Alexandra Forman, BSc^1*, Laura Dodge, ScD^2*, Thita Chiasakul, MD^3*, Sirui Ma, MD⁴, Jeffrey I. Zwicker, MD^5,6, Ellen McCarthy, PhD, MPH^2* and Rushad Patell, MD⁷

¹Harvard Medical School, Cambridge, MA
²Beth Israel Deaconess Medical Center, Boston, MA
³Center of Excellence in Translational Hematology, Division of Hematology, Department of Medicine, Faculty of Medicine, Chulalongkorn University and King Chulalongkorn Memorial Hospital, Bangkok, Thailand
⁴Division of Hematology and Oncology, University of California, San Francisco, San Francisco, CA
⁵Weill Cornell Medical College, New York, NY
⁶Memorial Sloan Kettering Cancer Center, New York, NY
⁷Division of Hematology/Oncology, Beth Israel Deaconess Medical Center, Boston, MA

Stefan W Eber, MD¹, Andreas Glenthøj, MD, PhD^2*, Bertil Glader, MD, PhD³, Dagmar Pospisilova, MD, PhD^4*, Eduard J. van Beers, MD, PhD⁵, Rachael F. Grace, MD, MMSc⁶, Joan-Lluis Vives Corrons, MD, PhD^7*, Hitoshi Kanno, MD, PhD^8*, Kevin H.M. Kuo, MD, MSc, FRCPC⁹, Paola Bianchi, PhD, BSc¹⁰, Audra Boscoe, PhD^11*, Bryan McGee, PharmD, MBA^11*, Yan Yan, MS^11*, Junlong Li, PhD^11*, Janet H. Ford, MPH, PhD^11* and Carl Lander, RN^12*

¹Special Practice for Pediatric Hematology/Oncology and Children`s Hospital, Technical University, Munich, Germany
²Danish Red Blood Cell Center, Department of Hematology, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark
³Division of Pediatric Hematology/Oncology, Stanford University School of Medicine, Palo Alto, CA
⁴Department of Pediatrics, Faculty of Medicine and Dentistry, Palacky University and University Hospital Olomouc, Olomouc, Czech Republic
⁵Center for Benign Hematology, Thrombosis and Hemostasis - Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, Netherlands
⁶Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA
⁷Red Blood Cell and Haematopoietic Disorders Research Unit, Institute for Leukaemia Research Josep Carreras, Barcelona, Spain
⁸Department of Transfusion Medicine and Cell Processing, Tokyo Women's Medical University, Tokyo, JPN
⁹Division of Hematology, University of Toronto, Toronto, ON, Canada
¹⁰Hematology Unit, Pathophysiology of Anemias Unit, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milano, Italy
¹¹Agios Pharmaceuticals, Inc., Cambridge, MA
¹²Thrive with PK Deficiency, Minneapolis, MN

Marie-Claude Pelland-Marcotte, MD, PhD¹, Alexandra Larouche, MD^1*, Valerie Dollo, MD^1*, Gabriel Mercier, MD^1*, Mahukpe Narcisse U. Singbo, MSc^2*, Chantal Ethier, PhD^2* and Marie-Christine Boulanger, PhD^1*

¹CHU de Québec - Université Laval, Québec, QC, Canada
²Centre de Recherche du CHU de Québec, Québec, QC, Canada

Susan Lattimore, BSN^1*, Eleanor Carrick, MS^1*, Heather MacFarlane, BA^1*, Virginie Sirianna, MHA^2* and Nicole Crook, RN^3*

¹The Hemostasis & Thrombosis Center, Oregon Health & Science University, Portland, OR
²UNC Hemophilia & Thrombosis Center, University of North Carolina School of Medicine, Chapel Hill, NC
³Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders, Orange, CA

Amy D. Shapiro, MD¹, Robert Schuldt, PhD^2*, Zhiyu Xia, PhD^2*, Carmen Ng, PhD^2*, Lucy Lee, PharmD, MPH^2*, Juliana M.L. Biondo, MD² and Janet S Lee^2*

¹Indiana Hemophilia & Thrombosis Center, Indianapolis, IN
²Genentech, Inc., South San Francisco, CA

