-Author name in bold denotes the presenting author
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Rational Design of Factor VIII Variants for Hemophilia A Gene Therapy

Program: Scientific Program
Session: Next Generation of Gene-Based Therapies for Bleeding Disorders
Saturday, December 9, 2023, 9:30 AM-10:45 AM

Lindsey A. George, MD

The Children's Hospital of Philadelphia, Philadelphia, PA

Disclosures: George: Regeneron: Consultancy, Membership on an entity's Board of Directors or advisory committees; AskBio: Patents & Royalties, Research Funding; Spark Therapeutics: Consultancy; STRM.BIO: Other: has a leadership/fiduciary role .