Chris Hartford, MPH^1*, Bradley Dain, PhD^2*, Steven Sherman, MPH^2*, Yi Zhang^2*, Rodrigo Pavani, MD, PhD^2*, Lisa Aurand, MD², Diana Rofail, PhD^2* and Richard Kelly, BSc, MD^3*

¹Regeneron Pharmaceuticals, Inc., Sleepy Hollow, NY
²Regeneron Pharmaceuticals, Inc., Tarrytown, NY
³Department of Haematology, St James University Hospital, Leeds, United Kingdom

Ash Lee Manley^1*, Jennifer Lotter^2*, Emma M. Groarke, MD³, Olga Rios, RN^3*, Neal S. Young, MD⁴ and Bhavisha A. Patel, MD³

¹Hematology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Silver Spring, MD
²National Institutes of Health, Bethesda, MD
³Hematology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
⁴National Institute of Health, Bethesda, MD

Alexander T Cohen, MBBS MSc MD FRACP FESC^1*, Virginia Noxon, PhD^2*, Amol D Dhamane, MS^3*, Shrushti Shah, MPH^2*, Dionne M Hines, PhD, MPH^4*, Tamuno Alfred, PhD, MSc^4*, Jose Chaves, PhD^5* and Xuemei Luo, PhD^6*

¹Guy's and St Thomas' NHS Foundation Trust, London, United Kingdom
²STATinMED, LLC, Dallas, TX
³Bristol Myers Squibb, Lawrenceville, NJ
⁴Pfizer, Inc., New York, NY
⁵Pfizer SLU, Madrid, Spain
⁶Pfizer Inc., Groton, CT

Amanda Stahl, MSW, LICSW^1*, Kaitlin Barnett, MSW, LCSW^2*, Amy K. Wilson, MSW, LICSW, ACM^3*, Siyang Ren, MS^4*, Donna S. Neuberg, ScD⁴, Hae Soo Park^1* and Aric D. Parnes, MD¹

¹Division of Hematology, Brigham and Women's Hospital, Boston, MA
²Icahn School of Medicine at Mount Sinai, New York, NY
³M Health Fairview Center for Bleeding and Clotting Disorders, Minneapolis, MN
⁴Department of Data Science, Dana-Farber Cancer Institute, Boston, MA

Aimee K. Hildenbrand, PhD^1,2*, Allison A. King, MD, PhD, MPH^3,4, Constance A Mara, PhD^5*, Yolanda Johnson, MLS^6*, Lisa M Shook, MA^7,8, Catharine Whitacre, MS^9*, Maria T Britto, PhD^10*, Charles T. Quinn, MD^11,12, William Brinkman, MD, MEd^13*, Rogelle Hackworth, BS^9*, Jean L. Raphael, MD, MPH^14,15, Venee N. Tubman, MD^16,17, Alexis A. Thompson, MD, MPH^18,19, Kim Smith-Whitley, MD^20,21, Sherif M. Badawy, MD^22,23, Susan E. Creary, MD, MSc^24,25, Neha Bhasin, MD²⁶, Marsha Treadwell, PhD^27,28*, Steven K Reader, PhD^29*, Angeli Rampersad, MD³⁰, Amy Sobota, MD, MPH³¹ and Lori E. Crosby, PhD^11,32