Srikanth Nagalla, MBBS¹, Moshe Y. Levy, MD^2*, Shruti Chaturvedi, MBBS³, Scott Kolodny, MD^4*, Abiola Oladapo^5*, Chelsea Bernheisel^4*, Elyse Swallow^6*, Debbie Goldschmidt, PhD^7*, Ali Greatsinger^7*, Kirthana Sarathy^7*, Loren Ormenaj^7* and Michael Vredenburg, PhD^4*

¹Miami Cancer Institute, Miami, FL
²Texas Oncology-Baylor Charles A. Sammons Cancer Center, Dallas, TX
³Division of Hematology, Department of Medicine, Johns Hopkins Hospital, BALTIMORE, MD
⁴Sobi, Inc., Durham, NC
⁵Sobi Inc., Waltham, MA
⁶Analysis Group, Inc., Boston, MA
⁷Analysis Group, Inc., New York, NY

Fartoon M Siad, MD, MSc¹, Andrea Lausman, MD^2*, Carolyn Snider, MD^3*, Martina Trinkaus, MD^4*, Filomena Meffe, MD, MSc^2* and Michelle Sholzberg, MD, M.Sc⁵

¹Department of Medicine, University of Toronto, Toronto, ON, Canada
²Department of Obstetrics and Gynecology, University of Toronto, Toronto, Canada
³Department of Emergency Medicine, University of Toronto, Toronto, Canada
⁴Deparment of Medicine, University of Toronto, Toronto, ON, CAN
⁵Departments of Medicine, and Laboratory Medicine and Pathobiology, St. Michael’s Hospital, Li Ka Shing Knowledge Institute, University of Toronto, Toronto, ON, Canada

Christopher P Keuker, MD^1*, Daniel A. Mazzolenis, MD, MBA² and Ana Baptista, MD^3*

¹Medical and Scientific Management, Syneos Health, Morrisville, NC
²Syneos Health, Morrisville, NC
³Syneos Health, Lisbon, Portugal

Qiusha Huang, MD^1*, Xiaolu Zhu^1*, Yun He^2*, HaiXia Fu, MD^1*, Qi Chen^3*, Peng Zhao^1*, Jin Wu, MD^4*, YingJun Chang, MD, PhD^5*, LanPing Xu, MD^6*, Xue Xu^7*, Xiaohong Zhang^8*, Jianliu Wang^8*, Xiaojun Huang^9* and Xiaohui Zhang, MD^10,11

¹Peking University People's Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing Key Laboratory of Hematopoietic Stem Cell Transplantation, Beijing, China
²Peking University People's Hospital, Peking University Institute of Hematology, Beijing, China
³Peking University People’s Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing, China
⁴Peking University People's Hospital, Beijing, CHN
⁵Peking University People's Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing, China
⁶Peking University People’s Hospital,Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing, China
⁷Department of Obstetrics and Gynecology, Peking University People's Hospital, Beijing, China, Beijing, China
⁸Department of Obstetrics and Gynecology, Peking University People's Hospital, Beijing, China
⁹Peking University People's Hospital & Peking University Institute of Hematology,, Beijing, CHN
¹⁰Peking University People’s Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing Key Laboratory of Hematopoietic Stem Cell Transplantation, Beijing, China
¹¹Peking University People's Hospital, Beijing, China

Karlyn A. Martin, MD, MS¹, Andrew Sparks, MS^2*, Katherine Wilkinson, MS^3*, Ryan Packer^4*, Deirdra R Terrell, PhD⁵, Mansour Gergi, MD⁶, Augusto Ferraris, MD MPH^7*, William A. Wood, MD, MPH⁸, Allen B Repp, MD MSc^9*, Nicholas S Roetker, PHD MS^10* and Neil Zakai⁶

¹Division of Hematology and Oncology, University of Vermont Larner College of Medicine, Burlington, VT
²Biomedical Statistics Research Core at the University of Vermont, Burlington, VT
³University of Vermont Larner College of Medicine, Burlington, VT
⁴Biostatistics Core, Laboratory for Clinical Biochemistry Research, University of Vermont Larner College of Medicine, Burlington, VT
⁵University of Oklahoma Health Sciences Ctr, Oklahoma City, OK
⁶Larner College of Medicine at the University of Vermont, Burlington, VT
⁷University of Washington, Ciudad Autonoma De Buenos Aires, BA, ARG
⁸Division of Hematology/Oncology, Department of Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC
⁹University of Vermont, Burlington, VT
¹⁰Chronic Disease Research Group, Hennepin Healthcare Research Institute, Minneapolis, MN

