-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

114. Hemoglobinopathies, Excluding Thalassemia: Clinical and Epidemiological: Poster II

Symposia: Hemoglobinopathies, Excluding Thalassemia: Clinical and Epidemiological Program: Oral and Poster Abstracts
Type: Poster
Sunday, December 11, 2022: 6:00 PM-8:00 PM
Hall D (Ernest N. Morial Convention Center)

Camille Roussel, MD, PhD1,2,3*, Sandra Manceau2,4*, Zeynep Cacan3*, Celine Gounou5*, Laurent Sabbah6*, Alain Brisson5*, Lucie Dumas2,7*, Delphine Borgel, PhD, PharmD3,8* and Laure Joseph, MD9*

1Université Paris Cité and Université des Antilles, Inserm, BIGR, Paris, France
2Laboratoire d’Excellence GR-Ex, Paris, France
3General hematology department, Hôpital Necker, Assistance-Publique Hôpitaux de Paris, Paris, France
4Biotherapy Department, French National Sickle Cell Referral Center, Hôpital Necker, Assistance-Publique Hôpitaux de Paris, Paris, France
5University of Bordeaux, CNRS, Bordeaux INP, CBMN, UMR 5248, Pessac, France
6Unité de cardiologie adulte, Hôpital Necker, Assistance-Publique Hôpitaux de Paris, Paris, France
7Université Paris Cité and Université des Antilles, Inserm, BIGR, PARIS, France
8Université Paris-Saclay, HITh, UMR_S1176, INSERM, le Kremlin Bicêtre, France
9Biotherapy Department, French National Sickle Cell Referral Center, Hôpital Necker, Assistance-Publique Hôpitaux de Paris, Paris, DC, France

Kristine Anne Karkoska, MD, MS1, Russell Sawyer, MD2* and Hyacinth I Hyacinth, MD, PhD, MPH3

1Division of Hematology/Oncology, Dept of Internal Medicine, University of Cincinnati College of Medicine, Cincinnati, OH
2Department of Neurology and Rehabilitation Medicine, University of Cincinnati Medical Center, Cincinnati, OH
3Department of Neurology and Rehabilitation Medicine, University of Cincinnati, Cincinnati, OH

Nirmish Shah, MD1, Clark Brown, MD, PhD2, Biree Andemariam, MD3, Modupe Idowu, MD4, Alexander Glaros, MD5, Jeffrey Glassberg, MD6*, Robert M Cronin, MD, MS7, Barbara Moehring, PharmD8*, Carolyn Hoppe, MD8*, Sandy Dixon8* and Deepa Manwani, MD9

1Department of Medicine, Division of Hematology - Duke Sickle Cell Comprehensive Care Unit, Duke University Hospital, Durham, NC
2Department of Pediatrics, Emory University School of Medicine, Atlanta, GA
3University of Connecticut Health, West Hartford, CT
4University of Texas McGovern Medical School, Houston, TX
5Children's Hospital of Michigan, Department of Pediatrics, Division of Pediatric Hematology-Oncology, Central Michigan University, Detroit, MI
6Icahn School of Medicine at Mount Sinai, New York City, NY
7Department of Internal Medicine, The Ohio State University, Hilliard, OH
8Global Blood Therapeutics, South San Francisco, CA
9Division of Pediatric Hematology/Oncology, Department of Pediatrics, Children's Hospital at Montefiore, Albert Einstein College of Medicine, Bronx, NY

Mycal Casey, DO, MPH1, Brandon Gramazio, PhD2,3*, Florence Urum, BS4*, Niren Patel, MBBS2*, Wenbo Zhi, PhD5* and Abdullah Kutlar, MD6

1Internal Medicine, Medical College of Georgia At Augusta University, Augusta, GA
2Center for Blood Disorders, Augusta University/Medical College of Georgia, Augusta, GA
3Augusta University, Augusta, GA
4Augusta University, Medical College of Georgia, Augusta, GA
5Center for Biotechnology and Genomic Medicine, Augusta University, Augusta, GA
6Department of Medicine, Sickle Cell Center, Augusta University, Augusta, GA