¹Center for Healthcare Delivery Science, Nemours Children's Health, Wilmington, DE
²Department of Pediatrics, Sidney Kimmel Medical College of Thomas Jefferson University, Philadelphia, PA
³Pediatric Hematology/Oncology, Washington University School of Medicine, Clayton, MO
⁴Washington University School of Medicine, St. Louis, MO
⁵Division of Behavioral Medicine & Clinical Psychology, Cincinnati Children's Hospital Medical Center, CINCINNATI, OH
⁶3333 Burnet Ave, MLC 7039, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
⁷College of Medicine/Department of Pediatrics, University of Cincinnati, Cincinnati, OH
⁸Cancer and Blood Diseases Institute, Cincinnati Childrens Hospital, Cincinnati, OH
⁹Cincinnati Children's Hospital Medical Center, Cincinnati, OH
¹⁰Adolescent and Transition Medicine, Cincinnati Children’s Hospital Medical Center, Cincinnati, OH
¹¹Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH
¹²Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Med. Ctr., Cincinnati, OH
¹³Cincinnati Children's Hospital Medical Center and University of Cincinnati College of Medicine, Cincinnati, OH
¹⁴Center for Child Health Policy and Advocacy, Baylor College of Medicine, Houston, TX
¹⁵Texas Children's Hospital, Houston, TX
¹⁶Department of Pediatrics - Hematology/Oncology, Baylor College of Medicine, Houston, TX
¹⁷Cancer and Hematology Centers, Texas Children's Hospital, Houston, TX
¹⁸Children's Hospital of Philadelphia, Philadelphia, PA
¹⁹University of Pennsylvania, Philadelphia, PA
²⁰Department of Pediatrics, University of Pennsylvania Perelman School of Medicine, Philadelphia, PA
²¹Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA
²²Ann %26 Robert Lurie Children's Hospital, Chicago, IL
²³Northwestern University Feinberg School of Medicine, Chicago, IL
²⁴Center for Innovation in Pediatric Practice, Division of Pediatric Hematology/Oncology/BMT, Nationwide Children's Hospital, Columbus, OH
²⁵Department of Pediatrics, The Ohio State University College of Medicine, Columbus, OH
²⁶Department of Pediatrics, UCSF Benioff Children's Hospitals, Oakland, Oakland, CA
²⁷UCSF, Oakland, CA
²⁸UCSF Benioff Children's Hospital Oakland, Oakland, CA
²⁹Nemours Children’s Health System, Wilmington
³⁰Indiana Hemophilia and Thrombosis Center, Indianapolis, IN
³¹Pediatric Hematology and Oncology, Boston Medical Center, Boston, MA
³²Division of Behavioral Medicine and Clinical Psychology, Children's Hospital Medical Center, Cincinnati, OH

Nicholas W Wilson¹, Lindsey Abel, BS^2*, Kristina Lai, MPH^3*, Marianne M Yee, MD, MSc⁴, Peter Lane, MD^5* and Beatrice E Gee, MD⁶

¹Morehouse School of Medicine, Atlanta, GA
²Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Atlanta, GA
³University of California, Davis, Davis, CA
⁴Center for Transfusion and Cellular Therapies, Department of Pathology and Laboratory Medicine, Department of Pediatrics, Division of Hematology/Oncology, Children's Healthcare of Atlanta; Emory University School of Medicine, Atlanta, GA
⁵Aflac Cancer and Blood Disorders Service, Children's Healthcare of Atlanta, Atlanta, GA
⁶Aflac Cancer and Blood Disorders Service, Children's Healthcare of Atlanta/Emory University, Atlanta, GA

Heather E Stefanski, MD¹, Stephanie Bo-Subait, MPH^2*, Hati Kobusingye, MS^2*, Deborah Mattila, BA^2*, Michelle Kuxhausen, MS^2*, Jennifer Schenfeld, MPH^3*, Darcie Sandschafer, PhD^3*, Cisio De Oliveira Brandao^3*, Linda J Burns, MD^4*, Bronwen E. Shaw, MD, PhD⁵, Michael A. Pulsipher, MD⁶, John P Miller, MD PhD^2* and Steven M Devine, MD⁷

¹CIBMTR® (Center for International Blood and Marrow Transplant Research), National Marrow Donor Program®/Be The Match®, Mendota Heights, MN
²CIBMTR® (Center for International Blood and Marrow Transplant Research), National Marrow Donor Program®/Be The Match®, Minneapolis, MN
³Amgen Inc, Thousand Oaks, CA
⁴CIBMTR® (Center for International Blood and Marrow Transplant Research), Milwaukee, WI
⁵CIBMTR Center for International Blood and Marrow Transplant Research, Department of Medicine, Medical College of Wisconsin, Milwaukee, WI
⁶Division of Pediatric Hematology and Oncology, Intermountain Primary Children’s Hospital/Huntsman Cancer Institute, Spencer Fox Eccles School of Medicine at the University of Utah, Salt Lake City, UT
⁷Center For International Blood and Marrow Transplant Research, Minneapolis, MN

