Grigorios Tsaknakis^1*, Alice Grossi^2*, Marta Rusmini^2*, Isabella Ceccherini^2*, Paolo Uva^3*, Maurizio Miano^4*, Irene Mavroudi^1*, Erasmia Boutakoglou^1*, Carlo Dufour, MD⁴, Francesca Fioredda^4* and Helen A. Papadaki, MD¹

¹Hemopoiesis Research Laboratory, School of Medicine, University of Crete & Department of Hematology, University Hospital of Heraklion, Heraklion, Greece
²Laboratory of Genetics & Genomics of Rare Diseases-IRCCS Istituto Giannina Gaslini, Genoa, Italy
³Clinical Bioinformatics, IRCCS Istituto Giannina Gaslini, Genoa, Italy
⁴Hematology Unit-IRCCS Istituto Giannina Gaslini, Genoa, Italy

Malte Ulrich Ritter^1*, Masoud Nasri, PhD^2*, Perihan Mir, PhD^2*, Benjamin Dannenmann, PhD^2*, Masako Monika Kaufmann^3*, Yun Xu^2*, Natalia Borbaran-Bravo^2*, Maksim Klimiankou, PhD^2*, Claudia Lengerke, MD^4,5, Cornelia Zeidler, MD^6*, Toni Cathomen, PhD^3*, Karl Welte, MD, PhD^2,7 and Julia Skokowa, MD, PhD^8,9

¹Department of Oncology, Hematology, Immunology, Rheumatology and Pulmonology, University Hospital Tuebingen, Tübingen, BW, Germany
²Department of Oncology, Hematology, Immunology, Rheumatology and Pulmonology, University Hospital Tuebingen, Tübingen, Germany
³Institute for Transfusion Medicine and Gene Therapy, Medical Center – University of Freiburg, Freiburg, Germany
⁴Department of Internal Medicine II, Hematology, Oncology, Clinical Immunology and Rheumatology, University Hospital Tuebingen, Tuebingen, Germany
⁵University Hospital Tuebingen, Tübingen, Germany
⁶Hematology / Oncology, SCNIR, Hannover Medical School, Hannover, Germany
⁷Pediatric Hematology and Oncology, University Children's Hospital, Tuebingen, Baden-Wuerttemberg, Germany
⁸University Hospital Tuebingen, Tuebingen, Germany
⁹Gene and RNA Therapy Center (GRTC), University Hospital Tübingen, Tübingen, Germany

Vahagn Makaryan, MD, Merideth Kelley, MS^*, Audrey Anna Bolyard^* and David C. Dale, MD

University of Washington, Seattle, WA

Malte Ulrich Ritter^1*, Masoud Nasri, PhD^2,3*, Benjamin Dannenmann, PhD^2,3*, Perihan Mir, PhD^2*, Benjamin Secker, MSc^4*, Cornelia Zeidler, MD^5*, Maksim Klimiankou, PhD^2,6*, Karl Welte, MD, PhD⁷ and Julia Skokowa, MD, PhD^3,8

¹Department of Oncology, Hematology, Immunology, Rheumatology and Pulmonology, University Hospital Tuebingen, Tübingen, BW, Germany
²Department of Oncology, Hematology, Immunology, Rheumatology and Pulmonology, University Hospital Tuebingen, Tübingen, Germany
³Gene and RNA Therapy Center (GRTC), University Hospital Tübingen, Tübingen, Germany
⁴University Hospital Tuebingen, Tuebingen, DEU
⁵Hematology / Oncology, SCNIR, Hannover Medical School, Hannover, Germany
⁶Gene and RNA Therapy Center, University Hospital Tübingen, Tübingen, Germany
⁷Pediatric Hematology and Oncology, University Children's Hospital, Tuebingen, Baden-Wuerttemberg, Germany
⁸University Hospital Tuebingen, Tuebingen, Germany

Christina Simoglou Karali^1*, Simone Riva, BSc, MSc^2*, Sally-Ann Clark, BSc, PhD^1*, Sean Wen, BSc, MSc, PhD^1*, Nikolaos Sousos, MD, MSc, DPhil^1,3*, Eleni Louka, MD, PhD^1*, E. Ravza Gür, BSc, MSc, PhD^2*, Nawshad Hayder, BSc, MSc^1*, William E. Pierceall, PhD^4*, Anjan Thakurta, PhD⁵, Anita K. Gandhi, PhD⁶, Patrick R Hagner, PhD^6*, Jim Hughes, BSc, PhD^2* and Adam J Mead, MRCP, FRCPath, PhD¹

¹Medical Research Council (MRC) Molecular Haematology Unit, MRC Weatherall Institute of Molecular Medicine, National Institute for Health Research Biomedical Research Centre, University of Oxford, Oxford, United Kingdom
²Centre for Computational Biology, Medical Research Council (MRC) Weatherall Institute of Molecular Medicine, Radcliffe Department of Medicine, University of Oxford, Oxford, United Kingdom
³Cancer and Haematology Centre, The Churchill Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, United Kingdom
⁴Hematology, Translational Medicine and Disease Team, Bristol Myers Squibb, Summit, NJ
⁵Oxford Translational Myeloma Centre, Nuffield Department of Orthopaedics, Rheumatology and Musculoskeletal Sciences, University of Oxford, Oxford, United Kingdom
⁶Translational Development and Diagnostics, Bristol Myers Squibb, Summit, NJ

Danielle E Arnold^1*, Saara Kaviany, DO^2*, Jahnavi Aluri^3*, Luis Murguia-Favela^4*, Nicola A. Wright, MD⁵, Thomas P. Loughran Jr., MD⁶, Jonathan Powell, MD^7*, Suk See De Ravin, MD, PhD^8*, V. Koneti Rao, MD⁹, Steven Holland, MD^10*, Jack Bleesing, MD, PhD^11*, Jeffrey J. Bednarski, MD, PhD¹², James A. Connelly, MD^13* and Megan Cooper, MD PhD^14*

¹National Cancer Institute, Immune Deficiency-Cellular Therapy Program, Center for Cancer Research, Bethesda, MD
²University of Chicago, Chicago
³Washington University, St Louis, MO
⁴University of Calgary, Calgary, AB, CAN
⁵Alberta Children's Hospital, Calgary, AB, Canada
⁶UVA Comprehensive Cancer Center, Charlottesville, VA
⁷Nemour's Children's Hospital, Wilmington
⁸NIAID, Bethesda, MD
⁹NIAID National Institutes of Health, Bethesda, MD
¹⁰NIAID/NIH, Bethesda, MD
¹¹Cincinnati Children's Hospital Medical Center, Cincinnati, OH
¹²Washington University School of Medicine in St. Louis, St Louis, MO
¹³Vanderbilt University Medical Center, Nashville, TN
¹⁴Department of Pediatrics, Washington University, St. Louis