-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

322.P1.70 322. Disorders of Coagulation or Fibrinolysis: Clinical and Epidemiological: Poster I

Symposia: Disorders of Coagulation or Fibrinolysis: Clinical and Epidemiological Program: Oral and Poster Abstracts
Type: Poster
Saturday, December 10, 2022: 5:30 PM-7:30 PM
Hall D (Ernest N. Morial Convention Center)

Robert F. Sidonio, Jr., MD, MSc1, Anan Lu2*, Sarah Hale, PhD, MS3*, Jorge Caicedo, MD4*, Michael Bullano, PharmD, MS3* and Shan Xing, PharmD, PhD4*

1Department of Pediatrics, Emory University School of Medicine, Atlanta, GA
2Charles River Associates, Boston, MA
3Takeda Development Center Americas, Inc., Lexington, MA
4Takeda Pharmaceuticals U.S.A., Inc., Lexington, MA

Huacong Cai, MD1*, Xinxin Cao, MD2*, Shujie Wang, MD3*, Yongqiang Zhao, MD3*, Jian Li, MD3 and Tie-nan Zhu, MD3*

1Department of Hematology, Peking Union Medical College Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Beijing, AL, China
2Department of Hematology, Peking Union Medical College Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Beijing, CA, China
3Department of Hematology, Peking Union Medical College Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Beijing, China

Rezan Abdul-Kadir1*, Ahmad Tarawah2*, Naveen Shridhar3* and Roshni Kulkarni, MD4

1Department of Obstetrics and Gynaecology, University College London, London, United Kingdom
2King Salman Medical City Al Madinah, Madinah, Saudi Arabia
3Rare Disease Global Medical Affairs, Novo Nordisk Service Centre India Private Ltd, Bangalore, India
4Michigan State University, Okemos, MI

Eliska Ceznerova, MSc1*, Jirina Kaufmanova, MSc2*, Marek Havlicek, MSc1*, Ondrej Pastva, PhD1*, Alzbeta Hlavackova, PhD1*, Roman Kotlin, PhD1 and Jiri Suttnar, PhD1*

1Department of Biochemistry, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
2Department of Biochemistry and Microbiology, University of Chemistry and Technology, Prague, Czech Republic

Ahmad Al-Huniti, MD1, Alexis Katherine Kuhn, PharmD, RPh2*, Linda Marshall, Pharm.D., R.Ph.3*, Dawn Rusk, R.N.4*, Rajiv K. Pruthi, M.B.B.S5,6,7 and Asmaa Ferdjallah, MD8*

1Division of Pediatric Hematology and Oncology, Mayo Clinic, Rochester, MN
2Department of Pharmacy. Mayo Clinic Hospital- Rochester, Rochester, MN
3Department of Pharmacy, Mayo Clinic, Rochester, Rochester, MN
4Department of Nursing, Mayo Clinic, Rochester, MN
5Division of Hematopathology, Special Coagulation Laboratory, Mayo Clinic, Rochester, MN
6Mayo Comprehensive Hemophilia Center, Mayo Clinic, Rochester, MN
7Division of Hematology, Mayo Clinic, Rochester, MN
8Division of Pediatric Hematology and Oncology, Mayo Clinic, Rochester, MN, USA, Rochester, MN

Brian Hu, MS, PhD1*, Martin Chandler, BS1*, Matthew Manuel, MS, PhD1*, Jorge Caicedo, MD2*, Michael Denne, PharmD2, Bruce Ewenstein, MD, PhD2, Ali Mokdad, MD, PhD, MBA2*, Shan Xing, PharmD, PhD2* and Michael Recht, MD, PhD, MBA1,3

1American Thrombosis and Hemostasis Network, Rochester, NY
2Takeda Pharmaceuticals U.S.A., Inc., Lexington, MA
3Yale University School of Medicine, Rochester, CT

Hidekazu Nishikii, MD, PhD1, Nobuaki Suzuki, MD2*, Ryota Kobayashi3*, Narumi Mizuno3*, Ryoto Ozaki3* and Midori Shima, MD, PhD4

1Department of Hematology, Faculty of Medicine, University of Tsukuba, Tsukuba, Japan
2Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
3Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
4Thrombosis and Hemostasis Research Center, Nara Medical University, Kashihara, Japan

Gili Kenet, MD1,2, Ampaiwan Chuansumrit, MD3*, Tadashi Matsushita, MD, PhD4, Guy Young, MD5, Vandana Yadav6*, Marek Zak, MD, PhD7* and Christoph Male, MD8*