Abena Appiah-Kubi, MD, MPH1, Seethal A Jacob, MD, MS2, Matthew M. Heeney, MD3, Clark Brown, MD, PhD4, Susan E. Creary, MD, MSc5, Christine R Hollenkamp, APRN6*, Emily Riehm Meier, MD, MSHS4*, Omar Niss, MD7, Connie M. Piccone, MD8, Maa-Ohui Quarmyne, MBChB MS9, Charles T. Quinn, MD7, Allison Remiker, MD10*, Kay L Saving, MD11, Min Dong12* and Patrick T. McGann, MD, PhD13,14

1Cohen Children's Medical Center, Northwell Health, New Hyde Park, NY
2Center for Pediatric and Adolescent Comparative Effectiveness Research, Riley Hospital For Children, Indianapolis, IN
3Pediatric Hematology-Oncology, Children's Hospital - Boston, Boston, MA
4Global Blood Therapeutics, South San Francisco, CA
5Center for Innovation in Pediatric Practice, Division of Pediatric Hematology/Oncology/BMT, Nationwide Children's Hospital, Columbus, OH
6Children's Minnesota, Minneapolis, MN
7Division of Hematology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
8Carle Foundation Hospital, Urbana, IL
9Hematology/Oncology, Phoenix Children's Medical Group, Phoenix, AZ
10Medical College of Wisconsin, Wisconsin
11University of Illinois Chicago, Peoria, IL
12Division of Clinical Pharmacology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
13Department of Pediatrics, The Warren Alpert Medical School of Brown University, Providence, RI
14Lifespan Comprehensive Sickle Cell Center, Providence, RI

Keli C Coleman1*, Kenneth McKinley, MD2*, Angela Ellison3*, Amanda M. Brandow, DO, MS4, Blake Nielsen, MS5*, Lawrence Cook, PhD5*, Elizabeth Alpern, MD, MSCE6*, Selena Hariharan, MD7*, Irina Topoz, MD8*, Morgan Wurtz, MD9*, Claudia R. Morris, MD10,11, Andrew D. Campbell, MD12, Robert Liem, MD13, Rachelle Nuss, MD14*, Charles T. Quinn, MD15, Alexis A. Thompson, MD, MPH16, Anthony Villella, MD9*, Ana Baumann, PhD17*, Allison A. King, MD, PhD, MPH18, Warren Frankenberger, PhD16* and David C Brousseau, MD, MS19

1Medical College of Wisconsin and the Children's Research Institute of Children's Wisconsin, Milwaukee, WI
2Children's National Medical Center, Washington, DC
3Department of Pediatrics, Children's Hospital of Philadelphia, Philadelphia, PA
4Pediatric Hematology/Oncology, Medical College of Wisconsin and Children’s Research Institute of the Children’s Hospital of Wisconsin, Milwaukee, WI
5University of Utah, Salt Lake City, UT
6Lurie Children's Hospital, Chicago, IL
7Cincinnati Children's Hospital, Cincinnati, OH
8Department of Pediatrics, Children's Colorado, Denver, CO
9Nationwide Children's Hospital, Columbus, OH
10Department of Pediatrics, Emory University School of Medicine, Atlanta, GA
11Childrens Healthcare of Atlanta, Atlanta, GA
12Center for Cancer and Blood Disorders, Childrens National Hospital, Washington, DC
13Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
14Center for Cancer and Blood Disorders, University of Colorado Anschutz Medical Campus, Aurora, CO
15Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Med. Ctr., Cincinnati, OH
16Children's Hospital of Philadelphia, Philadelphia, PA
17Washington University School of Medicine, St Louis, MO
18Pediatric Hematology/Oncology, Washington University School of Medicine, Clayton, MO
19Department of Pediatrics, Medical College of Wisconsin and the Children's Research Institute at Children's Wisconsin, Milwaukee, WI

