisma: Current holder of stock options in a privately-held company; Interius: Current holder of stock options in a privately-held company, Research Funding.

This session will focus on the basic biology that enables gene editing and correction and a discussion of the clinical implications of these novel therapies.

Marina Cavazzana, MD, PhD

Assistance Publique-Hôpitaux de Paris, Paris, France; Imagine Institute, Paris, France

Saar Gill, MD, PhD

University of Pennsylvania, Philadelphia, PA

Annarita Miccio, PhD

Imagine Institute, Paris, France

Marcela Maus, MD

Harvard Medical School, Lexington, MA

Janet L. Kwiatkowski, MD

Children's Hospital of Philadelphia, Philadelphia, PA; Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA

Noelle Frey, MD, MS

University of Pennsylvania, Philadelphia, PA