Ektha Parchuri^1*, Danielle Gruen, PhD^1*, Francis X Guyette, MD, MPH^2*, Charles L Jonassaint, PhD, MHS^3*, Joshua B Brown, MD, MSc, FACS^4* and Laura Decastro, MD⁵

¹Department of Emergency Medicine/Surgery, University of Pittsburgh Medical Center, Pittsburgh, PA
²Department of Emergency Medicine, University of Pittsburgh Medical Center, Pittsburgh, PA
³Department of Medicine, University of Pittsburgh Medical Center, Pittsburgh, PA
⁴Department of Surgery, University of Pittsburgh Medical Center, Pittsburgh, PA
⁵Division of Hematology/Oncology/BMT, University of Pittsburgh Medical Center, Pittsburgh, PA

Anil Ananthaneni, MD¹, Taras Benzar, MD^2*, Vishwa Grant, MS-IV^3*, Kenna Leethy, MS-IV^3*, Jacqueline Walton, BSN^2*, Samip R Master, MD², Richard Preston Mansour, MD² and Poornima Ramadas, MD²

¹Internal Medicine, Louisiana State University Health Sciences Center Shreveport, Shreveport, LA
²Hematology and Oncology, Louisiana State University Health Sciences Center Shreveport, Shreveport, LA
³Louisiana State University Health Sciences Center Shreveport, Shreveport, LA

Nanxin Li¹, Jennifer Drahos^1*, Adriana Boateng-Kuffour^1*, Melanie Calvert^2*, Laurice Levine^3*, Neelam Dongha^4*, Zahra Pakbaz, MD⁵, Fikret Kaan Oran^6*, Kamran Iqbal^6*, Farrukh Shah^7* and Antony P. Martin^8*

¹Vertex Pharmaceuticals Incorporated, Boston, MA
²Institute of Applied Health Research, University of Birmingham, Birmingham, United Kingdom
³Independent Consultant, Petaluma, CA
⁴Independent Consultant, London, United Kingdom
⁵Division of Hematology/Oncology, The University of California Irvine School of Medicine, Orange, CA
⁶Vertex Pharmaceuticals (Europe) Ltd, London, United Kingdom
⁷NHS Blood and Transplant, London, United Kingdom
⁸QC Medica, Liverpool, United Kingdom

Luisanna M. Sanchez Ventura, MD¹, Sarah H. O'Brien, MD², Joseph R Stanek, MS^3*, Jonathan M. Flanagan, PhD¹, Wendy Teuchter, BSc^1*, Michael E. Scheurer, PhD, MPH^1* and Jacquelyn M. Powers, MD¹

¹Texas Children's Hematology Center, Baylor College of Medicine, Department of Pediatrics, Section of Hematology/Oncology, Houston, TX
²Division of Pediatric Hematology/Oncology, Nationwide Children's Hospital, Columbus, OH
³Division of Biostatistics, Nationwide Children's Hospital, Columbus, OH

Olusegun Bakare^1*, Stephanie H Guarino, MD^2,3, Carolyn Jenkins, DrPH, MSN, MS, RD, LD, FAAN^4*, Charmaine Wright, MD, MSHP^5*, Keshab Subedi^1*, Sophie M. Lanzkron, MD⁶ and Lee Pachter, DO^1*

¹Institute for Research on Equity and Community Health, ChristianaCare, Newark, DE
²Nemours Dupont Hospital For Children, Wilmington, DE
³Center for Special Health Care Needs/Institute on Research in Equity and Community Health, ChristianaCare, Newark, DE
⁴College of Nursing, Medical University of South Carolina, Mount Pleasant, SC
⁵Center for Special Health Care Needs, ChristianaCare, Newark, DE
⁶Division of Hematology, Department of Medicine, Johns Hopkins School of Medicine, Baltimore, MD

