Wannakorn Khopanlert, MD^1*, Napat Prompat^2*, Jirakrit Saetang^3*, Kajornkiat Maneechai^4*, Shingo Okuno^5*, Seitaro Terakura, MD, PhD⁶ and Jakrawadee Julamanee, MD, PhD⁷

¹Prince of Songkla University, Hat Yai, Thailand
²Faculty of Medical Technology, Prince of Songkla University, Songkhla, Hatyai, Thailand
³International Center of Excellence in Seafood Science and Innovation, Faculty of Agro-Industry, Prince of Songkla University, Songkhla, Thailand, Hat yai, Thailand
⁴Prince of Songkla University, Songkhla, THA
⁵Nagoya University Graduate School of Medicine, Nagoya, JPN
⁶Nagoya University Graduate School of Medicine, Nagoya, Japan
⁷Prince of Songkla University, Songkhla, Thailand

Pratima Chowdary^1,2*, Ulrike M. Reiss, MD³, Edward G. D. Tuddenham, MD^2*, Paul Batty, MBBS, PhD^4*, Jenny H. McIntosh, PhD^5*, Vlad Calin Radulescu, MD⁶, Eugenia Chang, MD^7*, Michael A. Laffan, DM, FRCP, FRCPath^8*, Anne Riddell^9*, Joanna C. M. Calvert^1*, Arnulfo Pie^1*, Rita Peralta, MBBS^10*, Upuli Pabakumari Dissanayake, MD^11*, Kirollos Kamel, MSc, MBBChir¹⁰, Bharath Ram Sreedhar, MBBS^10*, Junfang Zhou^12*, Guolian Kang, PhD, MS¹³, Yunus Olufadi, PHD^14*, Michael M Meagher, PhD^15*, Christopher L Morton^16*, Alison J. Evans^2*, Andrew M. Davidoff, MD¹² and Amit C. Nathwani, MD, PhD¹⁷

¹Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, United Kingdom
²UCL, London, United Kingdom
³Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN
⁴Cancer Institute, University College, London, United Kingdom
⁵Cancer Institute, University College London, London, United Kingdom
⁶University of Kentucky Hospital Auxiliary, Inc., Lexington, KY
⁷St. Luke's Boise Medical Center, Boise, ID
⁸Imperial College School of Medicine, London, GBR
⁹Royal Free London NHS Foundation Trust, London, GBR
¹⁰Royal Free Hospital, London, United Kingdom
¹¹Royal Free London, London, United Kingdom
¹²Department of Surgery, St. Jude Children's Research Hospital, Memphis, TN
¹³Department of Biostatistics, St. Jude Children’s Research Hospital, Memphis, TN
¹⁴Department of Biostatistics, St. Jude Children's Research Hospital, Memphis, TN
¹⁵Department of Therapeutics Production and Quality, St. Jude Children's Research Hospital, Memphis, TN
¹⁶Department of Surgery, St Jude Children's Research Hospital, Memphis, TN
¹⁷Cancer Institute, UCL, London, ENG, United Kingdom

Linah Omer, MD¹, Omar Banda, PhD^1*, Sarah Adams, BS^1*, Seul K Jung, BS^1*, Stefano Rivella, phD², Mohamad-Gabriel Alameh, phD^3*, Drew Weissman, MD, PhD^3* and Peter Kurre, MD^1,2

¹Comprehensive Bone Marrow Failure Center, Children's Hospital of Philadelphia, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
²Department of Pediatrics, University of Pennsylvania, Philadelphia, PA
³Department of Medicine, University of Pennsylvania, Philadelphia, PA

Penelope Lafeuille^1*, Sheila Diamond, MS, CGC^2*, Alexandru Socolov, MBAn^1*, Jacob Aptekar, MD, PhD^2* and Theodore Nowicki, MD, PhD^3*

¹Medidata AI, Medidata, a Dassault Systemes Company, New York, NY
²Medidata AI, Medidata, a Dassault Systèmes company, New York, NY
³University of California, Los Angeles, Los Angeles, CA

Kiran R Majeti, BS^1*, Aadit P Shah, BS^2*, Sofia E Luna, BA², Eric Soupene, PhD^3*, Simon N Chu, MD, MS^4,5,6*, Devesh Sharma, MBBS^4,5,6*, Matthew Porteus, MD, PhD¹ and Kyle Cromer, PhD, MPhil, BS^4,5,6

¹Department of Pediatrics, Stanford University, Stanford, CA
²Stanford University School of Medicine, Stanford, CA
³Children’s Hospital of Oakland Research Institute, Oakland, CA
⁴Department of Surgery, University of California, San Francisco, San Francisco, CA
⁵Eli & Edythe Broad Center for Regeneration Medicine, University of California, San Francisco, San Francisco, CA
⁶Department of Bioengineering & Therapeutic Sciences, University of California, San Francisco, San Francisco, CA

Sylvia von Mackensen, PhD^1*, Jonathan M. Ducore, MD, MPH², Lindsey A. George, MD^3,4, Adam Giermasz, MD, PhD^5*, Catherine McGuinn, MD⁶, John E. J. Rasko, MBBS, PhD⁷, Ben J Samelson-Jones, MD, PhD^4,8, Spencer K. Sullivan, MD^3,4, Jerome M. Teitel, MD⁹, Amit Chhabra, MBBS, MPH¹⁰, Annie F. Fang, MD, PhD^10*, Amanda O'Brien^11*, Frank Plonski, MA, RN, BS^11*, Jeremy Rupon, MD, PhD¹¹, Lynne Smith, MBA^11* and Ian Winburn^12*

