Janice Staber, MD¹, Alix Arnaud, MS^2*, Ion Agirrezabal, MSc/PhD^3*, Lane Anson, PharmD/MBA/RPh^4*, Andrew Wilson, MS^4*, Nana Kragh, MSc^5*, Doris V. Quon, MD, PhD⁶ and Allison P Wheeler, MD/MSCI⁷

¹Pediatrics, University of Iowa Stead Family Children's Hospital, Iowa City, IA
²Sanofi, Boston, MA
³Sanofi, Barcelona, Spain
⁴Sanofi, Cambridge, MA
⁵Sobi, Stockholm, Sweden
⁶Orthopaedic Institute for Children, Orthopaedic Hemophilia Treatment Center, Los Angeles, CA
⁷University of Washington, Washington Center for Bleeding Disorders, Seattle, WA

Midori Shima¹, Katsuyuki Fukutake^2*, Masanori Matsumoto³, Yoshihiko Sugimura^4*, Chiaki Sugita^4*, Lyu Ji^4*, Mika Kawano^5* and Tadashi Matsushita, MD⁶

¹Thrombosis and Hemostasis Research Center and Department of Pediatrics, Nara Medical University, Kashihara, Japan
²Department of Blood Coagulation, Ogikubo Hospital, Tokyo, Japan
³Department of Blood Transfusion Medicine and Department of Hematology, Nara Medical University, Kashihara, Japan
⁴Drug Safety Division, Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
⁵Medical Affairs Division, Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
⁶Nagoya University Hospital, Nagoya, Japan

Valentina Restrepo, MD¹, Stephanie Prozora, MD², Evangelia Louizos^3*, Layla N Van Doren, MD, MBA⁴ and Robert D Bona, MD⁵

¹Section of Hematology, Yale University School of Medicine, New Haven, CT
²Department of Pediatric Hematology & Oncology, Yale University School of Medicine, New Haven, CT
³Hematology Section, Yale School of Medicine, New Haven, CT
⁴Section of Hematology, Division of Medicine, Yale School of Medicine, New Haven, CT
⁵Classical Hematology, Section of Hematology, Yale University School of Medicine, New Haven, CT

Allison P. Wheeler, MD¹, Aby Abraham, MD, DM^2*, Chris Barnes^3*, Renée Brown Frandsen^4*, Kingsley Hampton^5*, Francisco José López Jaime, MD^6*, Camila Martins Mazini Tavares^4*, Keiji Nogami^7*, Jerzy Windyga, MD, PhD⁸ and Giancarlo Castaman^9*

¹Washington Center for Bleeding Disorders, Seattle, WA
²Department of Haematology, Christian Medical College Ranipet Campus, Ranipet, India
³The Royal Children’s Hospital, Melbourne, VIC, Australia
⁴Novo Nordisk A/S, Søborg, Denmark
⁵Department of Cardiovascular Science, University of Sheffield, Sheffield, ENG, GBR
⁶Hemostasis and Thrombosis Unit, Málaga Regional University Hospital, IBIMA, Málaga, Spain
⁷Department of Pediatrics, Nara Medical University, Nara, Japan
⁸Laboratory of Hemostasis and Metabolic Diseases, Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
⁹Center for Bleeding Disorders, Department of Oncology, Careggi University Hospital, Florence, Italy

Zhexi Lu, MD^1* and Nicoletta C Machin, DO^2,3

¹Department of Medicine, University of Pittsburgh Medical Center, Pittsburgh, PA
²Division of Classical Hematology, Department of Medicine, University of Pittsburgh, Pittsburgh, PA
³Hemophilia Center of Western Pennsylvania, Pittsburgh, PA

Aikaterini Michalopoulou, MD^1*, Anna Kouramba, MD^2*, Aimilia Mantzou, PhD^3*, Styliani-Despoina Christidi, MD^4*, Athina Dettoraki, MD, PhD^1*, George Thivaios, MD^4*, Zoey Kapsimali, PhD^1*, Olga Katsarou Fasouli, MD, PhD^2*, Ioannis Papassotiriou, PhD⁵ and Helen Pergantou, MD, PhD^1*

