-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

508.P1.37 508. Bone Marrow Failure: Acquired: Poster I

Symposia: Bone Marrow Failure: Acquired Program: Oral and Poster Abstracts
Type: Poster
Saturday, December 10, 2022: 5:30 PM-7:30 PM
Hall D (Ernest N. Morial Convention Center)

Jason C Collins, PhD1*, Nicholas Balanda1*, Samuel J Magaziner2*, Maya English1*, Daniela Ospina Cardona2*, Mrinal M. M. Patnaik, MD3, Benjamin Terrier, MD, PhD4*, Olivier Kosmider, MD, PhD5*, Achim Werner, PhD6* and David B. Beck7*

1National Institutes of Health, Bethesda, MD
2New York University School of Medicine, New York, NY
3Division of Hematology, Mayo Clinic, Rochester, MN
4Service de Médecine interne, Assistance Publique des Hopitaux de Paris / Hôpital Cochin, Paris, FRA
5Assistance Publique Hôpitaux de Paris, Laboratoire d'hématologie, Hôpital Cochin, Institut Cochin, INSERM U1016, University Paris Descartes, Paris, France
6National Institutes of Heath, Bethesda, MD
7Center for Human Genetics and Genomics, New York University School of Medicine, New York, NY

Olisaemeka Ogbue1, Tariq Kewan, MD2*, Waled Bahaj2*, Carmelo Gurnari, MD2,3, Valeria Visconte, PhD4, Suresh Kumar Balasubramanian, MD5, Bhumika J. Patel, MD6*, Alan Lichtin, MD6, Hetty E. Carraway, MD, MBA6 and Jaroslaw P. Maciejewski, MD, PhD, FACP2

1Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic Foundation, Rocky River, OH
2Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic Foundation, Cleveland, OH
3Department of Biomedicine and Prevention, University of Rome "Tor Vergata", Rome, Italy
4Taussig Cancer Institute, Cleveland, OH
5Wayne State University, Detroit, MI
6Department of Hematology and Medical Oncology, Taussig Cancer Institute, Cleveland Clinic Foundation, Cleveland, OH

Simon Buatois1*, Khaled Benkali2*, Andrea Henrich3*, Félix Jaminion1*, Yuchen Zhang4* and Alexandre Sostelly, PhD, MSc1*

1F. Hoffmann-La Roche Ltd, Basel, Switzerland
2Certara, Inc., Paris, France
3Pharmetheus, Uppsala, Sweden
4China Innovation Center of Roche, Shanghai, China

Christopher J. Patriquin, MD, MSc, FRCPC1, Andrija Bogdanovic, MD, PhD, MSc2*, Morag Griffin, FRCPath, MRCP3*, Richard Kelly, BSc, MD3*, Jaroslaw P. Maciejewski, MD, PhD, FACP4, Brian Mulherin, MD5,6*, Regis Peffault De Latour7,8*, Alexander Roeth, MD9, Veena Selvaratnam10*, Jeffrey Szer, MBBS, FRACP11, Jessica Savage, MD, MHS12*, Regina Horneff, PhD13*, Lisa Tan13*, Michael Yeh, MD, MBA, MPH14* and Jens Panse, MD15,16

1Hematology & Apheresis Medicine, University Health Network, Toronto General Hospital, Toronto, ON, Canada
2Clinic of Hematology, Clinical Center of Serbia, Faculty of Medicine, University of Belgrade, Belgrade, Serbia
3Department of Haematology, St James University Hospital, Leeds, United Kingdom
4Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic Foundation, Cleveland, OH
5Hematology Oncology Of Indiana, Indianapolis, IN
6Ascension St. Vincent Carmel, Carmel, IN
7French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France
8Assistance Publique–Hôpitaux de Paris, Saint-Louis Hospital, Université Paris Cité, Paris, France
9Department of Hematology and Stem Cell Transplantation, West German Cancer Center, University Hospital Essen, Essen, Germany
10Department of Hematology, Ampang Hospital, Ampang, Malaysia
11Department of Clinical Haematology, The Royal Melbourne Hospital and Peter MacCallum Cancer Centre, Melbourne, VIC, Australia
12Apellis Pharmaceuticals, Waltham, MA
13Swedish Orphan Biovitrum AB, Stockholm, Sweden
14Apellis Pharmaceuticals, Inc., Waltham, MA
15Center for Integrated Oncology Aachen Bonn Cologne Düsseldorf (CIO ABCD), Aachen, Germany
16Department of Hematology, Oncology, Hemostaseology and Stem Cell Transplantation, University Hospital RWTH Aachen, Aachen, Germany