Caroline Piatek, MD¹, Louis A Jackson III, PharmD^2*, Caroline Brethenoux^3*, Alyssa DeLuca^3*, Zia Choudhry, MD, PhD, MBA^4*, Jacqueline Pesa, MSEd, PhD, MPH^4*, Alex Lorenzo, BBA^3*, Patrick Furey, MS^3*, Laura Gonzalez Quijano^3*, Rosario Alvarez^3*, Julija Paskevicius^3* and Nora Sandorfi, MD^5*

¹Jane Anne Nohl Division of Hematology and Center for the Study of Blood Diseases, USC Norris Comprehensive Cancer Center, Los Angeles, CA
²Janssen Scientific Affairs, LLC, Horsham, PA
³Human Dot Plus, Dallas, TX
⁴Janssen Scientific Affairs, LLC, Titusville, NJ
⁵Division of Rheumatology, University of Pennsylvania, Philadelphia, PA

David Araten, MD¹, Austin G. Kulasekararaj, MD, MBBS, FRCPath, MRCP², Jun-ichi Nishimura, MD, PhD³, Regis Peffault De Latour^4*, Ilene C. Weitz, MD⁵, Azalea Candelaria^6*, Aliza Fink, D.Sc.^7*, Alice Houk, MS^6*, Elizabeth W Kottke, MPH, CPH, CHES^7* and Brad A Wong^6*

¹NYU Cancer Institute, New York, NY
²King’s College Hospital-NHS Foundation Trust, NIHR/Wellcome King’s Clinical Research Facility, and King’s College London, London, United Kingdom
³Osaka University Graduate School of Medicine, Osaka, Japan
⁴BMT unit, Hôpital Saint-Louis,, Paris, France
⁵Division of Hematology, Keck School of Medicine of USC, Los Angeles, CA
⁶Aplastic Anemia & MDS International Foundation, Rockville, MD
⁷National Organization for Rare Diseases, Quincy, MA

Steven Fein, MD, MPH¹, Dayne Alonso, PA-C^1*, Gloria Campos^1*, Adam K Lewkowitz, MD, MPHS^2*, Layla N Van Doren, MD, MBA³, Michael Auerbach, MD⁴, Gina Peralta^5* and Nicole Peralta^5*

¹Heme On Call, a telemedicine hematology medical practice, Miami, FL
²Department of Obstetrics and Gynecology, Brown University, Providence, RI
³Section of Hematology, Division of Medicine, Yale School of Medicine, New Haven, CT
⁴Auerbach Hematology and Oncology, Baltimore, MD
⁵GNP Research, Hollywood, FL

Gohul Gopi Jalajakumari, MD DNB^1*, Manoj Unni, MD DM^2*, Vidya Jha, MD^3*, Bindhu Paul-Prasanth, PhD^4*, Amal Nandu^5*, Rema Ganapathy, MBBS, DNB^6*, Monisha Harimadhavan, MD, DNB, DrNB^7*, Gayathri Sajeevan, MD^8*, Akhila M, BSc^9*, Georg Gutjahr^10*, Anandkrishnan N^11*, Syamaprasad Vinayakumar, Pharm D^12*, Ullas Mony, PhD^13* and Neeraj Sidharthan, MD, MBBS, DM, DNB¹⁴

