-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

Plenary Scientific Session

PhD Trainee
Plenary Program: General Sessions
Sunday, December 6, 2015: 2:00 PM-4:00 PM
Hall D, Level 2 (Orange County Convention Center)

Adele K Fielding, MB, BS, PhD

Academic Department of Haematology, Hampstead Campus, University College London, London, United Kingdom

Sébastien Maury1*, Sylvie Chevret2*, Xavier Thomas3, Dominik Heim4,5, Thibaut Leguay6*, Françoise Huguet7*, Patrice Chevallier8*, Mathilde Hunault9*, Nicolas Boissel10, Martine Escoffre-Barbe11*, Urs Hess5,12*, Norbert Vey13, Thorsten Braun14*, Jean-Pierre Marolleau15, Yves Chalandon5,16, Véronique Lhéritier17*, Kheira Beldjord10*, Marie-Christine Béné, PharmSciD, PhD8*, Norbert Ifrah9 and Hervé Dombret10

1Hematology, Hôpital Henri Mondor, Créteil, France
2Biostatistics, Hôpital Saint-Louis, Paris, France
3Hematology, Centre Hospitalier Lyon-Sud, Pierre Bénite, France
4Hematology, University Hospital, Basel, Switzerland
5Swiss Group for Clinical Cancer Research (SAKK), Bern, Switzerland
6Hematology, Hôpital Haut-Lévêque, Pessac, France
7Hematology, Institut Universitaire du Cancer, Toulouse, France
8Hematology, Hôpital Hôtel Dieu, Nantes, France
9Hematology, CHU, Angers, France
10Hematology, Hôpital Saint-Louis, Paris, France
11Hematology, Hôpital Pontchaillou, Rennes, France
12Hematology, Kantonsspital, St Gallen, Switzerland
13Hematology, Institut Paoli-Calmette, Marseille, France
14Hematology, Hôpital Avicenne, Bobigny, France
15Hematology, Centre Hospitalier Universitaire, Amiens, France
16Hematology, Hôpitaux Universitaires, Genève, Switzerland
17GRAALL Coordination, Centre Hospitalier Lyon-Sud, Pierre Bénite, France

George J. Dover, MD

Johns Hopkins University School of Medicine, Baltimore, MD

Takeshi Masuda, Ph.D.1*, Xin Wang, Ph.D.2*, Manami Maeda, M.D., Ph.D.1*, Matthew C. Canver, B.S.3*, Falak Sher, Ph.D.3*, Alister P.W. Funnell, Ph.D.4*, Chris Fisher, Ph.D.5*, Maria Suciu5*, Gabriella E. Martyn4*, Laura J. Norton4*, Ruijia Zhu1*, Ryo Kurita, Ph.D.6*, Yukio Nakamura, M.D., Ph.D.6*, Jian Xu, Ph.D.7, Douglas R. Higgs, FRS5, Merlin Crossley, DPhil4*, Daniel E. Bauer, M.D., Ph.D.3, Stuart H. Orkin, M.D.8, Peter V. Kharchenko, Ph.D.2* and Takahiro Maeda, M.D., Ph.D.1

1Division of Hematology, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA
2Department of Biomedical Informatics, Harvard Medical School, Boston, MA
3Pediatric Hematology-Oncology, Boston Children's Hospital, Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA
4School of Biotechnology and Biomolecular Sciences, University of New South Wales, Sydney, Australia
5MRC Molecular Haematology Unit, Weatherall Institute of Molecular Medicine, Oxford University, Oxford, United Kingdom
6Cell Engineering Division, RIKEN BioResource Center, Tsukuba, Japan
7Children’s Medical Center Research Institute, University of Texas Southwestern Medical Center, Dallas, TX
8Department of Pediatric Hematology-Oncology, Boston Children's Hospital, Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA

Julie A. Panepinto, MD, MSPH

The Medical College of Wisconsin/Children's Research Institute of the Children's Hospital of Wisconsin, Milwaukee, WI

