-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

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905.O2.6 905. Outcomes Research: Non-Malignant Conditions Excluding Hemoglobinopathies: Innovative Approaches to Improve Care for Understudied Non-Malignant Hematologic Diseases

Symposia: Outcomes Research: Non-Malignant Conditions Excluding Hemoglobinopathies Program: Oral and Poster Abstracts
Type: Oral
Hematology Disease Topics & Pathways:
Research, Bleeding and Clotting, Bleeding disorders, Autoimmune disorders, Adult, Clinical trials, Clinical Practice (Health Services and Quality), Autoimmune hemolytic anemia, Epidemiology, Elderly, Clinical Research, Health outcomes research, Platelet disorders, Genetic Disorders, Health disparities research, Pediatric, Hemoglobinopathies, Diversity, Equity, and Inclusion (DEI), Diseases, Thrombocytopenias, Immune Disorders, Immunodeficiency, Real-world evidence, Treatment Considerations, Registries, Young adult , Survivorship, Study Population, Human, Maternal Health
Monday, December 9, 2024: 10:30 AM-12:00 PM
Room 6B (San Diego Convention Center)
Moderators:
Barbara D Lam, MD, and George Goshua, MD, MSc, Yale School of Medicine & Yale Cancer Center
Disclosures:
No relevant conflicts of interest to declare.
10:30 AM

Mary Morgan1*, Yulia Lin, MD1,2, Julia Lou1*, Anne McLeod, MD3,4*, Nadine Shehata, MD, FRCPC, MSc5,6, Noor Niyar N. Ladhani, MD7,8*, Maria Noronha, RN7*, Kristine Matusiak, MBBS, FRCP9 and Heather Vandermeulen, MD4,10*

1Precision Diagnostics and Therapeutics Program, Sunnybrook Health Sciences Centre, Toronto, ON, Canada
2Department of Laboratory Medicine and Pathobiology, University of Toronto, Toronto, ON, Canada
3Department of Medicine, Sunnybrook Health Sciences Centre, Toronto, ON, CAN
4Department of Medicine, University of Toronto, Toronto, Canada
5Department of Medicine, Mount Sinai Hospital, Toronto, ON, Canada
6Department of Medicine, University of Toronto, Toronto, ON, Canada
7Department of Obstetrics and Gynecology, Sunnybrook Health Sciences Centre, Toronto, Canada
8Department of Obstetrics and Gynecology, University of Toronto, Toronto, Canada
9Division of Hematology and Thromboembolism, McMaster University, Hamilton, ON, Canada
10Department of Medicine, Sunnybrook Health Sciences Centre, Toronto, Canada

10:45 AM

Maria A. Rodríguez Sánchez1*, Anna Collado Gimbert, MD1,2*, Sara Reidel, MSc1*, Patricia Aguilar-Martinez, MD, PhD3*, Celeste Bento, PhD4*, Elena Cela, MD, PhD5*, Laurence Dedeken, MD6*, Emma Drasar, MD, PhD7*, Frederic Galacteros, Prof, MD8*, Andreas Glenthoej, MD, PhD9, Monika Horvathova, PhD10, Pavla Koralkova, PhD10*, Andreas E. Kulozik, MD, PhD11, Joachim B. Kunz, Prof., MD12*, Marta Morado-Arias, MD, PhD13*, Ana Ortuno Cabrero, MD14*, Dagmar Pospíšilová, Prof., PhD15*, Minke A.E. Rab, MD, PhD16,17*, Noemi Roy, MD, PhD18*, Eduard J. Van Beers, MD, PhD19, Richard van Wijk, PhD20, Sarah Wambacq, MSc21*, Claire Diot, MEd1*, Victoria Gutiérrez Valle1*, Raquel Mosull del Campo, MSSc1*, Stella Tamana, PhD22*, Raffaella Colombatti, MD, PhD23*, Petros Kountouris, PhD24*, Béatrice Gulbis, MD, PhD25*, Paola Bianchi, PhD, BSc26 and Maria del Mar Mañú-Pereira, PhD1*