Biree Andemariam, MD1, Pernille Højlund Nielsen2*, Rikke Zillmer, MSc, PhD2* and Julie Derving Karsbøl, MD2*

1New England Sickle Cell Institute, University of Connecticut Health, Farmington, CT
2Novo Nordisk A/S, Soeborg, Denmark

Patrick T. McGann, MD, PhD1,2, Christine Briscoe, MSN, RN2*, Margarida Muhongo3*, Rui Pascoal3*, J. Ray Tanzer, PhD4*, Roxanne Wood5*, Anastacia da Conceicao Nguvela, MD6* and Eugenia Alberto Mateus, MSN6*

1Department of Pediatrics, The Warren Alpert Medical School of Brown University, Providence, RI
2Lifespan Comprehensive Sickle Cell Center, Providence, RI
3Hospital Pediátrico David Bernardino, Luanda, Angola
4Lifespan Biostatistics, Epidemiology, and Research Design, Providence, RI
5Brown University Oncology Research Group, Providence, RI
6Hospital Geral dos Cajueiros, Luanda, Angola

Deva Sharma, MD, MS1 and Ilknur Kozanoglu, MD, Prof.2,3*

1Hematology-Oncology & Transfusion Medicine, Vanderbilt University Medical Center, Nashville, TN
2Hematology, Baskent University, Adana, Turkey
3Faculty of Medicine, Baskent University, Ankara, Turkey

Xiaoshu Dai Gurov, PhD1*, Elizabeth Merica2*, Varsha Iyer, PhD1*, Annie Claeys1*, Spurthi Patil1*, Rolandas Urbstonaitis, MBA, PharmD1*, James Xiao, PhD1* and Michael U. Callaghan, MD1

1Agios Pharmaceuticals, Inc., Cambridge, MA
2Merica Clinical Consulting LLC, Boston, MA

Landon C. Power1*, Michael M. Binkley, PhD2*, Kristin P. Guilliams, MD, MSCI2,3*, Jade Beshears, BA2*, Amal Hamed, BA3*, Anna M Hood, PhD4*, Jin-Moo Lee, MD, PhD2,5,6*, Andria L. Ford, MD, MSCI2,5*, Allison A. King, MD, PhD, MPH7 and Melanie E. Fields, MD8

1Department of Pediatrics, Washington University School of Medicine, Hastings, NE
2Department of Neurology, Washington University School of Medicine, Saint Louis, MO
3Department of Pediatrics, Washington University School of Medicine, Saint Louis, MO
4Division of Psychology & Mental Health, The University of Manchester, Manchester, United Kingdom
5Mallinckrodt Institute of Radiology, Washington University School of Medicine, Saint Louis, MO
6Department of Biomedical Engineering, Washington University School of Medicine, Saint Louis, MO
7Pediatric Hematology/Oncology, Washington University School of Medicine, Clayton, MO
8Division of Pediatric Hematology/Oncology, Washington University in St. Louis, Saint Louis, MO

Chibuzo C Ilonze, MD, MPH1, Najibah Aliyu Galadanci, MBBS, MPH2, Dakshin Padmanabhan, MBBS3*, Ammar Saadoon, MD4*, Brandi Pernell, DNP5* and Jeffrey D. Lebensburger, DO, MSPH6

1Division of Pediatric Hematology and Oncology, Department of Pediatrics, University of Alabama at Birmingham, Birmingham, AL
2School of Public Health/Epidemiology, University of Alabama at Birmingham, Birmingham, AL
3Pediatric Hematology/ Oncology, University of Alabama at Birmingham, Birmingham, AL
4Division of Pulmonology and Sleep Medicine, Department of Pediatrics, University of Alabama at Birmingham, Birmingham, AL
5Division of Pediatric Hematology Oncology, University of Alabama at Birmingham, Birmingham, AL
6Division of Pediatric Hematology Oncology, University of Alabama At Birmingham, Birmingham, AL