Corinna L. Schultz, MD^1,2, Alison Taggi Pinto^3*, Morgan Thomas, MGC, CGC, LGC^4*, Melanie Pitone, MD^5*, Michael Cellucci, MD^6*, Robin E Miller, MD^2,7, Kim Smith-Whitley, MD^8,9 and Melissa A. Alderfer, PhD^1,3*

¹Department of Pediatrics, Sidney Kimmel Medical College of Thomas Jefferson University, Philadelphia, PA
²Center for Cancer and Blood Disorders, Nemours Children's Health, Wilmington, DE
³Center for Healthcare Delivery Science, Nemours Children's Health, Wilmington, DE
⁴Genetic Stewardship Department, Nemours Children's Health, Wilmington, DE
⁵Center for Healthcare Delivery Innovation, Nemours Children's Health, Wilmington, DE
⁶Diagnostic Referral Service, Newborn Screening Program, Nemours Children's Health, Wilmington, DE
⁷Department of Pediatrics, Sidney Kimmel Medical College, Philadelphia, PA
⁸Global Blood Therapeutics, San Francisco, CA
⁹Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA

Maria Domenica Domenica Cappellini, MD¹, Aylin Yucel, PhD^2*, Juliana Meyers, MA^3*, Maria Jimenez, MPH^3*, Tram Nham, BA^3*, Mrudula B. Glassberg, PHD, MS, BPharm^2* and Ferras Alashkar, MD^4*

¹Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, University of Milan, Milan, Italy
²Bristol Myers Squibb, Princeton, NJ
³RTI Health Solutions, Research Triangle Park, NC
⁴Department of Hematology and Stem Cell Transplantation, West German Cancer Center, University Hospital of Essen, Essen, Germany

Hatoon M. Ezzat, MBBS, FRCP¹, Abdullah Hasan Al Zayed^2*, Hussain H. Al Saeed^2*, Mohamed Al Darwish^2*, Muneer Albagshi^3*, Hafiz Malhan^4*, Ahmad Tarawah^5*, Aljawhara Al Manea^6*, Iman Alhazmi^6*, Mohamed Qari^7*, Azzah Alzahrani^8*, Mohsen Alzahrani, MD^9*, Wesam Soliman^10*, Farid Askar^10*, Al Shaimaa Yassin^10* and Wasil Jastaniah, MBBS, FRCPC^11*

¹MOH, Johns Hopkins Aramco Healthcare, Dahran, Saudi Arabia
²Qatif Central Hospital, Qatif, Saudi Arabia
³Almana General Hospital-Al Ahsa, Hofouf, Saudi Arabia
⁴Prince Mohamed bin Naser, Jizan, Saudi Arabia
⁵King Salman Medical City Al Madinah, Madinah, Saudi Arabia
⁶King Fahad Armed Forces Hospital, Jeddah, Saudi Arabia
⁷King Abdulaziz University Hospital, Jeddah, Saudi Arabia
⁸Prince Sultan Military Medical City, Riyadh, Saudi Arabia
⁹King Abdulaziz Medical City, Riyadh, Saudi Arabia
¹⁰Novartis Saudi Ltd, Riyadh, Saudi Arabia
¹¹King Faisal Specialist Hospital & Research Center (Gen. Org.), Jeddah, Saudi Arabia

Sydney M. Forman, BS^1*, Megan E. Connolly, PhD^1,2* and Steven J. Hardy, PhD^1,2

¹Division of Hematology, Children's National Hospital, Washington, DC
²Departments of Psychiatry & Behavioral Sciences and Pediatrics, George Washington University School of Medicine and Health Sciences, Washington, DC

Vaishnavi Siripurapu, BSc, BA^1* and Regina Crawford, MD²

¹East Carolina University Brody School of Medicine, Greenville, NC
²Duke University Medical Center, Durham, NC