Audrey Le Floch-Ramondou, PhD1*, Kirsten Nagashima2*, Kaitlyn Gayvert2*, Hao Pan2*, Chandrashekhar Korgaonkar2*, Hassan Shakil2*, Erica Ullman2*, Thomas Norton2*, Lorah Perlee, PhD3*, Andrew J. Murphy, PhD1*, Matthew Sleeman2* and Jamie Orengo2*

1Regeneron, Tarrytown, NY
2Regeneron, Tarrytown
3Regeneron Pharmaceuticals, Inc., Tarrytown, NY

Xiaoqing Liu1*, Qiqiang Long2*, Xi Chen2*, Chun Qiao3*, Guangsheng He4*, Shengyun Lin5* and Jianyong Li, MD4,6

1Hematology, the Second People's Hospital of Nanjing, Nanjing, China
2the Second People’s Hospital of Nanjing, Nanjing, China
3Department of Hematology, The First Affiliated Hospital of Nanjing Medical University, Jiangsu Province Hospital, Nanjing, China
4Department of Hematology, The First Affiliated Hospital of Nanjing Medical University, Nanjing, China
5The First Affiliated Hospital of Zhejiang Chinese Medical University, Hangzhou, China, Hangzhou, China
6Department of Hematology, The First Affiliated Hospital of Nanjing Medical University, Jiangsu Province Hospital, Collaborative Innovation Center for Cancer Personalized Medicine, Nanjing, China

Morag Griffin, FRCPath, MRCP1*, Shreyans Gandhi2*, Eden Hicks3*, Deepak Jain, MD3*, Richard Kelly, BSc, MD4*, Talha Munir, MBBS, MRCP, FRCPath, PhD5*, Petra Muus6*, Masayo Ogawa, MD3*, Roochi Trikha2*, Ji Yu3* and Austin Kulasekararaj, MD, MBBS, FRCPath, MRCP7

1St James's University Hospital, Sheffield, United Kingdom
2King’s College Hospital, National Institute for Health and Care Research/Wellcome King’s Clinical Research Facility, London, United Kingdom
3Alexion, AstraZeneca Rare Disease, Boston, MA
4Department of Haematology, St James University Hospital, Leeds, United Kingdom
5Consultant Haematologist, St James's Hospital, Leeds, United Kingdom
6St James’s University Hospital, Leeds, United Kingdom
7King’s College Hospital, National Institute for Health and Care Research/Wellcome King’s Clinical Research Facility, London, ENG, United Kingdom

Zoe McQuilten, MBBS, PhD1,2*, Lucy C. Fox, MBBS3,4, Vanessa Fox, BSc5*, Stephane Heritier, PhD4*, Tracey J Batt, FRACP, FRCPA, MBBS6*, Piers Blombery, MBBS7, Jennifer Curnow, MBBS FRACP FRCPA PhD8*, Alisa Higgins, PhD4*, Devendra Hiwase, MD, MBBS, PhD, FRACP, FRCPA9, Robin J Filshie, MBChB, PhD, FRACP, FRCPA10, Frank Firkin, MBBS11*, Paul Lacaze, PhD12*, Kylie D Mason, MBBS, MD, FRACP, FRCPA, PhD13, Tony Mills, MBBS14*, Sushrut S. Patil15*, Dominic Pepperell, MBBS16*, William S Stevenson, MBBS, PhD, FRACP, FRCPA17, Jeffrey Szer, MBBS, FRACP18, Neil Waters, BSc4*, Kate Wilson19*, Stephen B Ting, MBBS, FRACP, FRCPA, PhD20* and Erica M. Wood, MBBS, FRACP, FRCPA21,22

1Monash Haematology, Monash Health, Clayton, VIC, Australia
2Transfusion Research Unit, School of Public Health and Preventive Medicine, Monash University, Melbourne, VIC, Australia
3Peter MacCallum Cancer Centre, Melbourne, Australia
4Monash University, Melbourne, Australia
5Public Health and Preventative Medicine, Monash University, Melbourne, Australia
6Royal Hobart Hospital, Hobart, Australia
7Peter MacCallum Cancer Centre, Peter Maccallum Cancer Centre, East Melbourne, VIC, Australia
8Department of Haematology, Westmead Hospital, Western Sydney Local Health District, Sydney, Australia
9Adelaide Medical School, Faculty of Health and Medical Sciences, University of Adelaide, Adelaide, SA, Australia
10Department of Hematology, St. Vincent's Hospital Melbourne, Melbourne, VIC, Australia
11St Vincent's Hospital, Melbourne, Australia
12Department of Epidemiology and Preventive Medicine, Monash University, Melbourne, Australia
13Department of Medicine, University of Melbourne, Melbourne, Australia
14University of Queensland, Brisbane, Australia
15Alfred Hospital, Melbourne, AUS
16Department of Haematology, Fiona Stanley Hospital, Murdoch, Australia
17Department of Haematology, Royal North Shore Hospital, Sydney, NSW, Australia
18Department of Clinical Haematology, The Royal Melbourne Hospital and Peter MacCallum Cancer Centre, Melbourne, VIC, Australia
19University of Sydney, Sydney, Australia
20Department of Haematology, Eastern Health and Monash University, Melbourne, VIC, Australia
21Department of Clinical Haematology, Monash Health, Melbourne, VIC, Australia
22Transfusion Research Unit, School of Public Health and Preventive Medicine, Monash University, Melbourne, Australia

