-Author name in bold denotes the presenting author
-Asterisk * with author name denotes a Non-ASH member
Clinically Relevant Abstract denotes an abstract that is clinically relevant.

PhD Trainee denotes that this is a recommended PHD Trainee Session.

Ticketed Session denotes that this is a ticketed session.

634.O4.6 634. Myeloproliferative Syndromes: Clinical and Epidemiological: Avant-garde and Traditional Prognostic and Response Assessment in MPNs

Symposia: Myeloproliferative Syndromes: Clinical and Epidemiological Program: Oral and Poster Abstracts
Type: Oral
Hematology Disease Topics & Pathways:
Research, clinical trials, Fundamental Science, Biological therapies, Bleeding and Clotting, Translational Research, Non-Biological therapies, MPN, Clinical Research, thromboembolism, Chronic Myeloid Malignancies, Diseases, Therapies, real-world evidence, registries, Myeloid Malignancies, survivorship, Technology and Procedures, Transplantation, Pathology
Saturday, December 10, 2022: 4:00 PM-5:30 PM
217-219 (Ernest N. Morial Convention Center)
Moderators:
Nicola Polverelli, MD, PhD, and Ghaith Abu-Zeinah, MD,
Disclosures:
No relevant conflicts of interest to declare.
In this session are a selection of abstracts including new proposed prognostic scores in PV as well as arterial and venous thrombosis across MPN. Some abstracts also as the question about utility of bone marrow fibrosis grade assessment and finally data regarding molecular characterisation of response and loss of response to ruxolitinib in myelofibrosis
4:00 PM

Stephen T Oh, MD, PhD1, Srdan Verstovsek, MD, PhD2, Jason Gotlib, MD, MS3, Vikas Gupta, MD, FRCP, FRCPath4, Uwe Platzbecker, MD5, Heinz Gisslinger, MD6*, Timothy Devos, MD, PhD7, Jean-Jacques Kiladjian, MD8, Donal P. McLornan, MD, PhD9*, Andrew Charles Perkins, MBBS, PhD10, Maria Laura Fox, MD11*, Mary Frances McMullin, MD, FRCPath, FRCP12, Adam J Mead, MD PhD13,14, Miklos Egyed, MD, PhD15*, Jiri Mayer, Prof, MD16,17*, Tomasz Sacha, MD, PhD18*, Jun Kawashima, MD19*, Mei Huang, MS19*, Bryan Strouse, MSc19* and Ruben Mesa, MD, FACP20

1Siteman Cancer Center, Washington University School of Medicine, Saint Louis, MO
2MD Anderson Cancer Center, University of Texas, Houston, TX
3Stanford Cancer Institute, Stanford, CA
4Division of Medical Oncology and Hematology, University Health Network, Toronto, ON, Canada
5Department for Hematology, Cell Therapy and Hemostaseology, University of Leipzig Medical Center, Leipzig, Germany
6Medical University Vienna, Vienna, Austria
7University Hospitals Leuven and Laboratory of Molecular Immunology (Rega Institute), KU Leuven, Leuven, Belgium
8Université de Paris, AP-HP, Hôpital Saint-Louis, Centre d’Investigations Cliniques, Paris, France
9Haematology Department, Guy's and St Thomas' NHS Trust, London, United Kingdom
10Australian Centre for Blood Diseases, Monash University, Melbourne, VIC, Australia
11University Hospital Vall d’Hebron, Barcelona, Spain
12Centre for Medical Education, Queen's University, Belfast, United Kingdom
13University of Oxford, Oxford, United Kingdom
14Oxford University Hospitals NHS Foundation Trust, Oxford, United Kingdom
15Somogy County Mór Kaposi General Hospital, Kaposvár, Hungary
16Hematology and Oncology, University Hospital Brno, Czech Republic, Brno, Czech Republic
17Masaryk University, Brno, Czech Republic
18Jagiellonian University Hospital, Kraków, Poland
19Sierra Oncology Inc., San Mateo, CA
20UT Health San Antonio Cancer Center, San Antonio, TX

4:15 PM

Gu Wenjing, MD1*, Yuhui Zhang2*, Renchi Yang, MD3*, Jie Bai, MD2, Rongfeng Fu, MD4* and Lei Zhang, MD4*

1State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin, China
2Department of Hematology, The Second Hospital of Tianjin Medical University, Tianjin, China
3State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences, Tianjin, China
4CAMS Key Laboratory of Gene Therapy for Blood Diseases, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, Tianjin, China

