-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

322.O1.6 322. Disorders of Coagulation or Fibrinolysis: Clinical and Epidemiological: Bleeding Disorder Management Throughout the Lifespan Clinically Relevant Abstract

Symposia: Disorders of Coagulation or Fibrinolysis: Clinical and Epidemiological Program: Oral and Poster Abstracts
Type: Oral
Hematology Disease Topics & Pathways:
clinical trials, Research, Bleeding and Clotting, bleeding disorders, Biological therapies, Clinical Practice (Health Services and Quality), hemophilia, Bispecific Antibody Therapy, Clinical Research, health outcomes research, patient-reported outcomes, Diseases, real-world evidence, Therapies, VWD, Infusion
Sunday, December 10, 2023: 12:00 PM-1:30 PM
Room 29 (San Diego Convention Center)
Moderators:
Genevieve Moyer, MD, MSc, and Shannon L Carpenter, MD, Children's Mercy Kansas City
Disclosures:
Carpenter: Novo Nordisk: Honoraria; genentech: Honoraria.
12:00 PM

Steven Pipe, MD1, Peter Collins2*, Christophe Dhalluin3*, Gili Kenet4,5*, Christophe Schmitt3*, Muriel Buri3*, Víctor Jiménez-Yuste, MD, PhD6*, Flora Peyvandi, Prof7,8, Guy Young, MD9, Johannes Oldenburg10, Maria Elisa Mancuso11*, Kaan Kavakli12*, Anna Kiialainen3*, Tiffany Chang13*, Michaela Lehle3, Markus Niggli3* and Karin Fijnvandraat14*

1University of Michigan, Ann Arbor, MI
2School of Medicine, Cardiff University, Cardiff, United Kingdom
3F. Hoffmann-La Roche Ltd, Basel, Switzerland
4Sheba Medical Center, Ramat Gan, Israel
5Tel Aviv University, Tel Aviv, Israel
6La Paz University Hospital Idi-Paz, Autónoma University, Madrid, Spain
7Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milan, Italy
8Università degli Studi di Milan, Milan, Italy
9Children's Hospital Los Angeles, Los Angeles, CA
10University of Bonn, Bonn, Germany
11IRCCS Humanitas Research Hospital and Humanitas University, Rozzano, Italy
12Ege University Faculty of Medicine Children's Hospital, Izmir, Turkey
13Spark Therapeutics, Inc., South San Francisco, CA
14University of Amsterdam, Amsterdam, Netherlands

12:15 PM

Flora Peyvandi, Prof1, Cristina Tarango2, Mindy Simpson3*, Manuela Albisetti4*, Maria Teresa Álvarez-Roman5*, Anthony KC Chan, MBBS6, Julie Curtin7*, Linda Bystrická8*, Elena Santagostino9, Ekaterina Gresko9*, Sriya Gunawardena10*, Chandravathi Vage11* and Nancy Wong11*

1Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy
2Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, OH
3Rush University Medical Center, Rush Hemophilia and Thrombophilia Center, Chicago, IL
4Department of Hematology, University Children's Hospital, Zurich, Switzerland
5Hospital Universitario La Paz, Autonoma University of Madrid, IdiPAZ, Madrid, Spain
6McMaster Children's Hospital, McMaster University, Hamilton, ON, Canada
7The Children's Hospital at Westmead, Sydney, NSW, Australia
8Sobi, Stockholm, Sweden
9Sobi, Basel, Switzerland
10Sanofi, Bridgewater
11Sanofi, Bridgewater, NJ

12:30 PM

Lynn Malec, MD1,2, Manuel Carcao, MD, FRCP(C)3*, Mary Mathias4*, Nana Kragh, MSc5*, Jennifer Dumont, PhD6, Annemieke Willemze, MD7, Linda Bystrická5*, Amanda Wilson6* and Dana Dibenedetti8*

1Versiti Blood Research Institute, Milwaukee, WI
2Department of Pediatrics, Medical College of Wisconsin, Milwaukee, WI
3Division of Hematology/Oncology, Department of Pediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
4Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom
5Swedish Orphan Biovitrum AB, Stockholm, Sweden
6Sanofi, Cambridge, MA
7Sanofi, Amsterdam, NLD
8RTI Health Solutions, Research Triangle Park, NC

12:45 PM

Allison P Wheeler, MD1, John Waller2*, Sanket Shah3*, Mohd Nawi bin Wahid2*, Jennifer Dusendang4* and Amy D. Shapiro, MD5

1Department of Pathology, Microbiology, and Immunology, The Vanderbilt University, Nashville, TN
2Novo Nordisk Health Care AG, Zurich, Switzerland
3Novo Nordisk Inc, Palo Alto
4PicnicHealth, San Francisco, CA
5Indiana Hemophilia & Thrombosis Center, Inc., Indianapolis, IN

