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Hematopoietic Cell Transplantation Versus Gene Therapy for Hemoglobinopathies

Scientific Workshop on Genomic Toxicities of Gene and Cell Therapies
Program: Scientific Workshops
Session: Understanding Immediate Toxicities of Current Gene and Cell Therapy Tools
Friday, December 6, 2024, 2:03 PM-3:00 PM

Janet L. Kwiatkowski, MD

Children's Hospital of Philadelphia, Philadelphia, PA; Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA

Disclosures: Kwiatkowski: Forma Therapeutics: Consultancy, Research Funding; Vertex Pharmaceuticals: Consultancy; Agios: Consultancy, Research Funding; BioMarin: Consultancy; Chiesi: Consultancy; Bristol Myers Squibb: Consultancy; bluebird bio, Inc.: Consultancy, Research Funding; Editas Medicine: Research Funding; Pfizer: Research Funding; CRISPR/Vertex: Consultancy, Research Funding; Imara: Consultancy, Research Funding; Silence Therapeutics: Consultancy; Apopharma: Research Funding; Novo-Nordisk: Consultancy.