Russell E. Ware, MD, PhD1, Barry R Davis, MD PhD2*, William H Schultz, MHS PA3*, Clark Brown, MD, PhD4,5, Banu Aygun, MD6, Sharada A. Sarnaik, MD7, Isaac Odame, MD8, Beng Fuh, MD9*, Alex George, M.D., Ph.D.10, William Owen, MD11, Lori Luchtman-Jones, MD3, Zora R. Rogers, MD12, Lee Hilliard, MD13, Cynthia Gauger, MD14*, Connie M. Piccone, MD15, Margaret T. Lee, MD16, Janet Kwiatkowski, MD17, Sherron Jackson, MD18*, Scott T. Miller, MD19, Carla W Roberts, MD20*, Matthew M. Heeney, MD, FRCP(C)21, Theodosia A. Kalfa, MD, PhD3, Stephen C Nelson, MD22, Hamayun Imran, MD23*, Kerri A Nottage, MD, MPH24, Ofelia A. Alvarez, MD25, Melissa Rhodes, MD26, Alexis A. Thompson, MD27, Jennifer Rothman, MD28, Kathleen J. Helton, MD24*, Donna Roberts, MD18*, Jamie Coleman, MD24*, Melanie J Bonner, PhD28*, Abdullah Kutlar, MD29, Niren Patel, MD30*, John C Wood, MD, PhD31*, Linda Piller, MD2*, Peng Wei, PhD2*, Judy Luden, CCRP18*, Nicole A. Mortier, MHS, PA-C3*, Susan Stuber, MA3*, Naomi L.C. Luban, MD32, Alan R. Cohen, MD17, Sara L Pressel, MS2* and Robert J. Adams, MD, MS18*

1Division of Hematology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
2University of Texas School of Public Health, Houston, TX
3Cincinnati Children's Hospital Medical Center, Cincinnati, OH
4Children's Healthcare of Atlanta, Atlanta
5Emory University, Atlanta
6Cohen Children's Medical Center of New York, New Hyde Park, NY
7Pediatrics, Children's Hosp. of Michigan, Detroit, MI
8University of Toronto, The Hospital for Sick Children, Toronto, ON, Canada
9East Carolina University, Greenville, NC
10Baylor College of Medicine, Houston, TX
11Children's Hospital of the King's Daughters, Norfolk, VA
12UT Southwestern, Dallas, TX
13Department of Pediatrics, University of Alabama at Birmingham, Birmingham, AL
14Nemours, Jacksonville, FL
15Case Western Reserve University, Cleveland, OH
16Columbia University, New York, NY
17Children's Hospital of Philadelphia, Philadelphia, PA
18Medical University of South Carolina, Charleston, SC
19Pediatrics, SUNY - Downstate, Brooklyn, NY
20University of South Carolina, Columbia, SC
21Boston Children’s Hospital, Harvard Medical School, Boston, MA
22Children’s Hospitals and Clinics of Minnesota, Minneapolis, MN
23Pediatric Hematology-Oncology, University of South Alabama, Children's and Women's Hospital, Mobile, AL
24St. Jude Children's Research Hospital, Memphis, TN
25Univ. of Miami School of Med., Miami, FL
26University of Mississippi Medical Center, Jackson, MS
27Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL
28Duke University Medical Center, Durham, NC
29Georgia Regents University, Augusta, GA
30Sickle Cell Center, Georgia Regents University, Augusta, GA
31Division of Cardiology, Children's Hospital Los Angeles, Los Angeles, CA
32Transfusion Medicine, Hematology/Oncology, Children's National Medical Center, Washington, DC

Rafael Bejar, MD, PhD

UCSD Moores Cancer Center, La Jolla, CA

Stanley Chun-Wei Lee, PhD1*, Heidi Dvinge2*, Eunhee Kim, PhD3*, Hana Cho3*, Young Rock Chung, MS4*, Jean-Baptiste Micol, MD5,6*, Benjamin Durham, MD, PhD3*, Young Joon Kim1*, Michael Thomas7*, Camille Lobry, PhD8*, Silvia Buonamici, PhD7, Peter Smith9*, Robert K. Bradley, PhD10* and Omar Abdel-Wahab3

1MSKCC, New York
2Fred Hutchinson Cancer Center, Seattle
3Memorial Sloan Kettering Cancer Center, New York, NY
4Human Oncology and Pathogenesis Program, Memorial Sloan Kettering Cancer Center, New York, NY
5MSKCC, New York, NY
6Gustave Roussy Cancer Center, Villejuif, France
7H3 Biomedicine, Cambridge, MA
8Gustave Rousy Institute, Villejuif, France
9H3 Biomedicine Inc., Cambridge
10Fred Hutchinson Cancer Research Center, Seattle, WA