¹Department of Medical Psychology, University Medical Centre Hamburg-Eppendorf, Hamburg-Eppendorf, DEU
²Hemophilia Treatment Center, University of California Davis, Sacramento, CA
³The Children's Hospital of Philadelphia, Philadelphia, PA
⁴Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA
⁵University of California, Davis, Sacramento, CA
⁶Pediatric Hematology Oncology Division, Weill Cornell Medical College, New York, NY
⁷Department of Cell and Molecular Therapies, Royal Prince Alfred Hospital, Sydney, NSW, AUS
⁸Division of Hematology, Department of Pediatrics, The Children's Hospital of Philadelphia, Philadelphia, PA
⁹St. Michael's Hospital, Toronto, ON, CAN
¹⁰Pfizer Inc., New York, NY
¹¹Pfizer Inc., Collegeville, PA
¹²Pfizer Inc., Tadworth, GBR

Penelope Lafeuille^1*, William Blumentals^2*, Claire Brulle Wohlhueter^2*, Weixi Chen^1*, Chao Sang^1*, Sydney Manning^1*, Silvy Saltzman^1*, Jan Canvin^2*, Susan Richard^2*, Cris Kamperschroer^2*, Giovanni Abbadessa, MD, PhD², Aniketh Talwai^1*, Caroline Der-Nigoghossian^1*, Yahav Itzkovich^1*, Vibhu Agarwal, PhD^1*, Rahul Jain, PhD^3*, Tanmay Jain^1*, Jacob Aptekar, MD, PhD^3* and Stephan Grupp, MD, PhD⁴

¹Medidata AI, Medidata, a Dassault Systemes Company, New York, NY
²Sanofi, Bridgewater, NJ
³Medidata AI, Medidata, a Dassault Systèmes company, New York, NY
⁴Division of Oncology, Children's Hospital of Philadelphia, Philadelphia, PA

Hemantkumar Chavan, PhD^1*, Shirisha Amatya, MS^2*, Valeria Berlfein^2*, Patricia Cruite, MS^2*, Vandana Chaturvedi, PhD^2*, Vasily Vagin^3*, Neal van Hoeven, PhD^2*, Jagesh Shah, PhD^2*, Terry J. Fry, MD², Boris Gorovits^2* and Sundeep Chandra^2,4*

¹Sana Biotechnology, South San Francisco, CA
²Sana Biotechnology, Seattle, WA
³Sana Biotechnology, Cambridge, MA
⁴Sana Biotechnology, Cambridge

Jesse Green, PhD^1*, Andrew Tucker^1*, Aesha Vakil, MSc^1*, Matt Scott-Skandera^2*, Vasily Vagin^2*, Dharmesh Dingar^2*, Tarik Elgendi^2*, Christina Proano^2*, Brian Dolinski^2*, Matthew A. Lunning, DO, FACP^3*, Scott A Koepsell^3*, Charles A Branson^3*, Kerrie Enger^2*, Danielle Quarles, MPH^1*, Hosein Kouros-Mehr^4*, Sarah Miller^4*, Misha Shamashkin, PhD^2* and Kutlu G Elpek, PhD^2*

¹Sana Biotechnology, Seattle, WA
²Sana Biotechnology, Cambridge, MA
³University of Nebraska Medical Center, Omaha, NE
⁴Sana Biotechnology, South San Francisco, CA

Jesus Beltran-Garcia, PhD^1*, Sangwoo Han, PhD^2*, Barbara S. Perez^1*, Jonathan Gunn^2*, Ester Kwon, PhD^2* and Dan Kaufman, MD, PhD¹

¹Dept. of Medicine - Sanford Stem Cell Institute, University of California, San Diego, San Diego
²Department of Bioengineering, University of California, San Diego, San Diego

Chantal Lagresle-Peyrou, PhD^1*, Jean-Sebastien Diana, MD; PhD^2*, Elisa Magrin, PharmD; PhD^3*, Clotilde Aussel, PharmD; PhD^3*, Natael Sorel^1*, Yetki Aslan^1*, Cécile Roudaut^4*, Eden Schwartz, PharmD^3*, Aurélie Gabrion^5*, Caroline Tuchmann-Durand, PrarmD^3*, Francois Lefrere, M.D^3*, Anne Galy, PharmD, PhD^6*, Despina Moshous, MD; PhD^7* and Marina Cavazzana, MD, PhD^8,9,10

¹Institut Imagine, Paris, France
²Université de Paris Cité, Paris, France
³Necker Hospital (APHP), Paris, France
⁴Hopital Necker - Enfants Malades, Paris, FRA
⁵Hopital Necker Enfants-Malades, Paris, France
⁶INSERM U790 Genethon, Evry, FRA
⁷Hôpital Necker-Enfants Malades, Paris, FRA
⁸Department of Biotherapy, Hospital Necker, University Paris Descartes, Paris, France
⁹Imagine Institute, Paris, FRA
¹⁰Biotherapy Clinical Investigation Center, Inserm Assistance Publique Hôpitaux de Paris, Paris, France