-Author name in bold denotes the presenting author
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Clinically Relevant Abstract denotes an abstract that is clinically relevant.

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SCI-31 Clonal Tracking Post-Gene Therapy for Fanconi Anemia

Program: Scientific Program
Session: Precision Medicine Approaches to Leukemia Predisposition in Bone Marrow Failure
Hematology Disease Topics & Pathways:
Biological, Diseases, Bone Marrow Failure, Therapies, Genetic Disorders, gene therapy
Monday, December 7, 2020, 11:25 AM-11:30 AM

Paula Rio, PhD

Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas (CIEMAT), Madrid, Spain

Disclosures: Rio: Rocket Pharmaceuticals Inc.: Patents & Royalties, Research Funding.

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