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Luspatercept: A Treatment for Ineffective Erythropoiesis in Thalassemia

Program: Education Program
Session: Integrating New Therapies into the Management of Classical Heme Disorders
Hematology Disease Topics & Pathways:
Research, Clinical trials, Adult, Clinical Practice (Health Services and Quality), Drug development, Clinical Research, Thalassemia, Education, Hemoglobinopathies, Pediatric, Diseases, Real-world evidence, Treatment Considerations, Adverse Events, Young adult , Study Population, Human
Saturday, December 7, 2024, 2:00 PM-3:15 PM

Kleber Yotsumoto Fertrin, MD, PhD1,2 and Ali T. Taher, MD, FRCP3

1University of Washington, Seattle, WA
2Fred Hutchinson Cancer Center, Seattle, WA
3Division of Hematology and Oncology, Department of Internal Medicine, American University of Beirut Medical Center, Beirut, Lebanon

Disclosures: Fertrin: Sanofi Genzyme: Consultancy; Agios Pharmaceuticals: Consultancy, Membership on an entity's Board of Directors or advisory committees, Research Funding, Speakers Bureau; Bluebird bio: Membership on an entity's Board of Directors or advisory committees. Taher: Vifor: Consultancy, Research Funding; Pharmacosmos: Consultancy, Research Funding; Novo Nordisk: Consultancy; Bristol Myers Squibb (Celgene): Consultancy, Research Funding; Agios Pharmaceuticals, Inc.: Consultancy, Research Funding.

OffLabel Disclosure: I will discuss off-label use of luspatercept in non-transfusion dependent thalassemias.