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Pyruvate Kinase Activators for Treatment of Pyruvate Kinase Deficiency

Program: Education Program
Session: Energizing the Red Cell: Pyruvate Kinase Activators for Treatment of Hereditary Hemolytic Anemias
Hematology Disease Topics & Pathways:
Research, clinical trials, Sickle Cell Disease, Non-Biological therapies, Clinical Research, Genetic Disorders, Thalassemia, Hemoglobinopathies, drug development, Diseases, Therapies, metabolism, Pharmacology, Biological Processes, Metabolic Disorders, Study Population, Human
Monday, December 11, 2023, 10:30 AM-11:45 AM

Rachael F. Grace, MD

Boston Children's Hospital, Boston, MA

Disclosures: Grace: Sanofi: Consultancy; Agios: Consultancy, Research Funding; Novartis: Research Funding; Sobi: Research Funding.

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