Jinxia Yao1*, Andrew RW O'Brien, MD2, Yunjie Tong, PhD1* and Ying Wang, MD, PhD3*

1Purdue University, West Lafayette, IN
2Division of Hematology/Oncology, Indiana University School of Medicine, Indianapolis, IN
3Department of Anesthesia, Stark Neurosciences Research Institute, Indiana University School of Medicine, Indianapolis, IN

Emily M. Harris, MD1*, Emily Vilk, NP2*, Carolina Donado, MD, MBI3,4*, Alexis Williams, MD5*, Matthew M. Heeney, MD6, Jean Solodiuk, RN, PhD3,4*, Christine Greco, MD3,4* and Natasha M. Archer, MD1

1Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Boston, MA
2Division of Hematology,, Boston Children’s Hospital, Boston, MA
3Department of Anesthesiology, Critical Care, and Pain Medicine, Boston Children's Hospital, Boston, MA
4Department of Anaesthesia, Harvard Medical School, Boston, MA
5Department of Pediatrics, Boston Children's Hospital, Boston, MA
6Pediatric Hematology-Oncology, Children's Hospital - Boston, Boston, MA

William Beau Mitchell, MD1,2, Kaitlin L Strumph, DO, MSc3,4, Kerry A Morrone, MD5, Parmpreet Dhillon, MD1*, Kevin Hsu, MD1* and Deepa Manwani, MD6

1Children's Hospital at Montefiore, Bronx, NY
2Albert Einstein College of Medicine, Bronx, NY
3Division of Pediatric Hematology/Oncology, Department of Pediatrics, Children's Hospital at Montefiore, Albert Einstein College of Medicine, New York, NY
4Montefiore Medical Center, Albert Einstein College of Medicine, Bronx, NY
5Division of Pediatric Hematology, Oncology and Cellular Therapy, Children's Hospital At Montefiore, Bronx, NY
6Division of Pediatric Hematology/Oncology, Department of Pediatrics, Children's Hospital at Montefiore, Albert Einstein College of Medicine, Bronx, NY

Angela Liu, MD1*, Susanna Curtis, MD, PhD2, Paola Sebastiani, PhD3*, Donald Brambilla, PhD4 and Jeffrey A. Glassberg, MD5

1Tisch Cancer Institute, Division of Hematology and Medical Oncology, Icahn School of Medicine at Mount Sinai, New York, NY
2Icahn School of Medicine at Mount Sinai, New York
3Statistics, Boston University School of Public Health, Boston, MA
4RTI International, Rockville, MD
5Division of Hematology and Oncology, Department of Medicine and Department of Emergency Medicine, Mount Sinai Medical Center, New York, NY

Kiranveer Kaur, MD, Annum Faisal, MD, Katie Kennedy, DO, Charles L. Knupp, MD and Darla Liles, MD

Division of Hematology Oncology, East Carolina University, Greenville, NC

Ryan Sun, MD1*, Jin Han, PharmD, PhD2*, James P. Lash, MD1*, Victor R. Gordeuk, MD3 and Santosh L. Saraf, MD4

1University of Illinois at Chicago, Chicago
2Department of Pharmacy Practice, University of Illinois at Chicago, Chicago, IL
3Department of Medicine, University of Illinois at Chicago, Chicago, IL
4Comprehensive Sickle Cell Center, Section of Hematology/Oncology, Department of Medicine, University of Illinois at Chicago, Chicago, IL

Tyler J Barrett1*, Andrew Pucka, Undergraduate1*, Brandon Reyes, BS1*, Seethal A Jacob, MD, MS2, Andrew RW O'Brien, MD3, Richard E. Harris, PhD4*, Steven Harte, PhD4* and Ying Wang, MD, PhD1*

1Department of Anesthesia, Indiana University School of Medicine, Indianapolis, IN
2Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN
3Division of Hematology/Oncology, Indiana University School of Medicine, Indianapolis, IN
4Department of Anesthesiology, University of Michigan Medical School, Ann Arbor, MI

