Antonio M Risitano, MD, PhD^1,2, Austin Kulasekararaj, MD, MBBS, FRCPath, MRCP^3,4,5, Alexander Röth, MD⁶, Phillip Scheinberg, MD⁷, Yasutaka Ueda^8*, Carlos de Castro^9*, Eros Di Bona^10*, Morag Griffin, FRCPath, MRCP^11*, Saskia MC Langemeijer, MD, PhD^12*, Hubert Schrezenmeier, MD^13,14, Wilma Barcellini, MD^15*, Vitor AQ Mauad, MD^16*, Jens Panse, MD^17,18, Philippe Schafhausen^19*, Suzanne Tavitian, MD^20*, Eloise Beggiato^21*, Anna Gaya^22*, Wei-Han Huang^23*, Toshio Kitawaki, MD^24*, Abdullah Kutlar, MD^25*, Jaroslaw P. Maciejewski, M.D., Ph.D., FACP²⁶, Rosario Notaro^27,28*, Vinod Pullarkat, MD²⁹, Jörg Schubert^30*, Louis Terriou, M.D^31*, Michihiro Uchiyama^32*, Flore Sicre De Fontbrune^33*, Camilla Frieri^1,2*, Ferras Alashkar^6*, Shreyans Gandhi^3*, Rakesh Kumar^34*, Christine Thorburn^35*, Samopriyo Maitra^34*, Susan Solar-Yohay^36*, Tomasz Lawniczek^37*, Marion Dahlke, MD, MSc^38* and Régis Peffault De Latour^33,39*

¹AORN Moscati, Avellino, Italy
²University of Naples Federico II, Naples, Italy
³King’s College Hospital NHS, London, United Kingdom
⁴National Institute for Health and Care Research and Wellcome King’s Research Facility, London, United Kingdom
⁵King’s College London, London, United Kingdom
⁶West German Cancer Center, University Hospital Essen, University Duisburg-Essen, Essen, Germany
⁷Hospital A Beneficência Portuguesa, São Paulo, Brazil
⁸Osaka University Graduate School of Medicine, Suita, Japan
⁹Duke University School of Medicine, Durham, NC
¹⁰UOC Oncoematologia, AULSS7 Pedemontana, Bassano del Grappa (VI), Vicenza, Italy
¹¹St James’s University Hospital, Leeds, United Kingdom
¹²Radboud University Medical Center, Nijmegen, Netherlands
¹³University of Ulm, Ulm, Germany
¹⁴German Red Cross Blood Transfusion Service Baden-Württemberg-Hessen and University Hospital Ulm, Ulm, Germany
¹⁵Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy
¹⁶ABC Medical School, Santo André, Brazil
¹⁷University Hospital RWTH Aachen, Aachen, Germany
¹⁸Center for Integrated Oncology (CIO) Aachen Bonn Cologne Düsseldorf, Aachen, Germany
¹⁹Department of Oncology, Hematology and Bone Marrow Transplantation with Section of Pneumology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany
²⁰Centre Hospitalo-Universitaire de Toulouse, Institut Universitaire du Cancer de Toulouse-Oncopole, Service d’Hématologie, Toulouse, France
²¹University of Torino, Turin, Italy
²²Hospital Clinic of Barcelona, Barcelona, Spain
²³Hualien Tzu Chi Hospital, Hualien, Taiwan
²⁴Kyoto University, Kyoto, Japan
²⁵Department of Medicine, Medical College of Georgia, Augusta, GA
²⁶Taussig Cancer Institute, Cleveland Clinic, Cleveland, OH
²⁷Azienda Ospedaliera Universitaria Careggi, Firenze, Italy
²⁸Instituto per lo Studio, la Prevenzione e la Rete Oncologica, Firenze, Italy
²⁹City of Hope National Medical Center, Duarte, CA
³⁰Elblandklinikum Riesa, Riesa, Germany
³¹CHU Lille, Université de Lille, Lille, France
³²Japanese Red Cross Society Suwa Hospital, Suwa, Japan
³³French Référence Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France
³⁴Novartis Healthcare Private Limited, Hyderabad, India
³⁵Novartis Pharmaceuticals UK Limited, London, United Kingdom
³⁶Novartis Pharmaceuticals Corporation, East Hanover, NJ
³⁷Novartis Pharma AG, Basel, Switzerland
³⁸Novartis, Basel, Switzerland
³⁹Assistance Publique Hôpitaux de Paris, Université Paris Cité, Paris, France

Fengkui Zhang^1*, Li Zhang^1*, Chen Yang^2*, Chunrong Wang^3*, Changhe Yue^3*, Hui Yan^3*, Jay Ma^4*, Helen Fu^5*, Chaomei He^5*, Ping Tsui^5*, Jingtao Wu^5*, Richard Lee^5*, Wenru Song⁵ and Bing Han^2*

¹Anemia Therapeutic Center, Institute of Hematology and Blood Diseases Hospital, CAMS & PUMC, Tianjin, China
²Peking Union Medical College Hospital, Beijing, China
³Kira Pharmaceuticals (Suzhou) Limited, Suzhou, China
⁴Kira Pharmaceuticals (US), Bethany, CT
⁵Kira Pharmaceuticals (US), Boston, MA

Oksana Karnabeda, MD^1,2*, Valentyn Moskalenko, MD, PhD^1*, Zoreslava Lysak, MD^1*, Narinder Nangia, PhD^3*, Charlotte A. Osborne^3*, J. Steve Whitaker, MD^3*, Eleni Gavriilaki, MD, PhD⁴ and Jens Panse, MD^5,6

