Stacey Rifkin-Zenenberg, DO¹, Julie Kanter, MD², Melissa A. Kinney^3*, Janet L. Kwiatkowski, MD^4,5, Robert S. Nickel, MD, MSc⁶, Mark C. Walters, MD^7*, Suhag Parikh, MD^8*, Alexis Thompson, MD, MPH^5,9, Anil P. George^10*, Markus Mapara, MD, PhD^11*, Paul L. Martin, MD, PhD¹², Anjulika Chawla, MD³, Ankit Lodaya, MS^3*, Lin Pan^3*, Emily Sheldon-Waniga, PhD^3*, Francis J. Pierciey Jr., MSc^3*, John Tisdale, MD¹³ and Ashish O. Gupta, MBBS, MPH¹⁴

¹Pediatric Hematology/Oncology Division, Hackensack University Medical Center, Hackensack, NJ
²University of Alabama at Birmingham, Birmingham, AL
³bluebird bio, Inc., Somerville, MA
⁴Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
⁵Children's Hospital of Philadelphia, Philadelphia, PA
⁶Children's National Hospital, Washington, DC
⁷University of California, San Francisco Benioff Children’s Hospital, Oakland, CA
⁸Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Emory University, Atlanta, GA
⁹Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
¹⁰Baylor College of Medicine, Houston, TX
¹¹Columbia Center for Translational Immunology, Columbia University Irving Medical Center, New York, NY
¹²Duke University, Durham, NC
¹³National Heart, Lung, and Blood Institute and National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD
¹⁴University of Minnesota, Minneapolis, MN

Franco Locatelli, MD¹, Peter Lang, MD^2*, Roland Meisel, MD^3*, Donna Wall, MD⁴, Selim Corbacioglu, MD, PhD⁵, Amanda M Li, MD⁶, Josu de la Fuente, PhD FRCP⁷, Ami J. Shah, MD⁸, Ben Carpenter, MD^9*, Janet L. Kwiatkowski, MD¹⁰, Markus Y Mapara, MD¹¹, Robert I. Liem, MD¹², Maria Domenica Cappellini, MD¹³, Mattia Algeri, MD^14*, Antonis Kattamis, MD¹⁵, Sujit Sheth, MD¹⁶, Stephan A. Grupp, MD, PhD¹⁰, Hayley Lynne Merkeley¹⁷, Kevin H.M. Kuo, MD, MSc, FRCPC¹⁸, Joachim Rupprecht^2*, Puja Kohli, MD, MMSc^19*, Gang Xu^19*, Leorah Ross, MD, PhD^19*, Yael Bobruff, PhD^19*, Bo Tong^19*, William Hobbs, MD, PhD¹⁹ and Haydar Frangoul, MD²⁰

¹IRCCS, Ospedale Pediatrico Bambino Gesù Rome, Catholic University of the Sacred Heart, Rome, Italy
²University of Tübingen, Tübingen, Germany
³Division of Pediatric Stem Cell Therapy, Department of Pediatric Oncology, Hematology and Clinical Immunology, Medical Faculty, Heinrich-Heine-University, Duesseldorf, Germany
⁴The Hospital for Sick Children/University of Toronto, Toronto, Canada
⁵University of Regensburg, Regensburg, Germany
⁶BC Children’s Hospital, University of British Columbia, Vancouver, BC, Canada
⁷Imperial College Healthcare Trust, St Mary's Hospital, London, United Kingdom
⁸Stanford University, Palo Alto, CA
⁹University College London Hospitals NHS Foundation Trust, London, United Kingdom
¹⁰Children’s Hospital of Philadelphia and Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
¹¹Division of Hematology/Oncology, Columbia University, New York, NY
¹²Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
¹³University of Milan, Milan, Italy
¹⁴IRCCS, Ospedale Pediatrico Bambino Gesù Rome, Magna Graecia University of Catanzaro, Catanzaro, Italy
¹⁵National and Kapodistrian University of Athens, Athens, Greece
¹⁶Joan and Sanford I Weill Medical College of Cornell University, New York, NY
¹⁷Department of Medicine, The University of British Columbia, Vancouver, Canada
¹⁸Division of Hematology, University of Toronto, Toronto, ON, Canada
¹⁹Vertex Pharmaceuticals Incorporated, Boston, MA
²⁰Sarah Cannon Research Institute at the Children's Hospital at TriStar Centennial, Nashville, TN

Ashish O. Gupta, MBBS, MPH¹, Akshay Sharma, MBBS², Haydar Frangoul, MD³, Jignesh Dalal, MD^4*, Julie Kanter, MD⁵, Asif Alavi, MD^6*, John DiPersio, MD, PhD^7*, Mary Eapen, MBBS, MS⁸, Jennifer J. Jaroscak, MD⁹, Ernesto Ayala, MD¹⁰, Edward D. Ziga, MD, MPH^11*, Stacey Rifkin-Zenenberg, DO¹², Alex C. Minella, MD¹³, Guo Chen, PhD^13*, Yinzhong Chen, PhD^13*, Priya S. Chockalingam, PhD^13*, Ling Lin, PhD^13*, Marcelyne Joseney-Antoine^13*, Leanne Ianniello, MPH^13*, Beth Gardner, BSc, EMBA, PMP^13*, Adam J. Hartigan, PhD^13*, Giuseppe Ciaramella, PhD, BSc^13*, Sunita Goyal, MD^13*, Amy Simon, MD^13*, Alexis Thompson, MD, MPH¹⁴ and Matthew M. Heeney, MD¹⁵