Joanna E. Papadakis, BSc1*, Paulina Piwowarczyk, BA2*, Daniel S. Weber, BS2*, Anna L. Slingerland, BS2*, Dylan S. Keusch2*, Matthew M. Heeney, MD3, Edward R. Smith, MD2*, Alfred P. See, MD2* and Natasha M. Archer, MD4

1Department of Neurosurgery, Boston Children's Hospital, BOSTON, MA
2Department of Neurosurgery, Boston Children's Hospital, Boston, MA
3Pediatric Hematology-Oncology, Children's Hospital - Boston, Boston, MA
4Pediatric Hematology-Oncology, Dana-Farber / Boston Children’s Cancer and Blood Disorders Center, Boston, MA

Kennedy N Goldsborough, BSc1*, Molly Sonenklar, MD2*, Kalpna Gupta, PhD3, M Imad Damaj, PhD1*, Wally R Smith, MD4, Joyce Lloyd, PhD5* and Aron Lichtman, PhD1*

1Pharmacology and Toxicology, Virginia Commonwealth University, Richmond, VA
2Pediatric Hematology/Oncology, Children's Hospital of Richmond, Richmond
3Department of Medicine, Division of Hematology/Oncology, University of California, Irvine, Irvine, CA
4Internal Medicine, Virginia Commonwealth University, Richmond, VA
5Virginia Commonwealth University, Richmond, VA

Ibrahim Musa Idris, MBBS, MPH, FMCPath1, Aminu Abba Yusuf, MBBS, MSc, FMCPath1*, Ismail Isa Ismail, MBBS2*, Awwal Musa Borodo, MBBS, FMCPath3*, Mustapha Shuaibu Hikima, MBBS, FMCRad4*, Shehu Kana, MBBS, FWACP5*, Sani A Aji, MBBS, FWACS6*, Aisha Kuliya_Gwarzo, MBBS, MSc, FMCPath7*, Mohammad Kabir, BPharm8*, Jamil Aliyu Galadanci, MSc9*, Rukayya Alkassim, MSc10*, Nafiu Hussain, PhD11*, Mark Rodeghier, PhD12*, Aurthur Burnett, MD, PhD13* and Michael R. DeBaun, MD, MPH14

1Hematology, Aminu Kano Teaching Hospital/Bayero University Kano, Kano, Nigeria
2Aminu Kano Teaching Hospital, Kano, Nigeria
3Department of Hematology, Murtala Mohammed Specialist Hospital, Kano, Nigeria
4Radiology, Muhammad Abdullahi Wase Teaching Hospital, Kano, Nigeria
5Medicine, Aminu Kano Teaching Hospital, Kano, Nigeria
6Surgery, Aminu Kano Teaching Hospital/Bayero University Kano, Kano, Nigeria
7Department of Hematology, Aminu Kano Teaching Hospital/Bayero University Kano, Kano, Nigeria
8Department of Pharmacy, Aminu Kano Teaching Hospital, Kano, Nigeria
9Department of Computer Science, Bayero University Kano, Kano, Nigeria
10Department of Mathematical Science, Kano University of Science and Technology,, Kano, Nigeria
11Mathematical Science, Bayero University Kano, Kano, Nigeria
12Statistical Consultant, Rodeghier Consultants, Chicago, IL
13School of Medicine, Johns Hopkins University, Baltimore, MD
14Department of Pediatrics, Division of Hematology & Oncology, Vanderbilt University School of Medicine, Nashville, TN

Raffaella Colombatti, MD, PhD1*, Carolyn Hoppe, MD2*, Elliott P. Vichinsky, MD3, Mona Hamdy, MD, MCRA4*, Adeseye Michael Akinsete, MBBS5*, Mark Davis2*, Halima Bello-Manga, MBBS, MPH, FMCPath6, Iheanyi Okpala, FWACP, FRCPath7, Ana Cristina Silva Pinto, MD, PhD8* and Adlette Inati, MD, FAAP9,10