1Rare Anemia Disorders Research Laboratory, Cancer and Blood Disorders in Children, Vall d'Hebron Research Institute / Vall d'Hebron University Hospital, Barcelona, Spain
2Pediatric Oncology and Hematology, Vall d'Hebron Barcelona Hospital, Barcelona, Spain
3Department of hematology biology, University and CHU de Montpellier, Montpellier, France
4Hematolody Department, University Hospital Coimbra, Coimbra, Portugal
5Pediatric Hematology and Oncology, Hospital Gregorio Marañón. Universidad Complutense de Madrid, Madrid, Spain
6Department of Hematology-Oncology, Hôpital Universitaire des Enfants Reine Fabiola, Brussels, Belgium
7Department of Haematology, Whittington Health NHS Trust, London, United Kingdom
8GHU Henri Mondor, AP-HP, Creteil, France
9Danish Red Blood Cell Center, Department of Hematology, Copenhagen University Hospital - Rigshospitalet, Copenhagen, Denmark
10Department of Biology, Faculty of Medicine and Dentistry, Palacký University Olomouc, Olomouc, Czech Republic
11Department of Pediatric Oncology, Hematology and Immunology, Heidelberg University, Heidelberg, Germany
12Department of Pediatric Hematology, Oncology and Immunology, Heidelberg University Hospital, Heidelberg, Germany
13Hematology department, Hospital Universitario La Paz, Madrid, Madrid, Spain
14Haematology, Whittington Hospital, London, United Kingdom
15Department of Pediatrics, Faculty Hospital, Palacky University, Olomouc, Czech Republic
16Department of Hematology, Erasmus University Medical Center, Rotterdam, Netherlands
17Central Diagnostic Laboratory, University Medical center Utrecht, Utrecht, Netherlands
18Haematology, Oxford University Hospitals NHS Trust, Oxford, United Kingdom
19Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Centre Utrecht, University of Utrecht, Utrecht, Netherlands
20Central Diagnostic Laboratory, University Medical Center Utrecht, Utrecht, Netherlands
21Hôpital Universitaire des Enfants Reine Fabiola, Haemato-oncology, Hôpital Universitaire de Bruxelles (HUB), Brussels, Belgium
22Molecular Genetics Thalassaemia Department, The Cyprus Institute of Neurology and Genetics, Nicosia, Cyprus
23Department for Woman's and Child's Health, University of Padova, Padova, Italy
24Molecular Genetics Thalassaemia Department, The Cyprus Institute of Neurology and Genetics, Nicosia, CYP
25Centre of Human genetics, Hôpital Universitaire de Bruxelles, Université Libre de Bruxelles, Brussels, Belgium
26Hematology Unit, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Milano, Italy

11:00 AM

Rachael F Grace, MD1, MacGregor Steele, MD2*, Tatiana Kalashnikova2*, Ellis Bloom, DO3*, Aila Khan3*, Sherif M. Badawy, MD, MS, MBA4, Hannah Elkus, MD5*, Vicky R. Breakey, MD, BSc, FRCPC, MEd6, Sureka Pavalagantharajah, MD7*, Stephanie A. Fritch Lilla, MD8, John Leister, DO9*, Manpreet Kochhar, MD, MS10*, Kirsty Hillier, MD11*, Lia Phillips, MD12*, Jessica Chumsky, MD11*, Robert J. Klaassen, MD, FRCPC13, Dana Ghanem14*, Danielle Charland, BScH14*, Taizo A. Nakano, MD15, Joshua Kalter, MD16*, Allison Remiker, MD17*, Jennifer A. Rothman, MD18, Caitlyn McComb, MD18*, Brian Guedes, MD18*, Sanjay J. Shah, MBBS19, Cassandra J. Everly20*, Kristin A. Shimano, MD21, Alison Matsunaga, MD22*, Gerald C Tiu, MD, PhD22*, Russell P Valle, MD, MS22*, Shilpa Nataraj, MD22*, Stacey Rifkin-Zenenberg, DO23, Erika Tavares24*, Caitlin Montcrieff, MSN, CPNP24*, Emily M Harris, MD24, Nan Chen, MS25*, Wendy B. London, PhD25* and Michele P. Lambert, MD26

