Maria Domenica Cappellini¹, Ali T. Taher, MD, PhD, FRCP², Antonio Piga, MD³, Farrukh Shah^4*, Ersi Voskaridou^5*, Vip Viprakasit^6*, John B. Porter, MA, M.D., FRCP, FRCPath^7*, Olivier Hermine^8,9*, Ellis J. Neufeld¹⁰, Alexis A. Thompson, MD¹¹, Derek Tang^12*, Peiwen Yu^13*, Shien Guo^13*, Jeevan K. Shetty^12*, Dimana Miteva^12*, Tatiana Zinger^12*, Jay T. Backstrom^14* and Esther Natalie Oliva, MD¹⁵

¹University of Milan, Milan, Italy
²Department of Internal Medicine, American University of Beirut Medical Center, Beirut, Lebanon
³Department of Clinical and Biological Sciences, University of Turin, Turin, Italy
⁴Department of Haematology, Whittington Health NHS Trust, London, United Kingdom
⁵Thalassemia and Sickle Cell Center of Laiko General Hospital, Athens, Greece
⁶Siriraj Hospital, Mahidol University, Bangkok, Thailand
⁷University College London Hospitals NHS Foundation Trust, London, United Kingdom
⁸Necker Hospital, Assistance Publique–Hôpitaux de Paris, Paris, France
⁹Imagine Institute, INSERM Unité 1163, University of Paris, Paris, France
¹⁰St. Jude Children's Research Hospital, Memphis, TN
¹¹Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
¹²Bristol Myers Squibb, Princeton, NJ
¹³Evidera, Waltham, MA
¹⁴Acceleron Pharma, Cambridge, MA
¹⁵Grande Ospedale Metropolitano Bianchi-Melacrino-Morelli, Reggio Calabria, Italy

Julie Kanter, MD¹, John F. Tisdale, MD^2,3, Markus Y Mapara, MD, PhD⁴, Janet L. Kwiatkowski, MD, MSCE^5,6, Lakshmanan Krishnamurti, MD⁷, Ren Chen^8*, Meghan E. Gallagher, MSc^8*, Yuchen Ding, PhD^8*, Sunita Goyal, MD^8*, Clark Paramore, MPH^8*, Alexis A. Thompson, MD^9,10 and Mark C. Walters, MD¹¹

¹University of Alabama at Birmingham, Birmingham, AL
²National Institutes of Health, Bethesda, MD
³Clinical and Molecular Therapeutics Branch, NHLBI / NIDDK, NIH, Bethesda, MD
⁴Columbia Center for Translational Immunology, Columbia University, New York, NY
⁵University of Pennsylvania Perelman School of Medicine, Philadelphia, PA
⁶The Children's Hospital of Philadelphia, Philadelphia, PA
⁷Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Emory University, Atlanta, GA
⁸bluebird bio, Inc., Cambridge, MA
⁹Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
¹⁰Northwestern University Feinberg School of Medicine, Chicago, IL
¹¹UCSF Benioff Children's Hospital Oakland, Oakland, CA

Zaria Williams¹, Steven J. Hardy, PhD^2,3*, Carly Berger^4*, Danielle Griffin^4*, Hannah Weisman^4*, Hua Liang, PhD^5* and Deepika S. Darbari, MD^6,7,8

¹Howard University College of Medicine, Washington, DC
²Center for Cancer and Blood Disorders, Children's National Health System, Washington, DC
³Departments of Pediatrics and Psychiatry & Behavioral Sciences, George Washington University School of Medicine and Health Sciences, Washington, DC
⁴Children's National Hospital, Washington, DC
⁵The George Washington University, Washington, DC
⁶Division of Hematology and Oncology, Children's National Medical Center, Washington, DC
⁷Center for Cancer and Blood Disorders, Children's National Medical Center, Washington, DC
⁸Pediatrics, The George Washington University School of Medicine, Washington, DC

Shannon Phillips, PhD, RN^1*, Julie Kanter, MD², Martina Mueller, PhD^1*, Kenneth Ruggiero, PhD^1* and Teresa Kelechi, PhD, RN, FAAN^1*

¹College of Nursing, Medical University of South Carolina, Charleston, SC
²Hematology/Oncology, Comprehensive Sickle Cell Center, University of Alabama at Birmingham, Birmingham, AL

Elaissa L. Hardy, PhD^1,2,3*, Brenda Williams^4*, Christopher Harden^4*, Oluwamayokun Oshinowo^5,6, Renee Copeland, BS^6*, Beatrice Gee, MD^7,8 and Wilbur A. Lam, MD, PhD^1,6,9

¹Department of Pediatrics, Division of Pediatric Hematology/Oncology, Emory University School of Medicine, Atlanta, GA
²Aflac Cancer and Blood Disorders Center of Children’s Healthcare of Atlanta, Atlanta, GA
³Emory Univeristy, Atlanta, GA
⁴Children's Healthcare of Atlanta, Atlanta, GA
⁵Medical College of Georgia, Lagrange, GA
⁶Wallace H. Coulter Department of Biomedical Engineering, Georgia Institute of Technology and Emory University, Atlanta, GA
⁷Morehouse School of Med., Atlanta, GA
⁸Children's At Hughes Spalding, Atlanta, GA
⁹Children’s Healthcare of Atlanta, Atlanta, GA

Stéphanie Forté, MD, MSc, FRCPC^1,2,3, Maryline Couette, PhD^4,5*, Damien Oudin Doglioni, PhD^6*, Denis Soulieres, MD⁷, Kevin H.M. Kuo, MD, MSc, FRCPC^1,2 and Pablo Bartolucci, MD, PhD^8,9,10*

¹Division of Medical Oncology and Hematology, Department of Medicine, University Health Network, Toronto, ON, Canada
²Division of Hematology, Department of Medicine, University of Toronto, Toronto, ON, Canada
³Medicine, Centre hospitalier de l'Université de Montréal, Montréal, QC, Canada
⁴Medicine, CHU Henri Mondor, Créteil, France
⁵Neurorehabilitation Department, Hôpital Albert Chenevier, Créteil, France
⁶CHU Henri Mondor, Créteil, France
⁷Centre hospitalier de l'Université de Montréal, Montreal, QC, Canada
⁸Sickle cell referral center, Internal Medicine Unit, Henri Mondor Hospital, Assistance Publique-Hôpitaux de Paris, Creteil, France
⁹INSERM-U955, Equipe 2, Laboratoire D'Excellence, GRex, Institut Mondor, Créteil, France
¹⁰Henri Mondor Hospital - APHP, Creteil, France