1Department of Woman's and Child's Health, Pediatric Hematology Oncology, University of Padova, Padova, Italy
2Global Blood Therapeutics, South San Francisco, CA
3UCSF Benioff Children's Hospital Oakland, Oakland, CA
4Clinical Research center, Faculty of Medicine, Cairo University, Cairo, Egypt
5College of Medicine, Division of Pediatric Hematology & Oncology, Lagos University Teaching Hospital, Lagos, Nigeria
6Barau Dikko Teaching Hospital, Kaduna State University, Kaduna, Nigeria
7Department of Hematology, University of Nigeria, Enugu, Nigeria
8Center for Cell-Based Therapy, Hemotherapy Center of Ribeirão Preto, Ribeirão Preto Medical School, University of São Paulo, Ribeirão Preto, Brazil
9Lebanese American University, Beirut and Nini Hospital, Tripoli, Lebanon
10Division of Pediatric Hematology and Oncology, Nini Hospital, Tripoli, Lebanon

Anthea Louise Greenway, MBBS, FRACP, FRCPA, QIA1,2,3, Zane Kaplan, MBBS FRACP FRCPA PhD4,5,6, Pasquale Barbaro, MBBS FRACP FRCPA PhD7*, Tina Carter, PhD, FRACP, FRCPA8, Juliana Teo, MBBS, FRACP, FRCPA9 and Manika Pal, MBBS, FRACP FRCPA10*

1Congenital Blood Disorders, Monash Medical Centre, Clayton, VIC, Australia
2Royal Children's Hospital, Parkville, VIC, Australia
3Dept of Paediatrics, University of Melbourne, Parkville, VIC, Australia
4Monash Medical Centre, Clayton, Australia
5Australian Centre for Blood Diseases, Melbourne, AUS
6Monash University, Melbourne, Australia
7Queensland Children's Hospital, Brisbane, QLD, Australia
8Perth Children's Hospital, Nedlands, WEA, AUS
9The Children's Hospital Westmead, Westmead, NSW, AUS
10Dept of Haematology and Oncology, Womens and Children's Hospital, North Adelaide, SA, Australia

Ashrei Bayewitz and Sai Shalini Pillarisetty, MD

Coney Island Hospital, Brooklyn, NY

Olufunke Y. Martin, MD1, Stefanie L. Margulies, MS1*, Deepika S. Darbari, MD1,2, Patrick C. Hines, MD/PhD3,4 and Andrew D. Campbell, MD2,5

1Center for Cancer and Blood Disorders, Children's National Hospital, Washington, DC
2The George Washington University School of Medicine and Health Sciences, Washington, DC
3Functional Fluidics, Detroit, MI
4Carman and Ann Adams Department of Pediatrics, Division of Pediatric Critical Care, Children’s Hospital of Michigan/Wayne State University, Detroit, MI
5Center for Cancer and Blood Disorders, Children's National Medical Center, Washington, DC

Alexandra Power-Hays, MD1, Min Dong2,3*, Kathryn McElhinney, BS4*, Andrea L. Conroy, PhD5,6*, Teresa Latham, MA7,8*, Adam Lane, PhD7,9*, Robert O. Opoka, MMED, PhD10,11*, Alexander A. Vinks, PharmD, PhD, FCP2,3* and Russell E. Ware3,4,12,13

1Cancer and Blood Disorders Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
2Division of Clinical Pharmacology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
3Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH
4Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
5Indiana University, Indianapolis, IN
6Mulago Hospital, Global Health Uganda, Kampala, Uganda
7Division of Hematology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH
8Cancer and Blood Diseases Institute, Cincinnati Children's Hospital, Cincinnati
9University of Cincinnati - College of Medicine, Cincinnati, OH
10Global Health Uganda, Kampala, Uganda
11Paediatrics and Child Health, Makerere University, Kampala, Uganda
12Division of Hematology, Children's Hospital Medical Center, Cincinnati, OH
13Global Health Center, Cincinnati Children's Hospital Medical Center, Cincinnati, OH

*signifies non-member of ASH