1The Amalia Biron Thrombosis Research Institute, Sheba Medical Center, Tel Aviv University, Tel Aviv, Israel
2Sackler School of Medicine, Tel Aviv University, Tel Aviv, Israel
3Mahidol University, Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Bangkok, Thailand
4Nagoya University Hospital, Nagoya, Japan
5Children's Hospital Los Angeles, University of Southern California Keck School of Medicine, Los Angeles, CA
6Novo Nordisk Service Centre India Private Ltd, Bangalore, India
7Novo Nordisk A/S, Søborg, Denmark
8Department of Paediatrics, Medical University of Vienna, Vienna, Austria

Jill M. Johnsen, MD1,2, Sarah Ruuska3*, Peter A. Kouides, MD4 and Barbara Konkle5,6

1Bloodworks NW, Seattle, WA
2Department of Medicine, University of Washington, Seattle, WA
3Washington Center for Bleeding Disorders, Seattle, WA
4Department of Medicine, Mary M. Gooley Hemophilia Center, Rochester, NY
5Division of Hematology, University of Washington School of Medicine, Seattle, WA
6Washington Institute for Coagulation, Washington Center for Bleeding Disorders, Seattle, WA

Ihosvany Fernandez-Bello, BSPharm, PhD1*, Jose Manuel Calvo-Villas2*, Ana Marco, MD, PhD3*, Sonia Herrero-Martín, MD, PhD4*, Laura Entrena Ureña, MD5*, Adrián Montaño, Biotechnologist, PhD1,6*, Francisco José López-Jaime, MD1*, Bolivar Luis Diaz Jordan, MD7*, Covadonga Garcia Diaz, MD8*, Sergio Jurado Herrera, MD9*, Noelia Pérez González, MD, PhD10*, Faustino García-Candel, MD, PhD11*, Miguel Blanquer Blanquer, MD, PhD12 and Pascual Marco-Vera, MD, PhD3,13*

1Hospital Universitario Regional de Málaga-IBIMA, Málaga, Spain
2Hospital Universitario Miguel Servet, Zaragoza, Spain
3Hospital General Universitario de Alicante-ISABIAL, Alicante, Spain
4Hospital Universitario de Guadalajara, Guadalajara, Spain
5Hospital Universitario Virgen de las Nieves, Granada, AL, Spain
6University of Salamanca, Salamanca, Spain
7Hospital General de Valdepeñas, Valdepeñas, Spain
8Hematology Department, Hospital Universitario de Burgos, Burgos, Spain
9Hospital Universitario Torrecárdenas, Almeria, Spain
10Hospital Universitario Torrecárdenas, Almería, Spain
11Hospital Clínico Universitario Virgen de la Arrixaca, Murcia, Spain
12Hospital Clínico Universitario Virgen De La Arrixaca, Murcia, Murcia, Spain
13Department of Clinical Medicine, Miguel Hernández University, Alicante, Spain

Amy D. Shapiro, MD1, Aby Abraham, MD, DM2*, Silvia Linari3*, Jesper Skov Neergaard4*, Jan Odgaard-Jensen4*, Jay Jay Thaung Zaw4* and Huyen Tran, MBBS5*

1Indiana Hemophilia & Thrombosis Center, Indianapolis, IN
2Department of Haematology, Christian Medical College, Vellore, Tamil Nadu, India
3Center for Bleeding Disorders and Coagulation, Department of Oncology, Careggi University Hospital, Florence, Italy
4Novo Nordisk A/S, Søborg, Denmark
5Haemophilia Treatment Centre, The Alfred Hospital, Melbourne, Australia

Steven R. Lentz, MD, PhD1, Pratima Chowdary, MBBS, MRCP, FRCPATH2*, Francisco Jose Lopez Jaime, MD3*, Johnny Mahlangu, MD4, Irina Matytsina5*, Anne Louise Nielsen5* and Jerzy Windyga, MD, PHD6*

1Department of Internal Medicine, University of Iowa, Iowa City, IA
2Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, United Kingdom
3Hospital Universitario Regional de Málaga, Málaga, Spain
4National Health Laboratory Service and Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand, Johannesburg, South Africa
5Novo Nordisk A/S, Søborg, Denmark
6Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland

Tomasz Urasinski, MD, PhD1*, Klaudia Paczoska, MD1*, Wanda Badowska, PhD2*, Halina Bobrowska, MD3*, Lucja Dakowicz, MD4*, Grzegorz Dobaczewski5*, Elzbieta Latos-Grazynska, MD, PhD6*, Grazyna Karolczyk7, Anna Klukowska, MD, PhD8*, Andrzej Koltan, MD9*, Magdalena Wojdalska, MD10*, Pawel Laguna, MD, PhD8*, Maciej Niedzwiecki, MD11*, Danuta Pietrys12*, Julia Radon-Proskura13*, Monika Radwanska, MD14*, Iwona Ruranska, MD15*, Tomasz Szczepanski, MD, PhD16,17, Dariusz Wasinski, MD18*, Irena Woznica-Karczmarz, MD19* and Tomasz Ociepa, MD, PhD1*