1Dana-Farber/Boston Children's Cancer and Blood Disorders Center and Harvard Medical School, Boston, MA
2Alberta Children’s Hospital, Calgary, Alberta, Canada
3Division of Hematology, The Children's Hospital of Philadelphia, Philadelphia, PA
4Ann & Robert Lurie Children's Hospital, Chicago, IL
5Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
6McMaster Children's Hospital, Hamilton, ON, CAN
7McMaster University, Hamilton, ON, Canada
8Children's Minnesota, Minneapolis, MN
9University of Minnesota, Minneapolis, MN
10The Warren Alpert Medical School at Brown University, Hasbro Children's Hospital, Providence, RI
11NYU Langone Children’s Hospital, New York, NY
12Department of Pediatrics, NYU Grossman Long Island School of Medicine, Mineola, NY
13Division of Hematology/Oncology, Children's Hospital of Eastern Ontario, Ottawa, ON, Canada
14Children's Hospital of Eastern Ontario, Ottawa, ON, Canada
15Children's Hospital Colorado, Denver, CO
16Children’s Hospital Colorado, Denver, CO
17Children's Wisconsin, Medical College of Wisconsin, Milwaukee, WI
18Duke University Medical Center, Durham, NC
19Department of Child Health, Phoenix Children’s Hospital, University of Arizona College of Medicine, Chandler, AZ
20Phoenix Children’s Hospital, University of Arizona College of Medicine, Phoenix, AZ
21Pediatric Allergy, Immunology, and Bone Marrow Transplant Division, University of California San Francisco Benioff Children's Hospital, San Francisco, CA
22UCSF Benioff Children's Hospital, San Francisco, CA
23Pediatric Hematology/Oncology Division, Hackensack Meridian Health, Hackensack, NJ
24Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Boston, MA
25Dana Farber/Boston Children's Cancer and Blood Disorders Center, Boston, MA
26Children's Hospital of Philadelphia, Philadelphia, PA

11:15 AM

Michael Glenzer, MPH1, Momade Correia, MD2*, Virgilio Nhantumbo, MD2*, Daniel Agostinho, MD2*, Elvira Luis, MD2*, Ines Boaventura, MD2*, Sierra Washington, MD3*, Patricia Silva, MD2* and Annette von Drygalski, MD, PharmD, RMSK1

1Center for Bleeding and Clotting Disorders, University of California San Diego, San Diego, CA
2Hospital Central Maputo, Maputo, Mozambique
3Center for Global Health Equity, Stony Brook University, Stony Brook, NY

11:30 AM

Ariela Noy, MD1, Robert Ohgami, MD, PhD2*, Nikhil C. Munshi, MD3, Imran Siddiqi, MD, PhD4*, Kelley C. Dacus, PharmD5*, Alicia Watson Saltis, PhD5*, Francis Shupo, MSc6*, Nicole Princic7*, Kristin Evans, PhD8* and Sudipto Mukherjee, MD, PhD, MPH9

1Memorial Sloan Kettering Cancer Center and Weill Cornell Medical College, New York, NY
2ARUP Institute for Research and Innovation, Salt Lake City, UT
3Dana-Farber Cancer Institute, Boston, MA
4University of Southern California, Norris Comprehensive Cancer Center, Los Angeles, CA
5Recordati Rare Diseases Inc., Bridgewater, NJ
6Recordati Rare Disease UK Ltd., Hemel Hempstead, United Kingdom
7MarketScan by Merative, Reading, MA
8MarketScan by Merative, Ann Arbor, MI
9Department of Hematology and Medical Oncology, Cleveland Clinic Taussig Cancer Institute, Cleveland, OH

11:45 AM

Rialnat A. Lawal, MD, PhD1, Natalie T. Deuitch, MS2*, Erica Bresciani, PhD2*, Amra Kajdic2*, Shawn Chong2*, Kathleen Craft, B.S.N., R.N.2*, David J. Young, MD, PhD3 and Paul P. Liu, MD, PhD2

1Cellular and Molecular Therapeutics Branch, National Heart, Lung, and Blood Institute, National Institute of Health, BETHESDA, MD
2Oncogenesis and Development Section, National Human Genome Research Institute, NIH, Bethesda, MD
3Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institute of Health, Bethesda, MD

*signifies non-member of ASH