denotes an abstract that is clinically relevant.
denotes that this is a recommended PHD Trainee Session.
denotes that this is a ticketed session.Sponsor: BioMarin, uniQure, Pfizer
Program: Satellite Symposia
Hematology Disease Topics & Pathways:
Bleeding Disorders, Hemophilia, Biological, Diseases, Bleeding and Clotting, Therapies, gene therapy
Hematology Disease Topics & Pathways:
Bleeding Disorders, Hemophilia, Biological, Diseases, Bleeding and Clotting, Therapies, gene therapy
Friday, December 4, 2020: 3:00 PM-6:00 PM
Chair:
Glenn F. Pierce, MD, PhD, World Federation of Hemophilia
Disclosures:
Pierce: CRISPR Therapeutics: Honoraria; Generation Bio: Honoraria; VarmX: Honoraria; Pfizer: Honoraria; BioMarin: Consultancy, Honoraria; Voyager Therapeutics: Membership on an entity's Board of Directors or advisory committees; Third Rock Ventures: Consultancy; Ambys Medicines: Consultancy, Ended employment in the past 24 months; Decibel Therapeutics: Consultancy, Membership on an entity's Board of Directors or advisory committees.
Speakers:
Lindsey George, MD, The Children’s Hospital of Philadelphia
,
Alfonso Iorio, MD, PhD, McMaster University
and
Barbara A. Konkle, MD, Washington Center for Bleeding Disorders
Disclosures:
George: Avrobio: Other: DSMB. Konkle: Sigilon: Consultancy, Research Funding; Pfizer: Consultancy, Research Funding; BioMarin: Consultancy; CSL Behring: Consultancy; Roche: Consultancy; Baxalta: Research Funding; Spark: Consultancy, Research Funding; Sanofi: Consultancy, Research Funding; Takeda: Research Funding; Uniquire: Research Funding.
As the science of gene therapy for hemophilia treatments continues to advance it is important that clinicians are prepared for implementation in their respective hemophilia treatment centers (HTCs). During this session faculty will deliver content in a variety of formats designed to engage the learners and increase retention of the information. This will include Concept Check-In, questions designed to allow learners to self-assess current understanding of gene therapy, faculty presentations during which expert faculty will review data presented in multimedia formats, as well as the use of case-based learning strategies and live interactive panel discussions.
See more of: Satellite Symposia