1:00 PM

Ferdows Atiq, MD, MSc, PhD1,2,3, Robin Blok4*, Calvin Van Kwawegen4*, Dearbhla Doherty1*, Michelle Lavin, MD, PhD, FRCPath5,6*, Johanna G. Van Der Bom, MD, PhD7*, Niamh O'Connell8*, Joke De Meris9*, Kevin Ryan8*, Saskia Schols10*, Mary Byrne8*, Floor Moenen11*, Karin PM Van Galen, MD, MSc12*, Roger J.S Preston, PhD5*, Karin Fijnvandraat13,14*, Ross Baker, MBBS15,16*, Karina Meijer, MD, PhD17*, Paula James, MD, FRCPC18, Jorge Di Paola, MD19, Jeroen Eikenboom, MD, PhD20, Frank W.G. Leebeek, MD, PhD4 and James S. O'Donnell1,8,16*

1Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Dublin, Ireland
2Royal College of Surgeons In Ireland, Dublin, Ireland
3Erasmus MC-University Medical Center, Rotterdam, Netherlands
4Department of Haematology, Erasmus University Medical Center-Erasmus MC, Rotterdam, Rotterdam, Netherlands
5Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland (RCSI), Dublin, Ireland
6National Coagulation Centre, St James’s Hospital, Dublin, Ireland
7Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, Leiden, Netherlands
8National Coagulation Centre, St James’s Hospital, Dublin, Dublin, Ireland
9NVHP, Zoetermeer, Netherlands
10Department of Hematology, Radboud university medical center, Nijmegen, Netherlands
11Department of Hematology, Maastricht University Medical Center, Maastricht and Hemophilia Treatment Center Nijmegen-Eindhoven-Maastricht, Maastricht, Netherlands
12Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Utrecht, Netherlands
13Department of Blood Cell Research, Sanquin Research and Landsteiner Laboratory, Amsterdam, Netherlands
14University of Amsterdam, Amsterdam, Netherlands
15Perth Blood Institute, Murdoch University, Perth, Australia
16Irish-Australian Blood Collaborative (IABC) Network, Dublin, Ireland
17Department of Hematology, University Medical Center Groningen, Groningen, Groningen, Netherlands
18Division of Hematology, Department of Medicine, Queen's University, Kingston, ON, Canada
19Department of Pediatrics, Washington University School of Medicine, St Louis, MO
20Leiden Univ. Medical Center, Leiden, Netherlands

1:15 PM

Ferdows Atiq, MD, MSc, PhD1,2, Robin Blok3*, Calvin Van Kwawegen3*, Dearbhla Doherty2*, Michelle Lavin, MD, PhD, FRCPath4,5*, Johanna G. Van Der Bom, MD, PhD6*, Niamh O'Connell7*, Joke De Meris8*, Kevin Ryan7*, Saskia Schols9*, Mary Byrne7*, Floor Moenen10*, Karin PM Van Galen, MD, MSc11*, Roger J.S Preston, PhD4*, Karin Fijnvandraat12,13*, Ross Baker, MBBS14,15*, Karina Meijer, MD, PhD16*, Paula James, MD, FRCPC17, Jorge Di Paola, MD18, Jeroen Eikenboom, MD, PhD19, James S. O'Donnell2,7,15* and Frank W.G. Leebeek, MD, PhD3

1Royal College of Surgeons In Ireland, Dublin, Ireland
2Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Dublin, Ireland
3Department of Haematology, Erasmus University Medical Center-Erasmus MC, Rotterdam, Rotterdam, Netherlands
4Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland (RCSI), Dublin, Ireland
5National Coagulation Centre, St James’s Hospital, Dublin, Ireland
6Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, Leiden, Netherlands
7National Coagulation Centre, St James’s Hospital, Dublin, Dublin, Ireland
8NVHP, Zoetermeer, Netherlands
9Department of Hematology, Radboud university medical center, Nijmegen, Netherlands
10Department of Hematology, Maastricht University Medical Center, Maastricht and Hemophilia Treatment Center Nijmegen-Eindhoven-Maastricht, Maastricht, Netherlands
11Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Utrecht, Netherlands
12Department of Blood Cell Research, Sanquin Research and Landsteiner Laboratory, Amsterdam, Netherlands
13University of Amsterdam, Amsterdam, Netherlands
14Perth Blood Institute, Murdoch University, Perth, Australia
15Irish-Australian Blood Collaborative (IABC) Network, Dublin, Ireland
16Department of Hematology, University Medical Center Groningen, Groningen, Groningen, Netherlands
17Division of Hematology, Department of Medicine, Queen's University, Kingston, ON, Canada
18Department of Pediatrics, Washington University School of Medicine, St Louis, MO
19Leiden Univ. Medical Center, Leiden, Netherlands

*signifies non-member of ASH