Akiko Shimamura, MD, PhD^1*, Alexey Maschan, MD^2*, Carolyn Bennett, MD³, Jason E Farrar, MD⁴, Sujith Samarasinghe, PhD, FRCPath^5*, Brigitte Strahm, MD^6*, Winfred C. Wang, MD⁷, Adrianna Vlachos, MD⁸, Charlotte M. Niemeyer⁶, Timothy S. Olson, MD, PhD⁹, Denise D'Alessio, MBA^10*, Elise Burmeister Getz, PhD^11*, Tomasz Lawniczek, MD¹², Yunnan Xu, PhD^10* and David A. Williams, MD¹

¹Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA
²Dmitry Rogachev National Medical Research Center of Pediatric Hematology, Oncology and Immunology, Moscow, Russian Federation
³Aflac Cancer and Blood Disorder Center, Department of Pediatrics, Children's Healthcare of Atlanta, Emory University School of Medicine, Atlanta, GA
⁴University of Arkansas For Medical Sciences, Little Rock, AR
⁵Department of Paediatric Haematology, Great Ormond Street Hospital for Children, London, United Kingdom
⁶Department of Pediatrics and Adolescent Medicine, Division of Pediatric Hematology and Oncology, Medical Center, Faculty of Medicine, University of Freiburg, Freiburg, Germany
⁷Department of Hematology, St. Jude Children's Research Hospital, Memphis, TN
⁸Division of Hematology/Oncology and Cellular Therapy, Cohen Children's Medical Center, Northwell Health, New York, NY
⁹Department of Pediatrics, Division of Oncology, Children's Hospital of Philadelphia, Philadelphia, PA
¹⁰Novartis Pharmaceuticals Corporation, East Hanover, NJ
¹¹Novartis Institutes for BioMedical Research (NIBR), Emeryville, CA
¹²Novartis Pharma AG, Basel, Switzerland

Joseph H Oved, MD¹, Yash Shah^2*, Yimei Li, PhD^3*, Dimitri S. Monos, PhD^4*, Daria V. Babushok, MD⁵, Minjie Luo, Ph.D.^6*, Marilyn M. Li, MD^7* and Timothy S. Olson, MD, PhD⁸

¹Transplantation and Cellular Therapy, Memorial Sloan Kettering Cancer Center (MSK Kids), New York, NY
²Children's Hospital of Philadelphia, Philadelphia, PA
³Department of Biomedical and Health Informatics, Children's Hospital of Philadelphia, Philadelphia, PA
⁴Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, PA
⁵Division of Hematology-Oncology, Department of Medicine, University of Pennsylvania, Merion Station, PA
⁶Department of Pathology and Laboratory Medicine, The Children's Hospital of Philadelphia, Philadelphia, PA
⁷Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA
⁸Department of Pediatrics, Division of Oncology, Children's Hospital of Philadelphia, Philadelphia, PA

Yoshitaka Zaimoku, MD, PhD^1,2, Hiroki Mizumaki, MD, PhD^2*, Takeshi Yoroidaka, MD, PhD^2*, Noriharu Nakagawa, MD, PhD^2*, Tatsuya Imi, MD, PhD^2*, Hiroyuki Maruyama, MD, PhD^2*, Mikoto Tanabe, MD, PhD^2*, Noriaki Tsuji, MD, PhD^2*, Ryota Urushihara, MD^2*, Kohei Hosokawa, MD, PhD², Takamasa Katagiri, PhD^2*, Hiroyuki Takamatsu, MD, PhD², Ken Ishiyama, MD, PhD², Hirohito Yamazaki, MD, PhD^2*, Toshihiro Miyamoto, MD, PhD² and Shinji Nakao, MD, PhD²

¹Department of Infection Control and Prevention, Kanazawa University Hospital, Kanazawa, Japan
²Department of Hematology, Kanazawa University, Kanazawa, Japan

Srilatha Dasari, MD^1*, William Tse, MD² and Jiasheng Wang, MD³

¹Department of Medicine, MetroHealth Medical Center, Cleveland, OH
²Department of Hematology and Oncology, The MetroHealth System Campus of Case Western Reserve University, Cleveland, OH
³Department of Hematology and Oncology, Seidman Cancer Center, University Hospitals Cleveland Medical Center, Cleveland, OH

Hui Liu^1*, Linghui Xia^2*, Jianyu Weng^3*, Fengkui Zhang^4*, Chuan He^5*, Sujun Gao, PhD^6*, Jinsong Jia^7*, Alice C. Chang^8*, Pontus Lundberg^9*, Camelia S. Sima^8*, Jane Shi^10*, Zhenyu Xiao^10*, Yuchen Zhang^11*, Zilu Zhang^10* and Rong Fu^1*

¹Department of hematology, Tianjin Medical University General Hospital, Tianjin, China
²Wuhan Union Hospital, Wuhan, China
³Guangdong Provincial People’s Hospital, Guangdong, China
⁴Institute of Hematology and Blood Diseases Hospital, CAMS & PUMC, Tianjin, China
⁵West China Hospital, Sichuan University, Chengdu, China
⁶Department of Hematology, The First Hospital of Jilin University, Changchun, China
⁷Peking University People's Hospital, Beijing, China
⁸Genentech, Inc., South San Francisco, CA
⁹F. Hoffmann-La Roche Ltd, Basel, Switzerland
¹⁰Roche Product Development, Shanghai, China
¹¹China Innovation Center of Roche, Shanghai, China

Peter J. Browett¹, Austin Kulasekararaj, MD, MBBS, FRCPath, MRCP², Rosario Notaro, MD^3*, Masayo Ogawa, MD^4*, Antonio M Risitano, MD, PhD⁵, Ji Yu^4* and Jong Wook Lee, M.D., Ph.D.⁶

¹University of Auckland, Auckland, New Zealand
²King's College Hospital - NHS Foundation Trust, NIHR Wellcome King’s Clinical Research Facility, London and King’s College London, London, United Kingdom
³Azienda Ospedaliera Universitaria Careggi, Firenze, Italy
⁴Alexion, AstraZeneca Rare Disease, Boston, MA
⁵Federico II University, Naples, Italy
⁶Seoul St. Mary’s Hospital, The Catholic University of Korea, Seoul, Korea, Republic of (South)