Sudipto Mukherjee, MD, PhD, MPH¹, Matthew Franklin^2*, Francis Shupo^3*, Nicola Mason^4*, Grace Wayi-Wayi^3*, Natasa Zibelnik^3*, Mileva Repasky^5* and John Brazier^2*

¹Department of Hematology/Oncology, Cleveland Clinic, Cleveland, OH
²School of Health and Related Research, Sheffield, United Kingdom
³EUSA Pharma, Hemel Hempstead, United Kingdom
⁴Lumanity, Sheffield, United Kingdom
⁵Castleman Disease Collaborative Network, Paso Robles, CA

Kyaw Zin Thein, MD^1*, Thura Win Htut, MBBS, MRCP^2*, Myat Min Han, MD^3*, Yin Mon Myat, MBBS^4*, Myint Aung Win, MD, MBBS^5*, Ei Moe Phyu, MD^5* and Thein H. Oo, MD, FRCPE, FACP⁶

¹Oregon Health & Science University/ Knight Cancer Institute, PORTLAND, OR
²Hematology department, Aberdeen Royal Infirmary Hospital, Aberdeen, United Kingdom
³Interfaith Medical Center, Brooklyn
⁴University College Dublin, Dublin, Ireland
⁵Internal Medicine, LewisGale Medical Center, Salem, VA
⁶Section of Benign Hematology, The University of Texas MD Anderson Cancer Center, Houston, TX

Abiola Oladapo, PhD^1*, Scott Kolodny, MD^1*, Michael Vredenburg, PhD^1*, Brian Jamieson, MD¹, Elyse Swallow^2*, Debbie Goldschmidt, PhD^3*, Miriam L. Zichlin, MPH^2*, Mikhail Davidson^2*, Louise Yu, MSc^2* and John Yee, MD, MPH^1*

¹Sobi, Inc., Waltham, MA
²Analysis Group, Inc., Boston, MA
³Analysis Group, Inc., New York, NY

Frederic Karim, MD^1*, Nima Ghalehsari, MD², Andy Y. Huang, MD^3* and Ayanna Baptiste, MBBS²

¹NewYork Presbyterian Brooklyn Methodist Hospital, Brooklyn
²NewYork-Presbyterian Brooklyn Methodist Hospital, Brooklyn, NY
³NewYork-Presbyterian Brooklyn Methodist Hospital, Brooklyn

Janet Chupka, BSN, RN^1*, Marquita Decker-Palmer, MD, PhD^2*, Chia-Wei Lin, MD^2*, Ashley Martin, PhD, MS^3*, Kushal Modi^3*, Dawn Bates^3* and Karen Thomson, MA^3*

¹Hemophilia Federation of America, Washington, DC
²Genentech, Inc., South San Francisco, CA
³Cerner Enviza, North Kansas City, MO

Clemence Aldebert^1*, Mony Fahd, MD MSc^2*, Jacques-Emmanuel Galimard, PhD^3*, Ibrahim A. Ghemlas, MD^4*, Marco Zecca, MD^5*, Juliana Silva, MD^6*, Alexander Mohseny^7*, Alphan Kupesiz, MD^8*, Rose-Marie Hamladji, MD, PhD^9*, Nuno Miranda^10*, Tayfun Gungor^11*, Robert F Wynn, MRCP, MD, FRCPath¹², Pietro Merli, MD^13*, Mikael Sundin, MD, PhD¹⁴, Maura Faraci, MD^15*, Cristina Díaz-de-Heredia, MD, PhD^16*, Birgit Burkhardt, MD, PhD^17*, Victoria Bordon, MD, PhD^18*, Charlotte Jubert, MD^19*, Peter Bader, MD, PhD²⁰, Marianne Ifversen, MD, PhD^21*, Concepcion Herrera Arroyo, MD^22*, Natalia Maximova^23*, Susana Riesco^24*, Jerry Stein, MD^25*, Arnaud Dalissier, PhD^26*, Franco Locatelli, Prof., MD, PhD²⁷, Krzysztof Kalwak, MD, PhD^28*, Jean-Hugues Dalle, MD, PhD¹ and Selim Corbacioglu, MD²⁹

