-Author name in bold denotes the presenting author
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Clinically Relevant Abstract denotes an abstract that is clinically relevant.

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Risks and Rewards of a Unified Gene Therapy for Diamond-Blackfan Anemia

Scientific Workshop on Germline Predisposition to Hematopoietic Malignancies and Bone Marrow Failure
Program: Scientific Workshops
Session: Rapid Presentations of New Insights
Friday, December 6, 2024, 3:26 PM-4:06 PM

Richard Voit, MD, PhD

Department of Pediatrics, Division of Hematology/Oncology, University of Texas Southwestern Medical Center, Dallas, TX; University of Texas Southwestern, Dallas, TX

Disclosures: No relevant conflicts of interest to declare.