Alessandra Magnani, MD, PhD1,2*, Michaela Semeraro, MD, PhD1,3*, Frédéric ADAM4*, Claire Booth, MBBS, PhD, MSc5,6,7*, Loic Dupre, PhD8*, Emma C Morris9*, Aurélie Gabrion10*, Cecile Roudaut2*, Delphine Borgel, PhD, PharmD11*, Antoine Toubert, MD, PhD12,13,14*, Emmanuel Clave, PhD15*, Chrystelle Abdo, PharmD16*, Guy Gorochov17*, Rachel Petermann18*, Mélanie Guiot19*, Makoto Miyara, MD20*, Despina Moshous, MD, PhD1,21,22*, Elisa Magrin, PharmD10*, Adeline Denis23*, Felipe Suarez, MD, PhD24, Chantal Lagresle-Peyrou25,26,27*, Aoife Doto28*, John K. Everett, PhD29*, Amélie Trinquand30*, Marianne Guisset31*, Jin Hua Xu-Bayford32*, Salima Hacein-Bey-Abina33,34*, Alexandre Kauskot, PhD35*, Reem Elfeky, MD, PhD36*, Christine Rivat6,7,37*, Sarah Abbas38*, Bobby H Gaspar, MBBS, PhD, BS6,39*, Elizabeth A. Macintyre, PhD, MD40,41,42, Capucine Picard, MD, PhD43,44,45,46*, Frederic D. Bushman, PhD28,29*, Anne Galy, PharmD, PhD47,48, Alain Fischer, MD, PhD49,50,51,52, Emmanuelle Six, PhD53,54*, Adrian J. Thrasher, MBBS, PhD, FMedSci6,7,55,56* and Marina Cavazzana, MD, PhD57,58,59,60
1Necker Children’s Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France
2Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Assistance Publique-Hôpitaux de Paris, INSERM, Paris, France
3IMAGINE Institute, Université Paris Descartes, Sorbonne Paris Cité, Paris, France
4INSERM, Le Kremlin-bicêTre, FRA
5Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom
6UCL Great Ormond Street Institute of Child Health, London, United Kingdom
7University College London/Great Ormond Street Hospital, London, United Kingdom
8CPTP, Inserm UMR 1043, Toulouse, France
9University College London, London, United Kingdom
10Biotherapy Department and Clinical Investigation Center, Assistance Publique-Hôpitaux de Paris, INSERM, Paris, France
11INSERM, AP-HP, Paris, FRA
12Laboratoire d’Immunologie et d’Histocompatibilité, Hopital Saint-Louis - APHP, Paris, France
13Institut Universitaire d’Hématologie, INSERM UMR 1160, Université Paris Diderot, Sorbonne Paris Cité, Paris, France
14INSERM UMR 1160, Hopital Saint-Louis - APHP, Paris, France
15Institut Universitaire d’Hématologie, INSERM UMRS 1160, Université Paris Diderot, Sorbonne Paris Cité, Paris, France
16Hopital Necker enfants malades, Paris, FRA
17Hopital Pitie Salpetriere, Paris, FRA
18Institut National de la Transfusion Sanguine (INTS), Department of Platelet Immunology, F-75739, Paris, France
19Université Pierre Et Marie Curie, Paris, FRA
20Immunochemistry department, Pitie Salpetriere Hospital, Paris, FRA
21INSERM UMR 1163, Laboratory of Genome Dynamics in the Immune System, Equipe Labellisée Ligue contre le Cancer, Paris, France
22Imagine Institute, Genome Dynamics in the Immune System, INSERM U1163, Paris, France
23INSERM UMR 1163, Paris, FRA
24Service d'Hématologie adultes, Hôpital Universitaire Necker-Enfants Malades, AP-HP, Paris, France
25Biotherapy Clinical Investigation Center, INSERM. Institut Imagine U1163. Université de Paris, Paris, France
26Biotherapy Clinical Center, Assistance Publique - Hôpitaux de Paris, Paris, France
27INSERM, Paris, France
28University of Pennsylvania, Philadelphia, PA
29Department of Microbiology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA
30Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades (INEM), INSERM U1151, and Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris (AP-HP), Necker - Enfants Malades University Hospital, Paris, France, Paris, France
31Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France, Toulouse, France
32Great Ormond Street Hospital For Children NHS Trust, London, GBR
33Université de Paris, CNRS, INSERM, UTCBS, Unité des technologies Chimiques et Biologiques pour la Santé, Paris, France, Paris, France
34Clinical Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, Hôpital Kremlin-Bicêtre, Assistance Publique-Hôpitaux de Paris, Le-Kremlin-Bicêtre, France, Paris, France
35UMR-S Inserm 1176, Univ Paris Sud, Université Paris-Saclay, le Kremlin-Bicêtre, France
36Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK, London, GBR
37Institute of Child Health, Molecular and Cellular Immunology Unit, University College London, London, United Kingdom
38Généthon, Evry, France, Evry, France
39Orchard Therapeutics, London, United Kingdom
40Institut Necker Enfants Malades, Université de Paris (Descartes), Paris, France
41Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades (INEM), Institut national de recherche médicale (INSERM) U1151, Laboratory of Onco-Haematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, Paris, France
42Laboratory of Onco-Hematology, Necker University Hospital, Paris, France
43Laboratory of lymphocyte activation and susceptibility to EBV, Imagine Institute UMR1163, Paris, France
44Department of Pediatric Immunology, Hematology and Rheumatology, Necker Hospital, Paris, FRA
45Study Center for Primary Immunodeficiencies, Necker-Enfants Malades Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France
46Imagine Institute, University Paris Descartes-Sorbonne Paris Cité, Paris, France
47GENETHON, EVRY, FRA
48Genethon, Evry, France
49INSERM, Paris, FRA
50Department of Pediatric Immunology, Hematology and Rheumatology, Necker Enfants Malades University Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France
51Collège de France, Paris, France
52Imagine Institute, University Paris Descartes-Sorbonne Paris Cité, France, Paris, France
53Laboratory of Human Lymphohematopoiesis, INSERM UMR 1163, Paris, France
54Imagine Institute, Paris Descartes–Sorbonne Paris Cité University, Paris, France
55UCL Institute of Child Health, London, GBR
56University College London; Great Ormond Street Hospital NHS Trust, London, United Kingdom
57University of Paris, Imagine Institute, Laboratory of Human Lymphohematopoiesis, INSERM UMR 1163, Paris, France
58Smart Immune, Paris, France
59IMAGINE Institute Sorbonne Paris Cité, Université Paris Descartes, Paris, France
60Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Ouest, Paris, France