Donna DiMichele, MD

Weill Cornell Medical College, New York Presbyterian Hospital, New York, NY

Flora Peyvandi, MD, PhD1, Pier Mannuccio Mannucci, MD2, Isabella Garagiola, PhD3*, Mohsen Elalfy, MD4*, Amal El-Beshlawy, MD5, Madatha V. Ramanan, MD6*, Peyman Eshghi, MD7*, Suresh Hanagavadi8*, Ramabadran Varadarajan, MD9*, Mehran Karimi, MD10, Mamta V. Manglani, MD11*, Cecil Ross, MD12*, Guy Young, MD13, Tulika Seth, MD14*, Shashikant Apte, MD, FRCPA15, Dinesh M. Nayak, MD16*, Adriana C. Sandoval Gonzales, MD17*, Elena Santagostino, MD, PhD18, Maria Elisa Mancuso, MD, PhD18, Johnny N. Mahlangu, MD19*, Santiago Bonanad, PhD20*, Monica Cerqueira, MD21*, Nadia P. Ewing, MD22, Christoph Male, MD, MSC23*, Tarek Owaidah, MD, FRCPA24, Veronica Soto Arellano, MD25*, Nathan L. Kobrinsky, MD, FRCP26*, Suvankar Majumdar, MD27, Rosario Perez Garrido, MD28*, Anupam Sachdeva29, Mindy Simpson, MD, FAAP30, Mathew Thomas31*, Ezio Zanon, MD32*, ALI Bulent Antmen33*, Kaan Kavakli, MD34, Marilyn Manco-Johnson, MD35, Monica Martinez, MD36*, Esperanza Marzouka, MS, PS37*, Maria Gabriella Mazzucconi, MD38*, Daniela Neme, MD39*, Angeles Palomo Bravo, MD40*, Rogelio Paredes Aguilera, MD41*, Alessandra Nunes Loureiro Prezotti, MD42*, Schmitt Klaus, MD43*, Brian M. Wicklund, MD, MPH44, Bulent Zulfikar, MD45* and Rosendaal R. Frits, MD, PhD46*

1Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
2Scientific Direction, Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milano, Italy
32Department of Pathophysiology and Transplantation, Università degli Studi di Milano., Milan, Italy
4Pediatrics Department Ain Shams University, Cairo, Egypt
5Pediatrics, Cairo University, Cairo, Egypt
6Jehangir Clinical Development Centre, Department of Hematology, Jehangir Hospital Premises, Pune, India
7Pediatric Congenital Hematologic Disorders Research Center,Shahid Beheshti University of Medical Sciences, Tehran, Iran
8Department of Pathology, J J M Medical College,, Davangere, India
9Centre for Blood Disorders, Chennai, India
10Shiraz Hematology Research Center, Shiraz, Iran
11Lokmanya Tilak Municipal Medical College & General Hospital, Mumbai, India
12St. John's Medical College & Hospital, Bangalore, India
13Children's Hospital of Los Angeles, Los Angeles, CA
14All India Institute of Medical Sciences Department of Haematology, New Delhi, India
15Department of Haematology, Sahyadri Speciality Hospital, Pune, India
16Kasturba Medical College, Manipal University, Manipal, India
17Hospital de Especialidades UMAE, Istituto Mexicano del Seguro Social (IMSS), Monterry, Mexico
18Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan, Italy
19Haemophilia Comprehensive Care Centre, Faculty of Health Sciences, University of the Witwatersrand and National Health Laboratory Service., Johannesburg, South Africa
20Haemostasis and thrombosis Unit, La Fe University and Polytechnic Hospital, Valencia, Spain
21Centro de Pesquisa Clinica HEMORIO - Instituto Estadual de Hematologia Arthur de Siqueira Cavalcanti, Rio de Janeiro, Brazil
22City Of Hope National Medical Center, Duarte, CA
23Department of Pediatrics, Medical University of Vienna, Vienna, Austria
24Pathology and Laboratory Medicine, King Faisal Specialist Hospital and Research Centre, Riyadh, Saudi Arabia
25Centro de Diagnóstico y Tratamiento de Hemofilia Hospital de Niños Roberto del Rio, Santiago, Chile
26Sanford Roger Maris Cancer Center, Fargo, ND
27University of Mississipi Medical Center Division of pediatric Hematology/Oncology, Jackson
28Hospital universitario Virgen del Rocio Unidad de Hemofilia, Sevilla, Spain
29Pediatric Hematology Oncology & BMT Unit, Sir Ganga Ram Hospital, New Delhi, India
30Rush Hemophilia & Thrombophilia Center Rush University Medical Center, Chicago, IL
31Kerela Institute of Medical Science (KIMS), Trivandrum, India
32Clinica Medica II - Azienda Ospedaliera di Padova -, Padua, Italy
33Department of Pediatrics, Division of Pediatric Hematology Balcali Hospital, Pediatric Hematology Cukurova University, Adana, Turkey
34Dept. Pediatric Hematology, Ege University Medical School, Izmir, Turkey
35Hemophilia & Thrombosis Center University of Colorado Denver, Aurora, CO
36Hospital de Ninos Sor Maria Ludovica La Plata Servicio de Hematologia, Buenos Aires, Argentina
37Hospital de Niños Dr. Luis Calvo Mackenna Centro Hemofílico, Santiago, Chile
38Centro Regionale di Riferimento per l’Emofilia e Sindromi Correlate, Università Sapienza, Policlinico Umberto I, Rome, Italy
39Fundacion de la Hemofilia, BUENOS AIRES, Argentina
40Hospital Regional Universitario Carlos Haya, Malaga, Spain
41Instituto Nacional de Pediatria, México, D.F., Mexico
42Centro de Hematologia e Hemoterapia do Espirito Santo– Hemoes, Vitoria, Brazil
43Children`s Hospital Linz, Linz, Austria
44Children's Mercy Hospital, Kansas City, MO
45Istanbul University, ISTANBUL, Turkey
46Department of Clinical Epidemiology, Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, Netherlands