Congwei Zhong1*, Tong Chen2*, Chunyan Liu3*, Zonghong Shao4 and Rong Fu5*

1Tianjin Medical University General Hospital, Tianjin, China, AL, China
2Tianjin Medical University General Hospital, Tianjin, China
3Department of Hematology, Tianjin Medical University General Hospital, Tianjin, China
4Department of Hematology, General Hospital of Tianjin Medical University, Tianjin, China
5Department of hematology, Tianjin Medical University General Hospital, Tianjin, China

Hui Liu1*, Wei Wang2*, Lijie Zeng1*, Zhaoyun Liu1*, Liyan Li1*, Zonghong Shao3 and Rong Fu1*

1Department of hematology, Tianjin Medical University General Hospital, Tianjin, China
2Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and Technology, ShanghaiTech University, Shanghai, China
3Department of Hematology, Tianjin Medical University General Hospital, Tianjin, China

Morag Griffin, FRCPath, MRCP1*, Richard Kelly, BSc, MD1*, Dries Deeren, MD, PhD2, Yeow Tee Goh, MBBS3, Eric Tse, MBBS, PhD, FRCP, FRCPath4, Kensuke Usuki, MD, PhD5, Raymond Wong, MBChB, MD6, Regina Horneff, PhD7*, Lisa Tan7*, Michael Yeh, MD, MBA, MPH8*, Jessica Savage, MD, MHS9* and Jeff Szer, MBBS, FRACP10

1Department of Haematology, St James University Hospital, Leeds, United Kingdom
2Algemeen Ziekenhuis (AZ) Delta, Roeselare, Belgium
3Department of Hematology, Singapore General Hospital, Singapore, Singapore
4Queen Mary Hospital, University of Hong Kong, Pokfulam, Hong Kong
5Department of Hematology, NTT Medical Center Tokyo, Tokyo, Japan
6Sir YK Pao Centre for Cancer & Department of Medicine and Therapeutics, The Chinese University of Hong Kong, Prince of Wales Hospital, Hong Kong, Hong Kong
7Swedish Orphan Biovitrum AB, Stockholm, Sweden
8Apellis Pharmaceuticals Inc., Waltham, MA
9Apellis Pharmaceuticals, Waltham, MA
10Department of Clinical Haematology, Peter MacCallum Cancer Centre and the Royal Melbourne Hospital, Melbourne, Australia

Xin Zhao, MD*, Baohang Zhang*, Jianping Li*, Huihui Fan*, Yuan Li*, Wenrui Yang*, Liping Jing, MD*, Li Zhang*, Kang Zhou*, Youzhen Xiong*, Lei Ye*, Yingchang Mi, MD and Fengkui Zhang*

Institute of Hematology and Blood Diseases Hospital, CAMS & PUMC, Tianjin, China

Alice Garnier, MD1*, Amandine Le Bourgeois, MD1*, Thierry Guillaume, MD, PhD2*, Pierre Peterlin, MD3*, Maxime Jullien, MD4*, Marianne Coste-Burel, MD, PhD5*, Marie C Bene, PharmD, DPhil6,7* and Patrice Chevallier, MD8,9

1Hematology Department, Nantes University Hospital, Nantes, France
2Clinical Hematology Department, Nantes University Hospital, Nantes, France
3Clinical Hematology, Nantes University Hospital, Nantes, France
4Clinical Hematology, Nantes University Hospital, NANTES, France
5Virology, Nantes University Hospital, Nantes, France
6Hematology Biology, Nantes University Hospital, Nantes, France
7CHU Nantes, Centre de Recherche en Cancérologie et Immunologie Nantes-Angers (CRCINA), Nantes, France
8CRCI2NA, Integrated Research Center in Immunology and Oncology, Nantes University, Nantes, France
9Department of Clinical Hematology, Nantes University Hospital, Nantes, France

*signifies non-member of ASH