¹Haemophilia Centre/Haemostasis and Thrombosis Unit - Aghia Sophia Children's Hospital, Athens, Greece
²Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Laiko General Hospital, Athens, GRC
³First Department of Pediatrics, National and Kapodistrian University of Athens, School of Medicine, Athens, Greece
⁴Trauma and Orthopaedics Department, Laiko General Hospital, Athens, Greece
⁵First Department of Pediatrics, National and Kapodistrian University of Athens, School of Medicine, Athens, Attica, Greece

Azusa Nagao^1*, Keiji Nogami^2*, Nobuaki Suzuki^3*, Chiai Nagae^4*, Masahiko Ando^5*, Yachiyo Kuwatsuka, MD PhD^5*, Daisuke Nosaka^6*, Yui Kyogoku^6*, Tomomi Shimura^6* and Tadashi Matsushita, MD⁵

¹Department of Pediatrics, Ogikubo Hospital, Tokyo, Japan
²Nara Medical University, Nara, Japan
³Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
⁴Department of Pediatrics, St Marianna University School of Medicine, Kanagawa, Japan
⁵Nagoya University Hospital, Nagoya, Japan
⁶Chugai Pharmaceutical Co., Ltd., Tokyo, Japan

Guy Young, MD¹, Katherine Eakle^2*, Elise Lim^2* and Michael Wang^3*

¹Children's Hospital Los Angeles, Los Angeles, CA
²Genentech, Inc., South San Francisco, CA
³University of Colorado Anschutz Medical Campus, Aurora, CO

Randolph Leiser, PhD^1*, Chanchala Kaddi^2*, Mengdi Tao, MS^1*, Ane Salvador, PhD^3*, Ekta Seth Chhabra, PhD, MSc^4* and Susana Zaph, PhD^1*

¹Translational Disease Modelling, Data and Data Science, Sanofi, Bridgewater, United States, Bridgewater
²Sanofi, Cambridge, MA
³Rare and Neurologic Diseases, Sanofi, Cambridge, United States, Cambridge
⁴Global Research Lead, Rare and Neurologic Diseases, Sanofi, Cambridge

Hui Lu, PhD^1*, Jenny Whitty, PhD^1*, Travis Gould, PhD², Carmine Colavecchia, PhD, PharmD^2*, Josh Coulter, MA^2*, Nicola Dunn, BCA, Psych Dip^3*, Pratima Chowdary, MD, MRCP, FRCPath^4*, Lisa J Wilcox, PhD^5*, Joseph C. Cappelleri, PhD^6*, Stephanie A Christopher, MA^2*, Alexis Sohn, PharmD, MPH, MS^2* and Brett Hauber, PhD^2*

¹Evidera, London, United Kingdom
²Pfizer Inc, New York, NY
³Independent Consultant, London, United Kingdom
⁴Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, United Kingdom
⁵Senior Director – Global Medical Affairs at Pfizer, Pfizer, Toronto, ON, Canada
⁶Pfizer Inc, Groton, CT

Craig Kessler, MD¹, Fernando F Corrales-Medina, MD², Pier Mannuccio Mannucci^3* and Michael D Tarantino, MD⁴

¹Lombardi Comprehensive Cancer Center, MedStar Georgetown University Hospital, Washington, DC
²Division of Pediatric Hematology-Oncology, University of Miami-Miller School of Medicine-Sylvester Cancer Center, Miami, FL
³Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi, Hemophilia and Thrombosis Center, IRCCS Ca' Granda Foundation, Milano, Italy
⁴Bleeding and Clotting Disorders Institute, Peoria, IL

Martin Chandler^1*, Jessica Charlet, PhD, MSc, BSc^2* and Tammuella Chrisentery-Singleton, MD¹

¹American Thrombosis and Hemostasis Network, Rochester, NY
²Bayer US LLC Pharmaceuticals, Whippany, NJ

Steven W. Pipe, MD¹, Mark T Reding, MD², Bryan Chin^3*, Karen Campbell^3*, Hanlan Liu, PhD^3* and Wing Yen Wong, MD³

¹University of Michigan, Ann Arbor, MI
²Center for Bleeding and Clotting Disorders, University of Minnesota Medical Center, Minneapolis, MN
³Be Biopharma, Cambridge, MA