1Department of Pediatrics, Hemato-Oncology and Gastroenterology, Pomeranian Medical University, Szczecin, Poland
2Department of Pediatric Oncology and Hematology, School of Medicine, University of Warmia Mazury in Olsztyn, Olsztyn, POL
3Wielkopolska Child Health Center, Poznań, Poland
4Department of Pediatric Oncology and Hematology, Medical University of Bialystok, Białystok, Poland
5Department of Bone Marrow Transplantation, Pediatric Oncology and Hematology, Wroclaw Medical University, Wrocław, POL
6Department of Bone Marrow Transplantation, Pediatric Oncology and Hematology, Wroclaw Medical University, Wrocław, Poland
7II Department of Pediatrics, Collegium Medicum, Jan Kochanowski University, Kielce, Poland
8Department of Pediatric Oncology, Hematology and Transplantation, Medical University of Warsaw, Warszawa, Poland
9Department of Pediatrics, Hematology and Oncology, Collegium Medicum, Nicolaus Copernicus University, Bydgoszcz, POL
10Department of Pediatrics, Oncology and Hematology, Medical University of Lodz, Łódź, Poland
11Department of Pediatrics, Hematology and Oncology, Medical University of Gdansk, Gdansk, Poland
12Department of Pediatric Oncology and Hematology, Collegium Medicum, Jagiellonian University, Kraków, Poland
13Department of Pediatrics, Hematology and Oncology, Medical University of Gdansk, Gdańsk, Poland
14Department of Pediatric Oncology and Hematology, College of Medical Sciences, University of Rzeszow, Rzeszów, Poland
15Department of Pediatrics, Hematology and Oncology, Medical University of Silesia, Katowice, Poland
16Medical University of Silesia, Katowice, Poland
17Department of Pediatrics Hematology and Oncology in Zabrze, Medical University of Silesia, Zabrze, Poland
18Department of Pediatric Hematology and Oncology, Collegium Medicum, University of Zielona Gora, Zielona Góra, Poland
19Department of Transfusion Medicine, Medical University of Lublin, Lublin, Poland

Koichiro Yoneyama*, Mizuki Fukazawa-Shinotsuka* and Tomohisa Saito, PhD*

Chugai Pharmaceutical Co., Ltd., Tokyo, Japan

Midori Shima, MD, PhD1, Hideyuki Takedani, MD, PhD2*, Kaoru Kitsukawa, MD, PhD3*, Masashi Taki, MD, PhD4*, Akira Ishiguro, MD, PhD5*, Azusa Nagao, MD, MSc6*, Daisuke Nosaka, BS7*, Yui Kyogoku, BA7*, Keisuke Iwasaki, MPH7* and Keiji Nogami, MD1*

1Nara Medical University, Nara, Japan
2IMSUT Hospital, The University of Tokyo, Tokyo, Japan
3Chiba University Hospital, Chiba, Japan
4Department of Pediatrics, St. Marianna University School of Medicine, Yokohama, Japan
5National Center for Child Health and Development, Tokyo, Japan
6Department of Blood Coagulation, Ogikubo Hospital, Tokyo, Japan
7Chugai Pharmaceutical Co., Ltd., Tokyo, Japan

Michael Recht, MD, PhD, MBA1,2, Nabil Daoud, MA1*, Lucy Lee, PharmD, MPH3*, Paul Morton, BSc3* and Leslie J. Raffini, MD, MSCE4

1American Thrombosis and Hemostasis Network, Rochester, NY
2Yale University School of Medicine, New Haven, CT
3Genentech, Inc., South San Francisco, CA
4Children's Hospital of Philadelphia, Philadelphia, PA

Ho Jun Lee, MD1*, Aditi Parikh, MD2*, Sanjay Ahuja, MD3 and Lalitha V Nayak, MD1

1University Hospitals Cleveland Medical Center, Case Western Reserve University, Cleveland, OH
2Pediatric Genetics, Case Western Reserve University / UH Rainbow Babies and Children's Hospital, Cleveland, OH
3Division of Pediatric Hematology & Oncology, Rainbow Babies and Children's Hospital, Cleveland, OH

Lucy Z Kornblith1*, Bindhya Sadhanandhan2*, Sreepriya Arun2*, Rebecca Long3*, Alicia J Johnson4*, Jamie Noll5*, CN Ramchand6*, John K Olynyk3* and David H Farrell, PhD7*