4:30 PM

Adrian Mosquera Orgueira1*, Manuel Perez Encinas, MD2*, Alberto Hernández Sánchez, MD3*, Teresa González, PhD4*, Eduardo Arellano-Rodrigo, MD5*, Javier Martinez Martínez Elicegui6*, Angela Villaverde Ramiro7*, Jose Maria Raya Sanchez, MD, PhD8*, Rosa Ayala, MD, PhD9*, Francisca Ferrer Marin, MD, PhD10, Maria Laura Fox, MD11*, Patricia Velez Tenza12*, Elvira Mora Casterá, MD13*, Blanca Xicoy, MD14*, Maria Isabel Mata Vazquez, MD15*, María García Fortes16*, Anna Angona, MD17*, Beatriz Cuevas, MD18*, María Alicia Senin, MD19*, Angel Ramírez Payer, MD20*, María José Ramírez21*, Raul Perez Lopez, MD, PhD22*, Sonia González de Villambrosia, MD23*, Clara Martínez24*, María Teresa Gómez-Casares, MD, PhD25*, Carmen Garcia-Hernandez, MD26*, Mercedes Gasior Kabat, MD27*, Beatriz Bellosillo28*, Juan Luis Steegmann29, Alberto Alvarez-Larran, MD, PhD30*, Jesús María Hernández-Rivas, MD, PhD31 and Juan Carlos Hernandez Boluda, MD, PhD32*

1Complexo Hospitalario Universitario de Santiago de Compostela (CHUS), SERGAS, SANTIAGO DE COMPOSTELA, Spain
2Hospital Clínico Universitario de Santiago de Compostela, Santiago de Compostela, Spain
3Hematology Department, University Hospital of Salamanca, Salamanca, Spain
4University Hospital of Salamanca, Salamanca, Spain
5Hospital Clinic de Barcelona- GEMFIN, Barcelona, Spain
6Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain
7Molecular Genetics in Oncohematology, Institute for Biomedical Research of Salamanca (IBSAL), Salamanca, Spain
8Department of Hematology, Hospital Universitario de Canarias, Tenerife, Spain, La Laguna, Spain
9Hematology Department, Hospital Universitario 12 de Octubre, MADRID, Spain
10Servicio de Hematología y Oncología Médica. H.U. Morales Meseguer. Centro Regional de Hemodonación. Universidad de Murcia. IMIB-Arrixaca, Murcia, Spain
11Hematology Department, Hospital Universitario Vall d'Hebron, Barcelona, Spain
12Hospital Del Mar, Barcelona, Spain
13Dept. of Hematology, Hospital Universitario y Politécnico La Fe, Valencia, Spain
14HU German Trias i Pujol - Institut Català d' Oncologia, Barcelona, Spain
15Hospital Costa del Sol, Malaga, ESP
16Hospital Virgen de la Victoira, Malaga, Spain
17HU Dr. J Trueta - Institut Català d'Oncologia, Girona, Spain
18Hematology, Hospital Universitario de Burgos, BURGOS, ESP
19Hospital Duran i Reynals, Institut Catalá dÓncologia, L´Hospitalet de LLobregat., ESP
20Hospital Universitario Central de Asturias, Oviedo, Spain
21Hematology Department, Hospital de Jerez de la Frontera, Jerez, Spain
22HU Virgen de la Arrixaca, Murcia, Spain
23Hematology Department, Hospital Universitario Marqués de Valdecilla, Santander, Spain
24Hospital de la Santa Creu i Sant Pau, Barcelona, Spain
25Servicio de Hematología, Hospital Universitario de Gran Canaria Dr. Negrín, Las Palmas de Gran Canaria, Las Palmas de Gran Canaria, Spain
26Hospital General de Alicante, Alicante, Spain
27Hospital Universitario La Paz, Madrid, ESP
28Hospital del Mar, Barcelona, Spain
29University Hospital of La Princesa, Madrid, Spain
30Hematology Department, Hospital Clínic, Barcelona, Spain
31HARMONY, Salamanca, Salamanca, Spain
32Department of Hematology, Hospital Clínico Universitario de Valencia, Instituto de Investigación Sanitaria INCLIVA, Valencia, Spain