¹Department of Clinical Haematology, Amrita Institute of Medical Sciences, Amrita Vishwa Vidyapeetham, Cochin, Kerala, India
²Amrita institute of Medical sciences, Amrita Vishwa Vidyapeetham, Kochi, India
³Department of Cytogenetics, Amrita Institute of Medical Sciences and Research Centre, Amrita Vishwa Vidyapeetham, ERNAKULAM, AL, India
⁴Amrita Institute of Medical Sciences, Amrita Vishwa Vidyapeetham, kochi, India
⁵Amrita Institute of Medical Sciences, Amrita Vishwa Vidyapeetham, Kochi, India
⁶Department of Clinical Haematology, Amrita Institute of Medical Sciences , Amrita Viswa Vidyapeetam, Ernakulam, India
⁷Amrita Institute of Medical Sciences , Amrita Viswa Vidyapeetam, Kochi, India
⁸Amrita institute of medical science, Kochi, IND
⁹Department of Clinical Haematology , Transplant and Cellular Therapy, Amrita institute of Medical sciences, Amrita Vishwa Vidyapeetham, Kochi, Kerala, India
¹⁰Department of Health Science Research, Amrita Institute of Medical Sciences, Kochi, India, Kochi, India
¹¹Amrita school of Physical Sciences, Amita viswa vidyapeetam, Kochi, India
¹²Department of Clinical Haematology, Amrita institute of Medical sciences, Amrita Vishwa Vidyapeetham, Kochi, Kerala, India
¹³Centre of Molecular Medicine and Diagnostics (COMManD), Saveetha Dental College and Hospitals, Saveetha Institute of Medical and Technical Sciences, Saveetha University, Chennai, India
¹⁴Department of Clinical Haematology, Transplant and Cellular Therapy , Amrita Institute of Medical Sciences and Research Centre, Co-Director Amrita Amyloid Center, Amrita Vishwa Vidyapeetham, Kochi, India

Zulisa Saripuddin^1*, Tze Yen Loo^1*, Boey Yee Cheng^1*, Aine Kyle, PhD^2* and Ayse Levent, MSc^3*

¹Ipsos, Kuala Lumpur, Malaysia
²Ipsos, Maynooth, Ireland
³Ipsos, New York, NY

Adebimpe Adelaja, BS^1*, Joseph R Stanek, MS^2,3*, Meghan Pike, MD^4*, Victoria E. Price, MBChB, MSc^4* and Sarah H. O'Brien, MD, MSc^2,5,6

¹Center for Child Health Equity and Outcomes Research, The Abigail Wexner Research Institute, Nationwide Children's Hospital, Canal Winchester, OH
²Division of Pediatric Hematology/Oncology/BMT, Nationwide Children's Hospital, Columbus, OH
³Biostatistics Resource at Nationwide Children's Hospital, Columbus, OH
⁴Division of Pediatric Hematology Oncology, Department of Pediatrics, Dalhousie University, IWK Health Centre, Halifax, NS, Canada
⁵Department of Pediatrics, Ohio State University, Columbus, OH
⁶Center for Child Health Equity and Outcomes Research, The Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus, OH

Bhavisha A. Patel, MD¹, Emma M. Groarke, MD¹, Ruba Shalhoub^2*, Fernanda Rodrigues, PhD^3*, Alice Fike, PA-C^4*, Kaitlin Quinn, MD^4*, Ivana Darden, RN^1*, Shanni Liu, RN^5*, Wendy Goodspeed, RN^4*, Rui Miao^6*, Colin O. Wu, PhD^2*, Neal S. Young, MD¹ and Peter C Grayson, MD^4*

¹Hematology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
²Office of Biostatistics Research, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
³Hematology Branch, National Heart Lung and Blood Institutes, National Institutes of Health, Bethesda
⁴NIAMS, National Institutes of Health, Bethesda, MD
⁵NIAMS, National Institutes of Health, Bethesda
⁶Office of Biostatistical Research, National Heart Lung and Blood Institute, Bethesda

Jonathan Tucci, MD, PhD^1* and Allison P Wheeler, MD/MSCI^2,3

¹Vanderbilt University Medical Center, Nashville, TN
²University of Washington, Washington Center for Bleeding Disorders, Seattle, WA
³University of Washington, Seattle, WA

Zhengyi Cheng^1,2*, Ziyue Zhang^1,2*, Li Zhou, MD^1,2*, Guojing Yuan^1,2*, Mengyue Zhang^1,2*, Haihao Shen^1,2*, Xia Niu^3* and Zhimin Zhai, MD^1,2

¹Department of Hematology, the Second Affiliated Hospital of Anhui Medical University, Hefei, China
²Anhui Medical University, Hefei, China
³School of Nursing, Anhui Medical University, Hefei, China