1University of California, San Francisco, San Francisco, CA
2Theragen Biologics Pvt Ltd, Chennai, India
3Edith Cowan University, Joondalup, Western Australia, Australia
4Oregon Health & Science University, Portland, OR
5Jamie Noll, Pharm.D. LLC, The Villages, FL
6MagGenome Pvt Ltd, Chennai, India
7Department of Surgery, Oregon Health & Science University, Portland, OR

Martin Chandler, BS1*, Jessica Charlet, PhD, MSc, BSc2*, Thomas Moulton, MD2 and Michael Recht, MD, PhD, MBA1,3

1American Thrombosis and Hemostasis Network, Rochester, NY
2Bayer, Whippany, NJ
3Yale University School of Medicine, New Haven, CT

Brooke Sadler, PhD1, Pamela A Christopherson2*, Crystal L Perry3*, Daniel B. Bellissimo, PhD4*, Sandra L Haberichter, PhD5, Gabe Haller, PhD6*, Lilian Antunes, PhD1*, Veronica H Flood, MD7, Jorge Di Paola, MD8, Robert R Montgomery, MD9 and The Zimmerman Program Investigators10*

1Pediatrics, Washington University School of Medicine, Saint Louis, MO
2Blood Center of WI Blood Research Institute, Milwaukee, WI
3Blood Research Institute, Blood Center of Wisconsin, Milwaukee, WI
4OB/GYN and Reproductive Sciences, University of Pittsburgh School of Medicine, Pittsburgh, PA, Magee Women's Hospital, Pittsburgh, PA
5Blood Research Institute and Diagnostic Laboratories, Versiti, Milwaukee, WI
6Departments of Neurosurgery, Neurology and Genetics, Washington University, St Louis, MO
7Pediatric Hematology, Medical College of Wisconsin, Milwaukee, WI
8Department of Pediatrics, Washington University School of Medicine in St. Louis, Saint Louis, MO
9Blood Research Institute, Milwaukee, WI
10Medical College of Wisconsin, Milwaukee, WI

Craig M. Kessler, MD1 and Andreas Tiede, MD2

1Georgetown University School of Medicine, Washington
2Clinic for Haematology, Haemostaseology, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany

Zhengping Li, MBBS1*, Man-Chiu Poon, MD2, Guoqing Liu3*, Zekun Li, MD4*, Jie Sun4* and Runhui Wu, MD, PhD5*

1Hematology Department, Beijing Children's Hospital, Capital Medical University, Beijing, AL, China
2Foothills Hospital, Calgary, AB, Canada
3Hemophilia Comprehensive Care Center, Beijing Children's Hospital, Capital Medical University, Beijing, China
4Beijing Children's Hospital, Capital Medical University, Beijing, China
5Department of Hematology, National Center for Children's Health, Beijing Children's Hospital, Beijing, China

Ellen Cusano, MD1, Haowei Linda Sun, MD, MHSc, FRCPC2, M Dawn Goodyear, MD1, Man-Chiu Poon, MD1, Douglas Seal, MD, FRCPC3*, R Scott McClure, MD4* and Natalia Rydz, MD1

1Department of Medicine, Division of Hematology and Hematological Malignancies, University of Calgary, Calgary, AB, Canada
2Department of Medicine, University of Alberta, Division of Hematology, Edmonton, AB, Canada
3Department of Anesthesia and Pain Medicine, University of Calgary, Calgary, AB, Canada
4Libin Cardiovascular Institute, Department of Cardiac Sciences, University of Calgary, Calgary, AB, Canada

Anjali Sharathkumar, MD, MS1, Yanrong Jiang, MBBS, MRCP2,3*, Hwai Jing Hiew, MD, FRCPath3,4*, Athanasios Siadimas, MSc5*, Francis Nissen, MD, PhD5*, Gillian Hanson, ND6*, Emily Cibelli, PhD6*, Katya Moreno, MD5*, Johnny Wharton, PhD3* and Angela C. Weyand, MD7

1Carver College of Medicine, University of Iowa, Iowa City, IA
2University College London Hospitals NHS Foundation Trust, London, United Kingdom
3Roche Products Ltd., Welwyn Garden City, United Kingdom
4University Hospital Southampton NHS Trust, Southampton, United Kingdom
5F. Hoffmann-La Roche Ltd., Basel, Switzerland
6PicnicHealth, San Francisco, CA
7University of Michigan, Ann Arbor, MI

Hitan Patel, MB. ChB1*, Miranda Norton, PhD2* and Magdalena D. Lewandowska, MD3

1Bio Products Laboratory, Ltd., Elstree, United Kingdom
2Bio Products Laboratory. Ltd., Elstree, United Kingdom
3Indiana Hemophilia & Thrombosis Center, Indianapolis, IN

*signifies non-member of ASH