4:45 PM

Nico Gagelmann1*, Anita Badbaran1*, Rachel Beth Salit, MD2*, Thomas Schroeder3, Carmelo Gurnari, MD4, Simona Pagliuca, MD, PhD5, Arnold Ganser, MD6, Christina Rautenberg, MD7*, Bruno Cassinat, PharmD, PhD8, Felicitas R Thol, MD9, Christine Wolschke, MD10*, Marie Robin, MD, PhD11, Michael Heuser, MD6, Marie Thérèse Rubio, MD, PhD12*, Jaroslaw P. Maciejewski, MD, PhD, FACP13, Hans Christian Reinhardt, MD14, Bart L. Scott, MD2 and Nicolaus Kroeger, MD15

1University Medical Center Hamburg-Eppendorf, Department of Stem Cell Transplantation, Hamburg, Germany
2Fred Hutchinson Cancer Research Center, Seattle, WA
3Dept. of Bone Marrow Transplantation, University Hospital Essen, Essen, Germany
4Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic Foundation, Cleveland, OH
5Hematology Department, University Hospital of Nancy, Vandoeuvre, France
6Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
7Hematology and Stem Cell Transplantation, University Hospital Essen, Essen, Germany
8INSERM UMR 1131, Institut de Recherche Saint-Louis, Paris, France
9Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hanover, Germany
10Department of Stem Cell Transplantation, University Medical Center Hamburg-Eppendorf, Hamburg, Germany
11Hopital Saint-Louis, Paris Cedex 10, France
12Service Hématologie, CHRU Brabois, Nancy, France
13Translational Hematology and Oncology Research, Cleveland Clinic Foundation/ Taussig Cancer Institute, Cleveland, OH
14Department of Hematology and Stem Cell Transplantation, University Hospital Essen, Essen, Germany
15University Medical Center Hamburg-Eppendorf, Hamburg, Germany

5:00 PM

Hélène Pasquer, MSc1,2*, Rafael Daltro De Oliveira, MD2*, Juliette Soret, MD2*, Nabih Maslah, PharmD, PhD3,4*, Lin-Pierre Zhao, MD2*, Clemence Marcault, MD2*, Marine Cazaux, PhD2*, Nicolas Gauthier, MD2*, Emmanuelle Verger, PhD3,4*, Nathalie Parquet, MD5*, William Vainchenker, MD, PhD5*, Emmanuel Raffoux5*, Stephane Giraudier, MD PhD3,4*, Bruno Cassinat, PharmD, PhD3,4, Jean-Jacques Kiladjian, MD2,4 and Lina Benajiba, MD, PhD1,2

1INSERM UMR 944, Institut de Recherche Saint-Louis, Paris, France
2Centre d’Investigations Cliniques, INSERM CIC 1427, Université Paris Cité, APHP, Hôpital Saint-Louis, Paris, France
3Laboratoire de Biologie Cellulaire, Université Paris Cité, APHP, Hôpital Saint-Louis, Paris, France
4INSERM UMR 1131, Institut de Recherche Saint-Louis, Paris, France
5Département d’hématologie et d’Immunologie, Université Paris Cité, APHP, Hôpital Saint-Louis, Paris, France

5:15 PM

Paola Guglielmelli, MD, PhD1, Fiorenza Irushani Vanderwert, BiSc2*, Simone Romagnoli, PhD2*, Giacomo Coltro, MD2*, Giuseppe Gaetano Loscocco, MD2*, Francesco Mannelli, MD2*, Laura Calabresi, PhD2*, Giulia Gentili, BiSc Stud3*, Giada Rotunno, PhD2*, Niccolò Bartalucci, PhD, BSc2*, Valentina Boldrini, MD2*, Emanuela Sant'Antonio4*, Danilo Tarantino, PhD2*, Marco Pieraccioli5* and Alessandro Vannucchi, MD2

1CRIMM, Center of Research and Innovation of Myeloproliferative Neoplasms, University of Florence, AOU Careggi, Florence, Italy
2CRIMM, Center Research and Innovation of Myeloproliferative Neoplasms, University of Florence, AOU Careggi, Florence, Italy
3CRIMM, Center Research and Innovation of Myeloproliferative Neoplasms, University of Florence, Florence, Italy
4University of Siena, GENOMEC Doctorate School, Siena, Italy
5Dept Neurosciences, Sect Human Anatomy, Catholic University of the Sacred Heart, Rome, Italy

*signifies non-member of ASH