Stefano Giardino, MD^1*, Dirk-Jan Eikema^2,3*, Brian Piepenbroek^4*, Mattia Algeri, MD^5*, Mouhab Ayas, MD⁶, Maura Faraci, MD^7*, Abdelghani Tbakhi, MD^8*, Marco Zecca, MD^9*, Mohammed Essa^10*, Bénédicte Neven, MD, PhD^11*, Yves Bertrand, MD, PhD^12*, Gaurav Kharya^13*, Tatiana A Bykova, MD, PhD^14*, Sarah Lawson, MBBS FRCPath^15*, Mario Petrini¹⁶, Alexander Mohseny^17*, Fanny Rialland, MD^18*, Beki James^19*, Anca Colita, MD^20*, Mony Fahd, MD MSc^21*, Simone Cesaro, MD^22*, Ansgar Schulz, MD^23*, Carlo Dufour, MD²⁴, Antonio M Risitano, MD, PhD^25,26 and Regis Peffault De Latour^27*

¹Unità di Trapianto di Cellule Staminali Emopoietiche - Dipartimento di Ematologia, Oncologia e Trapianto di Cellule Staminali Emopoietiche, IRCCS Istituto Giannina Gaslini, Genova, Italy
²LUMC, Dept. Medical Statistics & Bioinformatics, Leiden, Netherlands
³EBMT Statistical Unit, Leiden, Netherlands
⁴EBMT Leiden Study Unit, Leiden, Netherlands
⁵Department of Pediatric Hematology/Oncology, Cell and Gene Therapy, IRCCS Bambino Gesù Children's Hospital, Rome, Lazio, Italy
⁶Department of Pediatric Hematology/Oncology, King Faisal Specialist Hospital & Research Center, Riyadh, Middle, Saudi Arabia
⁷Unità di Trapianto di Cellule Staminali Emopoietiche - Department of Hematology, Oncology and Hematopoietic Stem Cell Transplantion, IRCSS, Istituto Giannina Gaslini, Genova, Italy
⁸King Hussein Cancer Centre, Amman, Jordan
⁹Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy
¹⁰Ministry of National Guard Health Affairs, King Abdulaziz Medical City, Riyadh, SAU
¹¹Pediatric Immunology, Hematology and Rheumatology Unit, Hôpital Necker-Enfants Malades, AP-HP, Paris, France
¹²Unité de coordination interne et externe, Institut d`Hematologie et d`Oncologie Pediatrique, Lyon, France
¹³Indraprastha Apollo Hospitals, New Delhi, India
¹⁴RM Gorbacheva Research Institute, Pavlov University, St. Petersburg, Russian Federation
¹⁵Birmingham Children's Hospital, Birmingham, United Kingdom
¹⁶Azienda Ospedaliero Universitaria Pisana, Department of Clinical and Experimental Medicine, Hematology, Pisa, Italy
¹⁷Division of stem cell transplantation, Willem-Alexander Children’s Hospital, Leiden University Medical Center, Leiden, Netherlands
¹⁸Service Onco-Hématologie Pédiatrique, Hôpital Mère-Enfant, Nantes University Hospital, Nantes, France
¹⁹Leeds Children's Hospital, Leeds Teaching Hospitals NHS Trust, Leeds, United Kingdom
²⁰Fundeni Clinical Institute, University of Medicine Carol Davila, Bucharest, ROU
²¹Pediatric Hematology and Immunology Department, Robert-Debré Hospital, GH APHP Nord Université de Paris, Paris, France
²²Pediatric Hematology-Oncology, Ospedale della Donna e del Bambino, Azienda Ospedaliera Universitaria Integrata, Verona, Italy
²³Department of Pediatrics, University Medical Center, Ulm, Germany
²⁴Department of Hemato-Oncology,, Hematology Unit, IRCCS G. Gaslini Children's Hospital, Genova, Italy
²⁵Hematology and Hematopoietic Transplantation, AORN S. Giuseppe Moscati Avellino, Avellino, Italy
²⁶Department of Clinical Medicine and Surgery, Federico II University of Naples, Naples, Italy
²⁷Hematology and Transplantation Unit, Hôpital Saint Louis, AP-HP, Paris, France

Masanori Yoshida, MD, PhD^1*, Felicia Andresen, MD², Hermann Yang^3*, Sara Lewis, MS, CGC^4*, Miriam Erlacher, MD, PhD^2,5*, Dirk Lebrecht, PhD^2*, Akiko Shimamura, MD, PhD^3*, Charlotte M. Niemeyer^2,5, Sushree S Sahoo, PhD¹ and Marcin W. Wlodarski, MD, PhD^1,6

¹Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN
²Division of Pediatric Hematology and Oncology, Department of Pediatrics and Adolescent Medicine, University of Freiburg, Freiburg, Germany
³Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Boston, MA
⁴Department of Hematology, St Jude Children's Research Hospital, Lakeland, TN
⁵German Cancer Consortium (DKTK), Heidelberg, Germany
⁶University of Freiburg, Freiburg, Germany

Sarada Ketharnathan, PhD¹, Sergey V Prykhozhij, PhD^1*, Anna Cordeiro, PhD², Yigal Dror, MD, FRCPC^3,4 and Jason N. Berman, MD⁵