¹Medical Centre of ARENSIA Exploratory Medicine LLC, Kyiv, Ukraine
²Bogomolets National Medical University, Kyiv, Ukraine
³Omeros Corporation, Seattle, WA
⁴G. Papanikolaou General Hospital, Thessaloniki, Greece
⁵Universitätsklinikum RWTH Aachen, Aachen, Germany
⁶Center of Integrated Oncology (CIO), Aachen, Bonn, Cologne, Düsseldorf (ABCD), Germany

Carlos M de Castro, MD¹, Brian Mulherin, MD^2,3*, Christopher J. Patriquin^4*, Veena Selvaratnam, MBBS, FRCPath^5*, Raymond SM Wong, FRCP⁶, Richard J. Kelly, BSc, MD^7*, Lisa Tan^8,9*, Peter Hillmen, MD^10*, Dale Zhang^11*, Jessica Savage^11* and Regis Peffault De Latour^12,13*

¹Department of Medicine, Duke University, Durham, NC
²Ascension St. Vincent Carmel, Carmel, IN
³Hematology Oncology of Indiana, Indianapolis, IN
⁴Division of Medical Oncology & Hematology, University Health Network, Toronto, Canada
⁵Ampang Hospital, Ampang, Malaysia
⁶The Chinese University of Hong Kong, Prince of Wales Hospital, Hong Kong, Hong Kong
⁷Department of Haematology, St. James’s University Hospital, Leeds, United Kingdom
⁸Swedish Orphan Biovitrum AB, Stockholm, Sweden
⁹Lisa Tan Pharma Consulting Ltd., Cambridge, United Kingdom
¹⁰Apellis Pharmaceuticals, Waltham, MA
¹¹Apellis Pharmaceuticals, Inc., Waltham, MA
¹²French Référence Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France
¹³Université Paris Cité, Paris, France

Alexander Röth, MD¹, Rong FU, MD^2*, Guangsheng He^3*, Hazza A Alzahrani^4*, Sheng-Chieh Chou^5*, Yosr Hicheri^6*, Maciej Kazmierczak, MD^7*, Viviane Lacorte Recova^8*, Michihiro Uchiyama^9*, ANA Maria Vladareanu^10*, Leigh Beveridge, MBBS, FRACP¹¹, Simon Buatois^12*, Muriel Buri^12*, Dayu Shi^13*, Nadiesh Balachandran^14*, Sasha Srekovic^11* and Phillip Scheinberg, MD¹⁵

¹University Hospital Essen, Essen, Germany
²tianjin medical university general hospital, TIANJIN, CHN
³3. Jiangsu Province Hospital, Nanjing, People’s Republic of China, NANJING, CHN
⁴Department of Hematology, King Faisal Specialist Hospital & Research Centre., Riyadh, Saudi Arabia
⁵Division of Hematology, Department of Internal Medicine, National Taiwan University Hospital, Taipei City, Taiwan
⁶Department of Hematology, Department of Hematology, Institut Paoli Calemettes, Marseille, France, Montpellier, FRA
⁷Maria Skłodowska-Curie National Research Institute of Oncology, Krakow, Krakow, Poland
⁸8. Chronos Clinical Research, Brasília-DF, Brazil, Brasilia, Brazil
⁹Japanese Red Cross Society Suwa Hospital, Nagano, JPN
¹⁰Department of internal medicine, 10. Department of Internal Medicine II and Gastroenterology, Emergency University Hospital, Bucharest, BUCURESTI, ROU
¹¹Genentech, Inc., South San Francisco, CA, USA, San Fransisco, CA
¹²F. Hoffmann-La Roche Ltd, Basel, Switzerland
¹³F. Hoffmann-La Roche Ltd, Basel, Switzerland, Basel, Switzerland
¹⁴F. Hoffmann-La Roche Ltd., Basel, Switzerland
¹⁵Hospital A Beneficência Portuguesa de São Paulo, Sao Paulo, SP, Brazil

Austin Kulasekararaj, MD, MBBS, FRCPath, MRCP¹, Morag Griffin, FRCPath, MRCP^2*, Caroline I Piatek, MD³, Jamile Shammo, MD⁴, Jun-Ichi Nishimura, MD, PhD⁵, Christopher J. Patriquin^6*, Hubert Schrezenmeier, MD⁷, Anna Gaya, MD^8*, Yogesh Patel^9*, Peng Liu^9*, Gleb Filippov, MD^9*, Flore Sicre De Fontbrune^10*, Antonio M Risitano, MD, PhD¹¹ and Jong-Wook Lee, MD¹²

¹King's College Hospital-NHS Foundation Trust, NIHR/Wellcome King’s Clinical Research Facility, London, United Kingdom
²Department of Haematology, Leeds Teaching Hospitals, Leeds, GBR
³University of Southern California / LAC+USC Medical Center, Los Angeles, CA
⁴Feinberg School of Medicine, Northwestern University, Chicago, IL
⁵Department of Hematology and Oncology, Osaka University Graduate School of Medicine, Osaka, Japan
⁶Division of Medical Oncology & Hematology, University Health Network, Toronto, Canada
⁷Institute of Transfusion Medicine, University of Ulm, Ulm, Germany and Institute of Clinical Transfusion Medicine and Immunogenetics Ulm, University Hospital of Ulm and German Red Cross Blood Service Baden-Württemberg-Hessen, Ulm, Germany
⁸Hospital Clínic de Barcelona, Barcelona, Spain
⁹Alexion, AstraZeneca Rare Disease, Boston, MA
¹⁰Centre de Référence Aplasie Médullaire, Service d'Hématologie Greffe, Assistance Publique des Hôpitaux de Paris, Hôpital Saint-Louis, PARIS, FRA
¹¹Federico II University of Naples and AORN Moscati, Naples, Italy
¹²Department of Hematology, Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, Seoul, Korea, Republic of (South)