Mark J. Levis, MD, PhD

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins, Baltimore, MD

Richard M. Stone, MD1, Sumithra Mandrekar2*, Ben L Sanford, MS3*, Susan Geyer, PhD4,5*, Clara D. Bloomfield, MD6, Konstanze Dohner, M.D.7, Christian Thiede, MD8, Guido Marcucci, MD9, Francesco Lo-Coco10*, Rebecca B. Klisovic, MD11, Andrew Wei, MBBS, PhD12, Jorge Sierra, MD, PhD13, Miguel A. Sanz, MD, PhD14, Joseph M. Brandwein, MD, FRCPC15, Theo de Witte, MD16, Dietger Niederwieser, MD17, Frederick R. Appelbaum, MD18, Bruno C. Medeiros, MD19, Martin S Tallman, MD20*, Jurgen Krauter, MD21*, Richard F. Schlenk, MD7, Arnold Ganser, M.D.22, Hubert Serve23, Gerhard Ehninger, MD24, Sergio Amadori, MD25, Richard A. Larson, MD26 and Hartmut Dohner, MD7

1Department of Medical Oncology, Dana-Farber Cancer Institute, Boston, MA
2Mayo Clinic, Rochester
3Duke University, Durham, NC
4Alliance Statistics and Data Center, The Ohio State University, Columbus, OH
5Division of Hematology, The Ohio State University, Columbus, OH
6Comprehensive Cancer Center, The Ohio State University, Columbus, OH
7University Hospital of Ulm, Ulm, Germany
8Medizinische Klinik und Poliklinik I, Universitätsklinikum Carl Gustav Carus der TU Dresden, Dresden, Germany
9The Ohio State University Comprehensive Cancer Center, Columbus, OH
10Tor Vergata University Hospital, Rome, Italy
11Division of Hematology, Department of Internal Medicine, The Ohio State University, Columbus, OH
12Haematology, The Alfred Hospital, Melbourne, Australia
13Hospital de la Santa Creu i Sant Pau, Hematology Department, Autonomous University of Barcelona, Barcelona, Spain
14Hospital Universitario la Fe, Valencia, Spain
15Department of Medical Oncology and Hematology, Princess Margaret Hospital, Toronto, ON, Canada
16Radboud University Medical Centre, nijmegen, Netherlands
17Hematology and Oncology, University of Leipzig, Leipzig, Germany
18Transplantation Biology Department, Clinical Research Division, Fred Hutchinson Cancer Research Center, Seattle, WA
19Division of Hematology/Oncology, Stanford Comprehensive Cancer Center, Stanford Univ., Stanford, CA
20Leukemia Service, Department of Medicine, Memorial Sloan Kettering Cancer Center, New York, NY
21Hannover Medical School, Hannover, Germany
22Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
23Dept. of Medicine II, Hematology/Oncology, Goethe University Hospital Frankfurt, Frankfurt/Main, Germany
24Medical Dept. 1, University Hospital TU Dresden, Dresden, Germany
25Hematology, University Tor Vergata, Rome, Italy
26Medicine, University of Chicago, Chicago, IL

See more of: Plenary
See more of: General Sessions