¹CHEO Research Institute, Ottawa, ON, Canada
²AGADA Biosciences, Halifax, NS, Canada
³Institute of Medical Science, University of Toronto, Toronto, ON, Canada
⁴Marrow Failure and Myelodysplasia Program, Division of Hematology/Oncology, Department of Pediatrics, Hospital for Sick Children, Toronto, ON, Canada
⁵Department of Pediatrics, CHEO Research Institute, Ottawa, ON, Canada

Narasaiah Kovuru, PhD¹, Greer Jeffery, BA^1*, Theresa Menna, BS^1*, Yuning Hong, PhD^2*, Zhe Zhang, PhD^3*, Makiko Mochizuki Kashio, PhD^4* and Peter Kurre, MD⁵

¹Comprehensive Bone Marrow Failure Center, Department of Pediatrics, Children's hospital of Philadelphia, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
²Department of Biochemistry and Chemistry, La Trobe Institute for Molecular Science, La Trobe University, Melbourne, Australia
³Biostatistics and Bioinformatics Core, Gene Therapy Program, University of Pennsylvania, Philadelphia, PA
⁴Department of Microscopic and Developmental Anatomy, Tokyo Women’s Medical University, Tokyo., Japan
⁵Comprehensive Bone Marrow Failure Center, Children's hospital of Philadelphia, Philadelphia, PA

Juraj Kokavec, PhD^1*, Jan Procházka, PhD^2*, Tomas Stopka, MD, PhD¹ and Radislav Sedlacek, PhD^2*

¹BIOCEV, First Faculty of Medicine, Charles University, Prague, Czech Republic
²Czech Centre for Phenogenomics (BIOCEV / IMG), Institute of Molecular Genetics of the Czech Academy of Sciences, Prague, Czech Republic

Clarissa Gervasoni^1*, Alice Martina Giussani, PhD Student^1*, Nadia Bertola, PhD Student^2*, Erica Dander, PhD^1*, Andrea Biondi, MD^1,3, Paola Corti, MD^3*, Piero Farruggia, MD^4*, Giuseppe Menna, MD^5*, Marco Cipolli, MD^6*, Valentino Bezzerri, PhD^6*, Anna Pegoraro, MD^6*, Simone Cesaro, MD^7*, Carlo Dufour, MD⁸, Enrico Cappelli, MD^9*, Silvia Ravera, PhD^2* and Giovanna D'Amico, BSc, PhD, MSc^1*

¹Tettamanti Research Center, Department of Pediatrics, University of Milano - Bicocca/Fondazione MBBM, Monza, Italy
²Department of Experimental Medicine, University of Genoa, Genoa, Italy
³Pediatric Hemato-Oncolgy, Fondazione MBBM/ASST-Monza, University of Milano-Bicocca, Monza, Italy
⁴Pediatric Hematology and Oncology Unit, A.R.N.A.S. Ospedale Civico, Palermo, Italy
⁵Pediatric Hemato-Oncology Unit, Santobono-Pausilipon Hospital, Naples, Italy
⁶Cystic Fibrosis Center, Azienda Ospedaliera Universitaria Integrata, Verona, Italy
⁷Pediatric Hematology-Oncology, Department of Mother and Child, Azienda Ospedaliera Universitaria Integrata, Verona, Italy
⁸Department of Hemato-Oncology,, Hematology Unit, IRCCS G. Gaslini Children's Hospital, Genova, Italy
⁹Hematology Unit, IRCCS G. Gaslini Children's Hospital, Genoa, Italy

Brynn B Duncan, MD^1,2*, Jennifer Lotter, PA-C^3*, Jeanine Superata, RN^3*, Ma Evette Barranta, BS^4*, Ivana Darden, RN^3*, Sanjay Venugopal^4*, Colin O. Wu, PhD^5*, Cynthia E. Dunbar, MD⁶ and David J. Young, MD, PhD³

¹Pediatric Oncology Branch, NCI, Bethesda, MD
²Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health (NHLBI/NIH), Bethesda, MD
³Hematology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
⁴Office of the Clinical Director, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
⁵Office of Biostatistics Research, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
⁶Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda

Nidhi Aggarwal, BS¹, Xiaoyang Ma, MS^2*, Fernanda Gutierrez-Rodrigues, PhD³, Ruba Shalhoub, MS^2*, Ivana Darden, RN^1*, Bhavisha A. Patel, MD¹, Colin O. Wu, PhD^2*, Neal S. Young, MD¹ and Emma M. Groarke, MD¹

¹Hematology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
²Office of Biostatistics Research, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, MD
³Hematology Branch, National Heart, Lung, and Blood Institute, National Institute of Health, Bethesda, MD

Anne Olazabal Herrero^1,2, Fengshan Liang, PhD^3*, Arijit Dutta, PhD^4*, Yuxin Huang, PhD^4*, Zhuobin Liang, PhD^5*, Abhishek K Gupta, PhD^3*, Li Lan^6*, Manoj M Pillai, MD³, Patrick Sung, PhD^7* and Gary M. Kupfer, MD⁸

¹Department of Oncology, Georgetown University, Washington, DC
²Department of Internal Medicine, Yale University School of Medicine, New Haven, CT
³Department of Internal Medicine, Section of Hematology, Yale University School of Medicine, New Haven, CT
⁴Department of Biochemistry and Structural Biology, University of Texas Health Science Center at San Antonio, San Antonio, TX
⁵Institute of Molecular Physiology, Shenzhen, China
⁶Harvard Medical School, Boston, MA
⁷Department of Biochemistry and Structural Biology, University of Texas Health Sciences Center San Antonio, San Antonio, TX
⁸Department of Oncology, Georgetown University, washington, DC