¹Pediatric Hematology and Immunology Department, Robert Debré Hospital , GHU APHP Nord - Université Paris Cité, Paris, France
²Pediatric Hematology and Immunology Department, Robert-Debré Hospital, GH APHP Nord Université de Paris, Paris, France
³EBMT Statistical Unit, Sorbonne University, Saint-Antoine Hospital, AP-HP, INSERM UMRs 938, Paris, France
⁴Department of Pediatric Hematology-Oncology, King Faisal Specialist Hospital & Research Center, Saudi Arabia, Riyadh, Saudi Arabia
⁵Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy
⁶Bone Marrow Transplant Department, Great Ormond Street Hospital, London, United Kingdom
⁷Division of stem cell transplantation, Willem-Alexander Children’s Hospital, Leiden University Medical Center, Leiden, Netherlands
⁸Pediatric Hematology, Akdeniz University Medical School, Antalya, TUR
⁹Service Hématologie Greffe de Moëlle, Centre Pierre Et Marie Curie, Alger, Algeria
¹⁰BMT, Instituto Portugues de Oncologia, Lisboa, PRT
¹¹Division of Stem Cell Transplantation, The Hospital of the Eleonore Fondation,University Children`s Hospital, ZüRich, Switzerland
¹²Department of Paediatric Haematology, Bone Marrow Unit, Royal Manchester Children's Hospital, Manchester, United Kingdom
¹³Department of Pediatric Hematology/Oncology, Cell and Gene Therapy, IRCCS Bambino Gesù Children’s Hospital, Rome, Italy
¹⁴Division Pediatric Hematology, Immunology and HCT, Pediatric Hematology, Immunology and HCT Section, Astrid Lindgren Children's Hospital, Karolinska University Hospital and Division of Pediatrics, CLINTEC, Karolinska Institutet, Stockholm, Sweden
¹⁵Unità di Trapianto di Cellule Staminali Emopoietiche - Department of Hematology, Oncology and Hematopoietic Stem Cell Transplantion, IRCSS, Istituto Giannina Gaslini, Genova, Italy
¹⁶Pediatric Oncology and Hematology Department, Hospital Universitari Vall d’Hebron Vall d’Hebron, Barcelona, Spain
¹⁷Pediatric Hematology and Oncology, University Hospital Münster, Münster, Germany
¹⁸Department of Pediatric Hematology-Oncology and Stem Cell Transplantation, Ghent University Hospital, Ghent, Belgium
¹⁹Hematology Pediatrics, CHU Bordeaux, Bordeaux Cedex, France
²⁰Department for Children and Adolescents, Division for Stem Cell Transplantation, Immunology and Intensive Care Medicine, University Children's Hospital Frankfurt, Frankfurt, Germany
²¹Department of Paediatric and Adolescent Medicine, Copenhagen University Hospital Rigshospitalet,, Copenhagen, Denmark
²²Department of Hematology, Reina Sofia University Hospital / University of Cordoba, Cordoba, Spain
²³Bone Marrow Transplant Center, Institute for Maternal and Child Health - IRCCS Burlo Garofolo, Trieste, Italy
²⁴Department of Pediatrics, Hospital Universitario de Salamanca-IBSAL, Salamanca, Spain
²⁵Department for Hemato-Oncology, Schneider Children's Medical Center of Israel, Petach Tikva, Israel
²⁶EBMT Paris Study Unit, Sorbonne University, Saint-Antoine Hospital, AP-HP, INSERM UMRs 938, Paris, France
²⁷Department of Pediatric Hematology/Oncology, Cell and Gene Therapy, IRCCS Bambino Gesù Children's Hospital, Rome, Italy
²⁸Department of Pediatric Hematology, Oncology and Bone Marrow Transplantation, Wroclaw Medical University, Wroclaw, Poland
²⁹Department of Pediatric Hematology, Oncology and Stem Cell Transplantation, University of Regensburg, Regensburg, Germany