¹Division of Pediatric Blood and Marrow Transplant and Cellular Therapies, University of Minnesota, Minneapolis, MN
²Department of Bone Marrow Transplantation and Cellular Therapy, St. Jude Children's Research Hospital, Memphis, TN
³Sarah Cannon Research Institute at the Children's Hospital at TriStar Centennial, Nashville, TN
⁴Division of Hematology and Bone Marrow Transplant, Rainbow Babies & Children’s Hospital, Cleveland, OH
⁵Division of Hematology and Oncology, University of Alabama at Birmingham, Birmingham, AL
⁶Henry Ford Health System, Detroit, MI
⁷Division of Oncology, Washington University, St Louis, MO
⁸Department of Medicine, The Medical College of Wisconsin, Inc., Milwaukee, WI
⁹Medical University of South Carolina, Charleston, SC
¹⁰Department of Hematology/Oncology, Mayo Clinic, Jacksonville, FL
¹¹Miller School of Medicine, Miami, FL
¹²Pediatric Hematology/Oncology Division, Hackensack University Medical Center, Hackensack, NJ
¹³Beam Therapeutics Inc., Cambridge, MA
¹⁴Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA
¹⁵Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Boston, MA

Jack M Heath^1*, Justin G Tedeschi^1*, Upasana Sunil Arvindam, PhD^1*, Simran Padhye^1*, Kanut Laoharawee, PhD^1*, Allen C Ng^1*, David P Waterman, PhD^1*, Matthew S Roy, PhD^1*, Seth C Alexander, PhD^1*, Sarah Trusiak, PhD^1*, Christopher Divsalar, PhD^1*, Azhaar Alturkistani, PhD^1*, Barrett J Nehilla, PhD^1*, Mallik R Putta, PhD^1*, Katya Kosheleva, PhD^1*, Hetal K Patel, PhD^1*, Rowshon Alam, PhD^1*, Stefanie Urlinger, PhD^2*, Jeremy S Duffield, MD, PhD^1* and Jennifer L Gori, PhD¹

¹Prime Medicine, Inc., Cambridge, MA
²Cimeio Therapeutics AG, Basel, Switzerland

Lorenzo Tozzi, PhD^1*, Giulia Schiroli, PhD^1*, Yaser Heshmati, PhD², Yu Cao, PhD^1*, Michael T. Monte, MS^1*, Apiwat Wangweerawong, PhD^1*, James B. Rottman, PhD, DVM^1*, Rahul Palchaudhuri, PhD^1*, Jean-Antoine Ribeil, MD, PhD^3*, John Manis, MD⁴, Hari Pujar, PhD^1*, William Querbes, PhD^1*, Anne Bothmer, PhD^1*, Cecilia Cotta-Ramusino, PhD^1*, Z. Jane Wang, PhD^1*, William E. Salomon, PhD^1* and Michael C Holmes, PhD^1*

¹Tessera Therapeutics, Somerville, MA
²Tessera Therapeutics, Newton, MA
³Sickle Cell Disease Center of Excellence, Boston University Chobanian and Avedisian School of Medicine, Boston, MA
⁴Transfusion Medicine, Boston Children's Hospital, Boston, MA

Selami Demirci, PhD^1*, Nandini Mondal, PhD^2*, Wayne Austin^2*, Henna Butt, MD^1,3, Evan London^1*, Shruti Sathish^1*, Kathy Zhang^2*, Jeffrey Wong^2*, Hugh Kromer^2*, Alexander Harmon^2*, Jeremy Decker^2*, Anh Le^1*, Khaled Essawi, PhD^4*, Allen E Krouse^5*, N Seth Linde^5*, Aylin Bonifacino^5*, Theresa Engels^5*, Justin Golomb^5*, So Gun Hong, DVM, PhD⁵, Naoya Uchida, MD, PhD¹, Nicole Gaudelli, PhD^2*, Adam J. Hartigan, PhD^2*, Charlotte F McDonagh, PhD^2*, S Haihua Chu, PhD^2*, Robert E Donahue, DVM^1* and John Tisdale, MD⁶

¹Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute (NHLBI), National Institutes of Health (NIH), Bethesda, MD
²Beam Therapeutics Inc, Cambridge, MA
³Children's National Hospital, Washington, DC
⁴Department of Medical Laboratory Technology, College of Applied Medical Sciences, Jazan University, Gizan, Saudi Arabia
⁵Translational Stem Cell Biology Branch, NHLBI, NIH, Bethesda, MD
⁶National Institutes of Health, Bethesda, MD